Literature DB >> 24201212

Birth of a new therapeutic platform: 47 years of adeno-associated virus biology from virus discovery to licensed gene therapy.

Terence R Flotte1.   

Abstract

Entities:  

Mesh：

Year:  2013        PMID： 24201212      PMCID： PMC3831048          DOI： 10.1038/mt.2013.226

Source DB:  PubMed          Journal:  Mol Ther        ISSN： 1525-0016            Impact factor:   11.454


× No keyword cloud information.
  100 in total

1.  Epidemiology of adenovirus-associated virus infection in a nursery population.

Authors:  N R Blacklow; M D Hoggan; A Z Kapikian; J B Austin; W P Rowe
Journal:  Am J Epidemiol       Date:  1968-11       Impact factor: 4.897

2.  Serologic evidence for human infection with adenovirus-associated viruses.

Authors:  N R Blacklow; M D Hoggan; W P Rowe
Journal:  J Natl Cancer Inst       Date:  1968-02       Impact factor: 13.506

3.  Isolation of adenovirus-associated viruses from man.

Authors:  N R Blacklow; M D Hoggan; W P Rowe
Journal:  Proc Natl Acad Sci U S A       Date:  1967-10       Impact factor: 11.205

4.  Evidence for a single-stranded adenovirus-associated virus genome: formation of a DNA density hybrid on release of viral DNA.

Authors:  J A Rose; K I Berns; M D Hoggan; F J Koczot
Journal:  Proc Natl Acad Sci U S A       Date:  1969-11       Impact factor: 11.205

5.  Studies of small DNA viruses found in various adenovirus preparations: physical, biological, and immunological characteristics.

Authors:  M D Hoggan; N R Blacklow; W P Rowe
Journal:  Proc Natl Acad Sci U S A       Date:  1966-06       Impact factor: 11.205

6.  Rescue of adeno-associated virus from recombinant plasmids: gene correction within the terminal repeats of AAV.

Authors:  R J Samulski; A Srivastava; K I Berns; N Muzyczka
Journal:  Cell       Date:  1983-05       Impact factor: 41.582

7.  Repeated adeno-associated virus serotype 2 aerosol-mediated cystic fibrosis transmembrane regulator gene transfer to the lungs of patients with cystic fibrosis: a multicenter, double-blind, placebo-controlled trial.

Authors:  Richard B Moss; David Rodman; L Terry Spencer; Moira L Aitken; Pamela L Zeitlin; David Waltz; Carlos Milla; Alan S Brody; John P Clancy; Bonnie Ramsey; Nicole Hamblett; Alison E Heald
Journal:  Chest       Date:  2004-02       Impact factor: 9.410

8.  Phase I trial of intramuscular injection of a recombinant adeno-associated virus alpha 1-antitrypsin (rAAV2-CB-hAAT) gene vector to AAT-deficient adults.

Authors:  Terence R Flotte; Mark L Brantly; L Terry Spencer; Barry J Byrne; Carolyn T Spencer; Dawn J Baker; Margaret Humphries
Journal:  Hum Gene Ther       Date:  2004-01       Impact factor: 5.695

9.  Cloning of infectious adeno-associated virus genomes in bacterial plasmids.

Authors:  C A Laughlin; J D Tratschin; H Coon; B J Carter
Journal:  Gene       Date:  1983-07       Impact factor: 3.688

10.  Clades of Adeno-associated viruses are widely disseminated in human tissues.

Authors:  Guangping Gao; Luk H Vandenberghe; Mauricio R Alvira; You Lu; Roberto Calcedo; Xiangyang Zhou; James M Wilson
Journal:  J Virol       Date:  2004-06       Impact factor: 5.103
View more
  9 in total

1.  Probing the Link among Genomic Cargo, Contact Mechanics, and Nanoindentation in Recombinant Adeno-Associated Virus 2.

Authors:  Cheng Zeng; Sven Moller-Tank; Aravind Asokan; Bogdan Dragnea
Journal:  J Phys Chem B       Date:  2017-02-14       Impact factor: 2.991

2.  Development of a Beta Cell-Specific Expression Control Element for Recombinant Adeno-Associated Virus.

Authors:  Sunghee Chai; Youngjin Kim; Feorillo Galivo; Craig Dorrell; Leslie Wakefield; Jeffrey Posey; Amanda M Ackermann; Klaus H Kaestner; Matthias Hebrok; Markus Grompe
Journal:  Hum Gene Ther       Date:  2022-05-10       Impact factor: 4.793

Review 3.  Durability of transgene expression after rAAV gene therapy.

Authors:  Manish Muhuri; Daniel I Levy; Martin Schulz; Douglas McCarty; Guangping Gao
Journal:  Mol Ther       Date:  2022-03-10       Impact factor: 12.910

Review 4.  State-of-the-art human gene therapy: part I. Gene delivery technologies.

Authors:  Dan Wang; Guangping Gao
Journal:  Discov Med       Date:  2014 Jul-Aug       Impact factor: 2.970

5.  The cardiac microenvironment uses non-canonical WNT signaling to activate monocytes after myocardial infarction.

Authors:  Ingmar Sören Meyer; Andreas Jungmann; Christoph Dieterich; Min Zhang; Felix Lasitschka; Susann Werkmeister; Jan Haas; Oliver J Müller; Michael Boutros; Matthias Nahrendorf; Hugo A Katus; Stefan E Hardt; Florian Leuschner
Journal:  EMBO Mol Med       Date:  2017-09       Impact factor: 12.137

6.  Adenovirus-Mediated Gene Delivery: Potential Applications for Gene and Cell-Based Therapies in the New Era of Personalized Medicine.

Authors:  Cody S Lee; Elliot S Bishop; Ruyi Zhang; Xinyi Yu; Evan M Farina; Shujuan Yan; Chen Zhao; Zongyue Zheng; Yi Shu; Xingye Wu; Jiayan Lei; Yasha Li; Wenwen Zhang; Chao Yang; Ke Wu; Ying Wu; Sherwin Ho; Aravind Athiviraham; Michael J Lee; Jennifer Moriatis Wolf; Russell R Reid; Tong-Chuan He
Journal:  Genes Dis       Date:  2017-04-27

7.  Genome-wide RNAi screening identifies host restriction factors critical for in vivo AAV transduction.

Authors:  Miguel Mano; Rudy Ippodrino; Lorena Zentilin; Serena Zacchigna; Mauro Giacca
Journal:  Proc Natl Acad Sci U S A       Date:  2015-08-24       Impact factor: 11.205

8.  CRISPR/Cas9-Mediated Genome Editing of Herpesviruses Limits Productive and Latent Infections.

Authors:  Ferdy R van Diemen; Elisabeth M Kruse; Marjolein J G Hooykaas; Carlijn E Bruggeling; Anita C Schürch; Petra M van Ham; Saskia M Imhof; Monique Nijhuis; Emmanuel J H J Wiertz; Robert Jan Lebbink
Journal:  PLoS Pathog       Date:  2016-06-30       Impact factor: 6.823

9.  CNS-restricted Transduction and CRISPR/Cas9-mediated Gene Deletion with an Engineered AAV Vector.

Authors:  Giridhar Murlidharan; Kensuke Sakamoto; Lavanya Rao; Travis Corriher; Dan Wang; Guangping Gao; Patrick Sullivan; Aravind Asokan
Journal:  Mol Ther Nucleic Acids       Date:  2016-07-19       Impact factor: 10.183
  9 in total

北京卡尤迪生物科技股份有限公司 © 2022-2023.