Literature DB >> 25209781

Curing blindness: Vision quest.

Corie Lok1.   

Abstract

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Year:  2014        PMID: 25209781     DOI: 10.1038/513160a

Source DB:  PubMed          Journal:  Nature        ISSN: 0028-0836            Impact factor:   49.962


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  13 in total

1.  EFFECTS OF MONOCULAR DEPRIVATION IN KITTENS.

Authors:  D H HUBEL; T N WIESEL
Journal:  Naunyn Schmiedebergs Arch Exp Pathol Pharmakol       Date:  1964-08-19

2.  Stem-cell research: Never say die.

Authors:  Corie Lok
Journal:  Nature       Date:  2012-01-11       Impact factor: 49.962

3.  Retinal gene therapy coming of age.

Authors:  Connie L Cepko; Luk H Vandenberghe
Journal:  Hum Gene Ther       Date:  2013-03       Impact factor: 5.695

4.  Effect of gene therapy on visual function in Leber's congenital amaurosis.

Authors:  James W B Bainbridge; Alexander J Smith; Susie S Barker; Scott Robbie; Robert Henderson; Kamaljit Balaggan; Ananth Viswanathan; Graham E Holder; Andrew Stockman; Nick Tyler; Simon Petersen-Jones; Shomi S Bhattacharya; Adrian J Thrasher; Fred W Fitzke; Barrie J Carter; Gary S Rubin; Anthony T Moore; Robin R Ali
Journal:  N Engl J Med       Date:  2008-04-27       Impact factor: 91.245

5.  Age-dependent effects of RPE65 gene therapy for Leber's congenital amaurosis: a phase 1 dose-escalation trial.

Authors:  Albert M Maguire; Katherine A High; Alberto Auricchio; J Fraser Wright; Eric A Pierce; Francesco Testa; Federico Mingozzi; Jeannette L Bennicelli; Gui-shuang Ying; Settimio Rossi; Ann Fulton; Kathleen A Marshall; Sandro Banfi; Daniel C Chung; Jessica I W Morgan; Bernd Hauck; Olga Zelenaia; Xiaosong Zhu; Leslie Raffini; Frauke Coppieters; Elfride De Baere; Kenneth S Shindler; Nicholas J Volpe; Enrico M Surace; Carmela Acerra; Arkady Lyubarsky; T Michael Redmond; Edwin Stone; Junwei Sun; Jennifer Wellman McDonnell; Bart P Leroy; Francesca Simonelli; Jean Bennett
Journal:  Lancet       Date:  2009-10-23       Impact factor: 79.321

6.  Treatment of leber congenital amaurosis due to RPE65 mutations by ocular subretinal injection of adeno-associated virus gene vector: short-term results of a phase I trial.

Authors:  William W Hauswirth; Tomas S Aleman; Shalesh Kaushal; Artur V Cideciyan; Sharon B Schwartz; Lili Wang; Thomas J Conlon; Sanford L Boye; Terence R Flotte; Barry J Byrne; Samuel G Jacobson
Journal:  Hum Gene Ther       Date:  2008-10       Impact factor: 5.695

7.  Restoration of vision after transplantation of photoreceptors.

Authors:  R A Pearson; A C Barber; M Rizzi; C Hippert; T Xue; E L West; Y Duran; A J Smith; J Z Chuang; S A Azam; U F O Luhmann; A Benucci; C H Sung; J W Bainbridge; M Carandini; K-W Yau; J C Sowden; R R Ali
Journal:  Nature       Date:  2012-05-03       Impact factor: 49.962

8.  The human visual cortex responds to gene therapy-mediated recovery of retinal function.

Authors:  Manzar Ashtari; Laura L Cyckowski; Justin F Monroe; Kathleen A Marshall; Daniel C Chung; Alberto Auricchio; Francesca Simonelli; Bart P Leroy; Albert M Maguire; Kenneth S Shindler; Jean Bennett
Journal:  J Clin Invest       Date:  2011-05-23       Impact factor: 14.808

9.  Photoreceptor precursors derived from three-dimensional embryonic stem cell cultures integrate and mature within adult degenerate retina.

Authors:  Anai Gonzalez-Cordero; Emma L West; Rachael A Pearson; Yanai Duran; Livia S Carvalho; Colin J Chu; Arifa Naeem; Samuel J I Blackford; Anastasios Georgiadis; Jorn Lakowski; Mike Hubank; Alexander J Smith; James W B Bainbridge; Jane C Sowden; Robin R Ali
Journal:  Nat Biotechnol       Date:  2013-07-21       Impact factor: 54.908

10.  Retinal gene therapy in patients with choroideremia: initial findings from a phase 1/2 clinical trial.

Authors:  Robert E MacLaren; Markus Groppe; Alun R Barnard; Charles L Cottriall; Tanya Tolmachova; Len Seymour; K Reed Clark; Matthew J During; Frans P M Cremers; Graeme C M Black; Andrew J Lotery; Susan M Downes; Andrew R Webster; Miguel C Seabra
Journal:  Lancet       Date:  2014-01-16       Impact factor: 79.321

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  2 in total

Review 1.  Gene therapy of inherited retinal degenerations: prospects and challenges.

Authors:  Ivana Trapani; Sandro Banfi; Francesca Simonelli; Enrico M Surace; Alberto Auricchio
Journal:  Hum Gene Ther       Date:  2015-04       Impact factor: 5.695

2.  Retinal Processing: Insights from Mathematical Modelling.

Authors:  Bruno Cessac
Journal:  J Imaging       Date:  2022-01-17
  2 in total

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