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Abstract
Entities: Disease
Mesh: See more » Cell- and Tissue-Based TherapyCerebroside-Sulfatase/geneticsCerebroside-Sulfatase/metabolismEthics, ResearchGalactosylceramidase/geneticsGalactosylceramidase/metabolismGenetic TherapyGenetic Vectors/geneticsGenetic Vectors/metabolismHematopoietic Stem Cell TransplantationHematopoietic Stem Cells/cytologyHematopoietic Stem Cells/metabolismHereditary Central Nervous System Demyelinating Diseases/therapyHumans
Substances: See more » Cerebroside-SulfataseGalactosylceramidase
Year: 2014 PMID: 24933566 DOI: 10.1089/humc.2014.2509
Source DB: PubMed Journal: Hum Gene Ther Clin Dev ISSN: 2324-8637 Impact factor: 5.032