Literature DB >> 25745148

RNA interference. Drugging RNAi.

Dirk Haussecker1, Mark A Kay2.   

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Year:  2015        PMID： 25745148      PMCID： PMC6018011          DOI： 10.1126/science.1252967

Source DB:  PubMed          Journal:  Science        ISSN： 0036-8075            Impact factor:   47.728


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  12 in total

1.  A genetic strategy to treat sickle cell anemia by coregulating globin transgene expression and RNA interference.

Authors:  Selda Samakoglu; Leszek Lisowski; Tulin Budak-Alpdogan; Yelena Usachenko; Santina Acuto; Rosalba Di Marzo; Aurelio Maggio; Ping Zhu; John F Tisdale; Isabelle Rivière; Michel Sadelain
Journal:  Nat Biotechnol       Date:  2005-12-25       Impact factor: 54.908

2.  Widespread siRNA "off-target" transcript silencing mediated by seed region sequence complementarity.

Authors:  Aimee L Jackson; Julja Burchard; Janell Schelter; B Nelson Chau; Michele Cleary; Lee Lim; Peter S Linsley
Journal:  RNA       Date:  2006-05-08       Impact factor: 4.942

3.  The loop position of shRNAs and pre-miRNAs is critical for the accuracy of dicer processing in vivo.

Authors:  Shuo Gu; Lan Jin; Yue Zhang; Yong Huang; Feijie Zhang; Paul N Valdmanis; Mark A Kay
Journal:  Cell       Date:  2012-11-09       Impact factor: 41.582

Review 4.  Current issues of RNAi therapeutics delivery and development.

Authors:  D Haussecker
Journal:  J Control Release       Date:  2014-08-09       Impact factor: 9.776

5.  Safety and efficacy of RNAi therapy for transthyretin amyloidosis.

Authors:  Teresa Coelho; David Adams; Ana Silva; Pierre Lozeron; Philip N Hawkins; Timothy Mant; Javier Perez; Joseph Chiesa; Steve Warrington; Elizabeth Tranter; Malathy Munisamy; Rick Falzone; Jamie Harrop; Jeffrey Cehelsky; Brian R Bettencourt; Mary Geissler; James S Butler; Alfica Sehgal; Rachel E Meyers; Qingmin Chen; Todd Borland; Renta M Hutabarat; Valerie A Clausen; Rene Alvarez; Kevin Fitzgerald; Christina Gamba-Vitalo; Saraswathy V Nochur; Akshay K Vaishnaw; Dinah W Y Sah; Jared A Gollob; Ole B Suhr
Journal:  N Engl J Med       Date:  2013-08-29       Impact factor: 91.245

6.  Hepatocyte-targeted RNAi therapeutics for the treatment of chronic hepatitis B virus infection.

Authors:  Christine I Wooddell; David B Rozema; Markus Hossbach; Matthias John; Holly L Hamilton; Qili Chu; Julia O Hegge; Jason J Klein; Darren H Wakefield; Claudia E Oropeza; Jochen Deckert; Ingo Roehl; Kerstin Jahn-Hofmann; Philipp Hadwiger; Hans-Peter Vornlocher; Alan McLachlan; David L Lewis
Journal:  Mol Ther       Date:  2013-02-26       Impact factor: 11.454

7.  Improved specificity of gene silencing by siRNAs containing unlocked nucleobase analogs.

Authors:  Narendra Vaish; Feng Chen; Shaguna Seth; Kathy Fosnaugh; Yan Liu; Roger Adami; Tod Brown; Yan Chen; Pierrot Harvie; Rachel Johns; Gregory Severson; Brian Granger; Patrick Charmley; Michael Houston; Michael V Templin; Barry Polisky
Journal:  Nucleic Acids Res       Date:  2010-11-02       Impact factor: 16.971

8.  Sustained miRNA-mediated knockdown of mutant AAT with simultaneous augmentation of wild-type AAT has minimal effect on global liver miRNA profiles.

Authors:  Christian Mueller; Qiushi Tang; Alisha Gruntman; Keith Blomenkamp; Jeffery Teckman; Lina Song; Phillip D Zamore; Terence R Flotte
Journal:  Mol Ther       Date:  2012-01-17       Impact factor: 11.454

9.  The Business of RNAi Therapeutics in 2012.

Authors:  Dirk Haussecker
Journal:  Mol Ther Nucleic Acids       Date:  2012-02-07       Impact factor: 10.183

10.  Targeted delivery of antisense oligonucleotides to hepatocytes using triantennary N-acetyl galactosamine improves potency 10-fold in mice.

