Literature DB >> 24933566

Therapeutic challenge in leukodystrophies: translational and ethical research toward clinical trials (LeukoTreat).

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Year:  2014        PMID: 24933566     DOI: 10.1089/humc.2014.2509

Source DB:  PubMed          Journal:  Hum Gene Ther Clin Dev        ISSN: 2324-8637            Impact factor:   5.032


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  1 in total

Review 1.  The ethical framework for performing research with rare inherited neurometabolic disease patients.

Authors:  Viviana Giannuzzi; Hugo Devlieger; Lucia Margari; Viveca Lena Odlind; Lamis Ragab; Cinzia Maria Bellettato; Francesca D'Avanzo; Christina Lampe; Linda Cassis; Elisenda Cortès-Saladelafont; Ángels Garcia Cazorla; Ivo Barić; Ljerka Cvitanović-Šojat; Ksenija Fumić; Christine I Dali; Franco Bartoloni; Fedele Bonifazi; Maurizio Scarpa; Adriana Ceci
Journal:  Eur J Pediatr       Date:  2017-01-16       Impact factor: 3.183

  1 in total

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