Sara Reardon. Show Affiliations »
Abstract
Mesh: See more » Anemia, Sickle Cell/drug therapyAnemia, Sickle Cell/epidemiologyCystic Fibrosis/drug therapyCystic Fibrosis/epidemiologyDrug Approval/legislation & jurisprudenceDrug Approval/statistics & numerical dataDrug Industry/economicsHumansOrphan Drug Production/economicsOrphan Drug Production/legislation & jurisprudenceOrphan Drug Production/statistics & numerical dataRare Diseases/drug therapyRare Diseases/economicsRare Diseases/epidemiologyUnited StatesUnited States Food and Drug Administration/legislation & jurisprudence
Year: 2014 PMID: 24695293 DOI: 10.1038/508016a
Source DB: PubMed Journal: Nature ISSN: 0028-0836 Impact factor: 49.962