Authors:  Thazha P Prakash; Mark J Graham; Jinghua Yu; Rick Carty; Audrey Low; Alfred Chappell; Karsten Schmidt; Chenguang Zhao; Mariam Aghajan; Heather F Murray; Stan Riney; Sheri L Booten; Susan F Murray; Hans Gaus; Jeff Crosby; Walt F Lima; Shuling Guo; Brett P Monia; Eric E Swayze; Punit P Seth
Journal:  Nucleic Acids Res       Date:  2014-07-03       Impact factor: 16.971
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  31 in total

Review 1.  Neurology--the next 10 years.

Authors:  Ralf Baron; Donna M Ferriero; Giovanni B Frisoni; Chetan Bettegowda; Ziya L Gokaslan; John A Kessler; Annamaria Vezzani; Stephen G Waxman; Sven Jarius; Brigitte Wildemann; Michael Weller
Journal:  Nat Rev Neurol       Date:  2015-10-27       Impact factor: 42.937

2.  Future of rAAV Gene Therapy: Platform for RNAi, Gene Editing, and Beyond.

Authors:  Paul N Valdmanis; Mark A Kay
Journal:  Hum Gene Ther       Date:  2017-01-10       Impact factor: 5.695

Review 3.  The Race of 10 Synthetic RNAi-Based Drugs to the Pharmaceutical Market.

Authors:  Ricardo Titze-de-Almeida; Catherine David; Simoneide Souza Titze-de-Almeida
Journal:  Pharm Res       Date:  2017-04-07       Impact factor: 4.200

Review 4.  Advances in the clinical translation of nanotechnology.

Authors:  David A Scheinberg; Jan Grimm; Daniel A Heller; Evan P Stater; Michelle Bradbury; Michael R McDevitt
Journal:  Curr Opin Biotechnol       Date:  2017-02-07       Impact factor: 9.740

5.  Mastering Dendrimer Self-Assembly for Efficient siRNA Delivery: From Conceptual Design to In Vivo Efficient Gene Silencing.

Authors:  Chao Chen; Paola Posocco; Xiaoxuan Liu; Qiang Cheng; Erik Laurini; Jiehua Zhou; Cheng Liu; Yang Wang; Jingjie Tang; Valentina Dal Col; Tianzhu Yu; Suzanne Giorgio; Maurizio Fermeglia; Fanqi Qu; Zicai Liang; John J Rossi; Minghua Liu; Palma Rocchi; Sabrina Pricl; Ling Peng
Journal:  Small       Date:  2016-05-31       Impact factor: 13.281

6.  The effector mechanism of siRNA spherical nucleic acids.

Authors:  Gokay Yamankurt; Robert J Stawicki; Diana M Posadas; Joseph Q Nguyen; Richard W Carthew; Chad A Mirkin
Journal:  Proc Natl Acad Sci U S A       Date:  2020-01-03       Impact factor: 11.205

Review 7.  The delivery of therapeutic oligonucleotides.

Authors:  Rudolph L Juliano
Journal:  Nucleic Acids Res       Date:  2016-04-15       Impact factor: 16.971

Review 8.  Non-coding RNAs in cardiovascular diseases: diagnostic and therapeutic perspectives.

Authors:  Wolfgang Poller; Stefanie Dimmeler; Stephane Heymans; Tanja Zeller; Jan Haas; Mahir Karakas; David-Manuel Leistner; Philipp Jakob; Shinichi Nakagawa; Stefan Blankenberg; Stefan Engelhardt; Thomas Thum; Christian Weber; Benjamin Meder; Roger Hajjar; Ulf Landmesser
Journal:  Eur Heart J       Date:  2018-08-01       Impact factor: 29.983

9.  Adenovirus-mediated shRNA interference against HSV-1 replication in vitro.

Authors:  Bo Song; Xinjing Liu; Qingzhi Wang; Rui Zhang; Ting Yang; Zhiqiang Han; Yuming Xu
Journal:  J Neurovirol       Date:  2016-08-26       Impact factor: 2.643

10.  A biodistribution study of solid lipid-polyethyleneimine hybrid nanocarrier for cancer RNAi therapy.

Authors:  Hui Yi Xue; Ngoc Tran; Ho Lun Wong
Journal:  Eur J Pharm Biopharm       Date:  2016-08-26       Impact factor: 5.571
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