Literature DB >> 25300501

Copy number variants in short children born small for gestational age.

Jan M Wit1, Hermine A van Duyvenvoorde, Jan B van Klinken, Janina Caliebe, Cathy A J Bosch, Julian C Lui, Antoinet C J Gijsbers, Egbert Bakker, Martijn H Breuning, Wilma Oostdijk, Monique Losekoot, Jeffrey Baron, Gerhard Binder, Michael B Ranke, Claudia A L Ruivenkamp.   

Abstract

BACKGROUND/AIMS: In addition to genome-wide association studies (GWAS), height-associated genes may be uncovered by studying individuals with extreme short or tall stature.
METHODS: Genome-wide analysis for copy number variants (CNVs), using single nucleotide polymorphism (SNP) arrays, was performed in 49 index cases born small for gestational age with persistent short stature. Segregation analysis was performed, and genes in CNVs were compared with information from GWAS, gene expression in rodents' growth plates, and published information.
RESULTS: CNVs were detected in 13 cases. In 5 children a known cause of short stature was found: UPD7, UPD14, a duplication of the SHOX enhancer region, an IGF1R deletion, and a 22q11.21 deletion. In the remaining 8 cases, potential pathogenic CNVs were detected, either de novo (n = 1), segregating (n = 2), or not segregating with short stature (n = 5). Bioinformatic analysis of the de novo and segregating CNVs suggested that HOXD4, AGPS, PDE11A, OSBPL6, PRKRA and PLEKHA3, and possibly DGKB and TNFRSF11B are potential candidate genes. A SERPINA7 or NRK defect may be associated with an X-linked form of short stature.
CONCLUSION: SNP arrays detected 5 known causes of short stature with prenatal onset and suggested several potential candidate genes. 2014 S. Karger AG, Basel

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Year:  2014        PMID: 25300501      PMCID: PMC4236248          DOI: 10.1159/000367712

Source DB:  PubMed          Journal:  Horm Res Paediatr        ISSN: 1663-2818            Impact factor:   2.852


  59 in total

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Authors:  Andrew Dauber; Yongguo Yu; Michael C Turchin; Charleston W Chiang; Yan A Meng; Ellen W Demerath; Sanjay R Patel; Stephen S Rich; Jerome I Rotter; Pamela J Schreiner; James G Wilson; Yiping Shen; Bai-Lin Wu; Joel N Hirschhorn
Journal:  Am J Hum Genet       Date:  2011-11-23       Impact factor: 11.025

2.  PAR1 deletions downstream of SHOX are the most frequent defect in a Spanish cohort of Léri-Weill dyschondrosteosis (LWD) probands.

Authors:  Sara Benito-Sanz; Darya Gorbenko del Blanco; Miriam Aza-Carmona; Luis F Magano; Pablo Lapunzina; Jesús Argente; Angel Campos-Barros; Karen E Heath
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3.  Synthesizing genome-wide association studies and expression microarray reveals novel genes that act in the human growth plate to modulate height.

Authors:  Julian C Lui; Ola Nilsson; Yingleong Chan; Cameron D Palmer; Anenisia C Andrade; Joel N Hirschhorn; Jeffrey Baron
Journal:  Hum Mol Genet       Date:  2012-08-21       Impact factor: 6.150

4.  Unexpected phenotype in a boy with trisomy of the SHOX gene.

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Journal:  J Clin Endocrinol Metab       Date:  2012-08-29       Impact factor: 5.958

6.  Clinical and molecular evaluation of SHOX/PAR1 duplications in Leri-Weill dyschondrosteosis (LWD) and idiopathic short stature (ISS).

Authors:  S Benito-Sanz; E Barroso; D Heine-Suñer; A Hisado-Oliva; V Romanelli; J Rosell; A Aragones; M Caimari; J Argente; J L Ross; A R Zinn; R Gracia; P Lapunzina; A Campos-Barros; K E Heath
Journal:  J Clin Endocrinol Metab       Date:  2010-12-08       Impact factor: 5.958

7.  Mutations in paralogous Hox genes result in overlapping homeotic transformations of the axial skeleton: evidence for unique and redundant function.

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8.  Osteoprotegerin, a crucial regulator of bone metabolism, also regulates B cell development and function.

Authors:  T J Yun; M D Tallquist; A Aicher; K L Rafferty; A J Marshall; J J Moon; M E Ewings; M Mohaupt; S W Herring; E A Clark
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9.  Gene amplification as a cause of inherited thyroxine-binding globulin excess in two Japanese families.

Authors:  Y Mori; Y Miura; H Takeuchi; Y Igarashi; J Sugiura; H Saito; Y Oiso
Journal:  J Clin Endocrinol Metab       Date:  1995-12       Impact factor: 5.958

10.  Short stature and thyroxine-binding globulin excess: improvement with triiodothyronine treatment.

Authors:  N Alain; W B Zipf
Journal:  Pediatrics       Date:  1988-05       Impact factor: 7.124

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  6 in total

1.  Rare pseudoautosomal copy-number variations involving SHOX and/or its flanking regions in individuals with and without short stature.

Authors:  Maki Fukami; Yasuhiro Naiki; Koji Muroya; Takashi Hamajima; Shun Soneda; Reiko Horikawa; Tomoko Jinno; Momori Katsumi; Akie Nakamura; Yumi Asakura; Masanori Adachi; Tsutomu Ogata; Susumu Kanzaki
Journal:  J Hum Genet       Date:  2015-06-04       Impact factor: 3.172

2.  Focused Revision: ACMG practice resource: Genetic evaluation of short stature.

Authors:  Cassie S Mintz; Laurie H Seaver; Mira Irons; Adda Grimberg; Reymundo Lozano
Journal:  Genet Med       Date:  2021-01-29       Impact factor: 8.822

Review 3.  A Track Record on SHOX: From Basic Research to Complex Models and Therapy.

Authors:  Antonio Marchini; Tsutomu Ogata; Gudrun A Rappold
Journal:  Endocr Rev       Date:  2016-06-29       Impact factor: 19.871

4.  Prevalence of copy number variants (CNVs) and rhGH treatment efficacy in an Italian cohort of children born small for gestational age (SGA) with persistent short stature associated with a complex clinical phenotype.

Authors:  E Inzaghi; A Deodati; S Loddo; M Mucciolo; F Verdecchia; E Sallicandro; G Catino; M Cappa; A Novelli; S Cianfarani
Journal:  J Endocrinol Invest       Date:  2021-07-13       Impact factor: 4.256

5.  Copy number variations in 119 Chinese children with idiopathic short stature identified by the custom genome-wide microarray.

Authors:  Guorui Hu; Yanjie Fan; Lili Wang; Ru-En Yao; Xiaodong Huang; Yiping Shen; Yongguo Yu; Xuefan Gu
Journal:  Mol Cytogenet       Date:  2016-02-16       Impact factor: 2.009

6.  Rare CNVs provide novel insights into the molecular basis of GH and IGF-1 insensitivity.

Authors:  Emily Cottrell; Claudia P Cabrera; Miho Ishida; Sumana Chatterjee; James Greening; Neil Wright; Artur Bossowski; Leo Dunkel; Asma Deeb; Iman Al Basiri; Stephen J Rose; Avril Mason; Susan Bint; Joo Wook Ahn; Vivian Hwa; Louise A Metherell; Gudrun E Moore; Helen L Storr
Journal:  Eur J Endocrinol       Date:  2020-12       Impact factor: 6.664

  6 in total

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