Jane C Davies1. Show Affiliations » 1. Department of Paediatric Respiratory Medicine, Royal Brompton and Harefield NHS Foundation Trust, London, UK; Imperial College London, Manresa Road, London SW3 6LR, UK. Electronic address: j.c.davies@imperial.ac.uk.
Abstract
Entities: Disease
Mesh: See more » Aminophenols/therapeutic useChildChild, PreschoolCystic Fibrosis/therapyCystic Fibrosis Transmembrane Conductance Regulator/antagonists & inhibitorsGenetic Therapy/trendsHumansInfantInfant, NewbornQuinolones/therapeutic use
Substances: See more » AminophenolsQuinolonesCystic Fibrosis Transmembrane Conductance Regulatorivacaftor
Year: 2013 PMID: 24429232 DOI: 10.1016/S2213-2600(13)70136-X
Source DB: PubMed Journal: Lancet Respir Med ISSN: 2213-2600 Impact factor: 30.700