Literature DB >> 24189171

Sorafenib does not improve efficacy of chemotherapy in advanced pancreatic cancer: A GISCAD randomized phase II study.

Stefano Cascinu1, Rossana Berardi2, Alberto Sobrero3, Paolo Bidoli4, Roberto Labianca5, Salvatore Siena6, Daris Ferrari7, Sandro Barni8, Enrico Aitini9, Vittorina Zagonel10, Francesco Caprioni3, Federica Villa4, Stefania Mosconi5, Luca Faloppi2, Giuseppe Tonini11, Corrado Boni12, Pierfranco Conte13, Francesco Di Costanzo14, Michela Cinquini15.   

Abstract

BACKGROUND: The RAF-MEK-ERK pathway is commonly activated in pancreatic cancer because of a high frequency of KRAS-BRAF mutations. A phase II randomized trial was designed to investigate the activity of sorafenib in combination with chemotherapy in advanced pancreatic cancer.
METHODS: Locally advanced or metastatic pancreatic adenocarcinoma patients were randomized in a 1:1 ratio to receive cisplatin plus gemcitabine with sorafenib 400mg bid (arm A) or without sorafenib (arm B).
RESULTS: One hundred and fourteen patients were enrolled; of these, 43 (74.6%) patients progressed in arm A and 44 (82.4%) in arm B. Median progression-free survival was 4.3 months (95% CI: 2.7-6.5) and 4.5 months (95% CI: 2.5-5.2), respectively (HR=0.92; 95% CI: 0.62-1.35). Median overall survival was 7.5 (95% CI: 5.6-9.7) and 8.3 months (95% CI: 6.2-8.7), respectively (HR=0.95; 95% CI: 0.62-1.48). Response rates were 3.4% in arm A and 3.6% in arm B.
CONCLUSIONS: Sorafenib does not significantly enhance activity of chemotherapy in advanced pancreatic cancer patients, and therefore should not be assessed in phase III trials.
Copyright © 2013 Editrice Gastroenterologica Italiana S.r.l. Published by Elsevier Ltd. All rights reserved.

Entities:  

Keywords:  Cisplatin; Gemcitabine; Pancreatic cancer; Phase II study; Sorafenib

Mesh:

Substances:

Year:  2013        PMID: 24189171     DOI: 10.1016/j.dld.2013.09.020

Source DB:  PubMed          Journal:  Dig Liver Dis        ISSN: 1590-8658            Impact factor:   4.088


  14 in total

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8.  The value of lactate dehydrogenase serum levels as a prognostic and predictive factor for advanced pancreatic cancer patients receiving sorafenib.

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