| Literature DB >> 25149931 |
Elizabeth A Sellars1, Katherine A Bosanko2, Tiffany Lepard2, Adolfo Garnica2, Gerald Bradley Schaefer2.
Abstract
A newborn presented to genetics with complex skeletal abnormalities, joint contractures, and bilateral corneal clouding with sclerocornea. The patient survived for 8 months before succumbing to respiratory failure. Exome sequencing revealed a compound heterozygous mutation in theB3GALT6gene. Mutations in this gene have been associated with both Ehlers- Danlos syndrome, progeroid type 2 and spondyloepimetaphyseal dysplasia with joint laxity type 1. These diagnoses encompass the skeletal and joint findings. Our patient expands the phenotype of these diagnoses, as anterior segment eye anomalies have not been described with either syndrome, and he is much more profoundly affected. Interestingly, our patient fits the description of a rare genetic disease referred to as Al-Gazali syndrome, for which the genetic cause is unknown.Entities:
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Year: 2014 PMID: 25149931 DOI: 10.1016/j.spen.2014.04.007
Source DB: PubMed Journal: Semin Pediatr Neurol ISSN: 1071-9091 Impact factor: 1.636