Literature DB >> 25951531

Corrigendum: Translation from a DMD exon 5 IRES results in a functional dystrophin isoform that attenuates dystrophinopathy in humans and mice.

Nicolas Wein, Adeline Vulin, Maria S Falzarano, Christina Al-Khalili Szigyarto, Baijayanta Maiti, Andrew Findlay, Kristin N Heller, Mathias Uhlén, Baskar Bakthavachalu, Sonia Messina, Giuseppe Vita, Chiara Passarelli, Simona Brioschi, Matteo Bovolenta, Marcella Neri, Francesca Gualandi, Steve D Wilton, Louise R Rodino-Klapac, Lin Yang, Diane M Dunn, Daniel R Schoenberg, Robert B Weiss, Michael T Howard, Alessandra Ferlini, Kevin M Flanigan.   

Abstract

Entities:  

Year:  2015        PMID: 25951531     DOI: 10.1038/nm0515-537c

Source DB:  PubMed          Journal:  Nat Med        ISSN: 1078-8956            Impact factor:   53.440


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  1 in total

1.  Translation from a DMD exon 5 IRES results in a functional dystrophin isoform that attenuates dystrophinopathy in humans and mice.

Authors:  Nicolas Wein; Adeline Vulin; Maria S Falzarano; Christina Al-Khalili Szigyarto; Baijayanta Maiti; Andrew Findlay; Kristin N Heller; Mathias Uhlén; Baskar Bakthavachalu; Sonia Messina; Giuseppe Vita; Chiara Passarelli; Simona Brioschi; Matteo Bovolenta; Marcella Neri; Francesca Gualandi; Steve D Wilton; Louise R Rodino-Klapac; Lin Yang; Diane M Dunn; Daniel R Schoenberg; Robert B Weiss; Michael T Howard; Alessandra Ferlini; Kevin M Flanigan
Journal:  Nat Med       Date:  2014-08-10       Impact factor: 53.440

  1 in total

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