Literature DB >> 24296360

Association of a paraneoplastic motor neuron disease with anti-Ri antibodies and a novel SOD1 I18del mutation.

Capucine Diard-Detoeuf1, Audrey Dangoumau2, Nadège Limousin3, Julien Biberon3, Patrick Vourc'h2, Christian R Andres2, Bertrand de Toffol3, Julien Praline3.   

Abstract

INTRODUCTION: Whether motor neuron diseases (MNDs) can be considered in some cases of paraneoplastic syndromes is controversial. We report a case of rapidly progressive motor neuronopathy following a diagnosis of breast carcinoma, with a presence of anti-Ri antibodies, and a novel SOD1 gene mutation. OBSERVATION: An 80-year-old woman with mucinous adenocarcinoma of the left breast for 4 years developed sub-acute quadriparesis. Myography revealed chronic denervation signs. The patient had serum anti-Ri onconeural antibodies. The diagnosis of paraneoplastic MND was established. Because of a familial history of ALS, a genetic analysis for familial ALS was performed. We identified a novel heterozygous mutation in SOD1 gene, SOD I18del. This mutation may reflect a genetic predisposition to develop a MND, inducing fragility of motor neurons. Neurological improvement was observed after three months of both intravenous gamma globulin and corticosteroids.
CONCLUSION: The present observation supports the idea that MND can be considered as a paraneoplastic syndrome. A combination of anti-Ri onconeural antibodies and a particular SOD1 gene mutation, consisting in risk factor, might be in cause in the process of motor neuron death. When in doubt, paraneoplastic cause should be suspected in the differential diagnosis of MND. Immunotherapy treatment may lead to a favorable outcome.
Copyright © 2013 Elsevier B.V. All rights reserved.

Entities:  

Keywords:  Amyotrophic lateral sclerosis; Genetic predisposition; Motor neuron disease; Nova antigen; Onconeuronal antibodies; Paraneoplastic syndrome; SOD1 mutations

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Year:  2013        PMID: 24296360     DOI: 10.1016/j.jns.2013.11.025

Source DB:  PubMed          Journal:  J Neurol Sci        ISSN: 0022-510X            Impact factor:   3.181


  3 in total

1.  Cerebellar dysfunction and spastic paraparesis associated to anti-Ri antibodies in a patient with a pancreatic neuroendocrine tumor.

Authors:  Abel Díaz Díaz; Miguel Hervás García; Ayoze González Hernández
Journal:  J Neurooncol       Date:  2016-09-03       Impact factor: 4.130

Review 2.  Motor neuron disease of paraneoplastic origin: a rare but treatable condition.

Authors:  Nicolas Mélé; Giulia Berzero; Thierry Maisonobe; François Salachas; Guillaume Nicolas; Nicolas Weiss; Guillemette Beaudonnet; Francois Ducray; Dimitri Psimaras; Timothée Lenglet
Journal:  J Neurol       Date:  2018-05-03       Impact factor: 4.849

3.  Paraneoplastic Amyotrophic Lateral Sclerosis: Case Series and Literature Review.

Authors:  Zhao Yang; Lu He; Manli Ren; Yizhou Lu; Huanyu Meng; Dou Yin; Sheng Chen; Qinming Zhou
Journal:  Brain Sci       Date:  2022-08-08
  3 in total

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