Andrea Ballabio1, Luigi Naldini. Show Affiliations » 1. 1 Telethon Institute of Genetics and Medicine (TIGEM) , Pozzuoli, Naples 80078, Italy .
Abstract
Entities: Chemical
Mesh: See more » Academies and Institutes/organization & administrationAnimalsGenetic Diseases, Inborn/geneticsGenetic Diseases, Inborn/therapyGenetic ResearchGenetic TherapyGenetics, MedicalHumansItalyRare Diseases/geneticsRare Diseases/therapy
Year: 2015 PMID: 25901396 DOI: 10.1089/hum.2015.2501
Source DB: PubMed Journal: Hum Gene Ther ISSN: 1043-0342 Impact factor: 5.695