Literature DB >> 25809543

Targeting the EWS-FLI1 transcription factor in Ewing sarcoma.

R Tancredi1, A Zambelli, G A DaPrada, V Fregoni, L Pavesi, A Riccardi, S Burdach, P J Grohar, M D'Incalci.   

Abstract

PURPOSE: Preclinical data indicate there is strong synergism of action against Ewing sarcoma in sequential treatment with trabectedin followed by irinotecan and it appears to be related to a selective blockade of the transcription factor EWS-FLI1. This combination was evaluated in Ewing sarcoma patient who was progressing with standard therapies.
METHODS: Trabectedin was given as a 24-h iv infusion on day 1 at the dose of 1 mg/sqm, and irinotecan 75 mg/sqm on day 2 and then on days 2 and 4, every 3 weeks from the seventh course.
RESULTS: The therapy was well tolerated with transient hematological toxicity and transaminitis and induced stabilization of the disease lasting for 11 courses, with clinical improvement and marked reduction of the need for opioids. However, shortly before the 12th course, sudden death occurred, possibly due to cerebral stroke, presumably not related to the drug treatment.
CONCLUSIONS: The encouraging clinical benefit observed with the combination and its good tolerability deserves further investigation in Ewing sarcoma.

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Year:  2015        PMID: 25809543     DOI: 10.1007/s00280-015-2726-7

Source DB:  PubMed          Journal:  Cancer Chemother Pharmacol        ISSN: 0344-5704            Impact factor:   3.333


  10 in total

1.  EWSR1 rearrangement is a frequent event in papillary thyroid carcinoma and in carcinoma of the thyroid with Ewing family tumor elements (CEFTE).

Authors:  G Oliveira; A Polónia; J M Cameselle-Teijeiro; D Leitão; S Sapia; M Sobrinho-Simões; C Eloy
Journal:  Virchows Arch       Date:  2017-02-24       Impact factor: 4.064

2.  Establishment and characterization of a novel patient-derived Ewing sarcoma cell line, NCC-ES2-C1.

Authors:  Yuki Yoshimatsu; Rei Noguchi; Yooksil Sin; Ryuto Tsuchiya; Takuya Ono; Taro Akiyama; Rumi Nakagawa; Satoshi Kamio; Kaoru Hirabayashi; Iwao Ozawa; Kazutaka Kikuta; Tadashi Kondo
Journal:  Hum Cell       Date:  2022-04-19       Impact factor: 4.174

Review 3.  Advances in the Treatment of Pediatric Bone Sarcomas.

Authors:  Patrick J Grohar; Katherine A Janeway; Luke D Mase; Joshua D Schiffman
Journal:  Am Soc Clin Oncol Educ Book       Date:  2017

4.  Lurbinectedin Inactivates the Ewing Sarcoma Oncoprotein EWS-FLI1 by Redistributing It within the Nucleus.

Authors:  Matt L Harlow; Nichole Maloney; Joseph Roland; Maria Jose Guillen Navarro; Matthew K Easton; Susan M Kitchen-Goosen; Elissa A Boguslawski; Zachary B Madaj; Ben K Johnson; Megan J Bowman; Maurizio D'Incalci; Mary E Winn; Lisa Turner; Galen Hostetter; Carlos María Galmarini; Pablo M Aviles; Patrick J Grohar
Journal:  Cancer Res       Date:  2016-10-03       Impact factor: 12.701

5.  Trabectedin Followed by Irinotecan Can Stabilize Disease in Advanced Translocation-Positive Sarcomas with Acceptable Toxicity.

Authors:  J Herzog; F von Klot-Heydenfeldt; S Jabar; A Ranft; C Rossig; U Dirksen; J Van den Brande; M D'Incalci; I von Luettichau; P J Grohar; W E Berdel; St Burdach
Journal:  Sarcoma       Date:  2016-10-24

6.  Combined analysis of gene expression and genome binding profiles identified potential therapeutic targets of ciclopirox in Ewing sarcoma.

Authors:  Baisheng Yuan; Wei Ji; Haipeng Xia; Jianmin Li
Journal:  Mol Med Rep       Date:  2018-01-10       Impact factor: 2.952

7.  Trabectedin and Campthotecin Synergistically Eliminate Cancer Stem Cells in Cell-of-Origin Sarcoma Models.

Authors:  Lucia Martinez-Cruzado; Juan Tornin; Aida Rodriguez; Laura Santos; Eva Allonca; Maria Teresa Fernandez-Garcia; Aurora Astudillo; Juana Maria Garcia-Pedrero; Rene Rodriguez
Journal:  Neoplasia       Date:  2017-05-08       Impact factor: 5.715

8.  Gene expression signature based screening identifies ribonucleotide reductase as a candidate therapeutic target in Ewing sarcoma.

Authors:  Kelli L Goss; David J Gordon
Journal:  Oncotarget       Date:  2016-09-27

Review 9.  Current Approaches for Personalized Therapy of Soft Tissue Sarcomas.

Authors:  Kirill I Kirsanov; Ekaterina A Lesovaya; Timur I Fetisov; Beniamin Yu Bokhyan; Gennady A Belitsky; Marianna G Yakubovskaya
Journal:  Sarcoma       Date:  2020-03-31

10.  A systems biology approach to investigate the mechanism of action of trabectedin in a model of myelomonocytic leukemia.

Authors:  L Mannarino; L Paracchini; I Craparotta; M Romano; S Marchini; R Gatta; E Erba; L Clivio; C Romualdi; M D'Incalci; L Beltrame; L Pattini
Journal:  Pharmacogenomics J       Date:  2016-12-13       Impact factor: 3.550

  10 in total

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