Literature DB >> 24042093

Clinical and genetic features of hearing loss in facioscapulohumeral muscular dystrophy.

Katie L Lutz1, Lenore Holte, Stephanie A Kliethermes, Carrie Stephan, Katherine D Mathews.   

Abstract

OBJECTIVE: To describe the hearing loss in facioscapulohumeral muscular dystrophy (FSHD) and examine the relationship to genotype.
METHODS: Medical records of all individuals with FSHD seen at the University of Iowa neuromuscular clinic between July 2006 and July 2012 (n = 59) were reviewed. Eleven had significant hearing loss and no non-FSHD cause. All available audiology records for these individuals were analyzed. The relationship between the FSHD mutation (EcoRI/BlnI fragment size) and hearing loss was evaluated using a logistic regression analysis.
RESULTS: In patients with hearing loss, recalled age at onset of facial weakness ranged from birth to 5 years and shoulder weakness was 3 to 15 years. The age at diagnosis of hearing loss ranged from birth to 7 years. Only 2 were identified by newborn hearing screen. Most audiograms demonstrated a bilateral, sloping, high-frequency sensorineural hearing loss. Of the 4 patients with more than 5 years of data, 3 had progression of hearing loss. Logistic regression showed statistically significant negative association between the presence of hearing loss and EcoRI/BlnI fragment size (p = 0.0207).
CONCLUSIONS: FSHD with a small EcoRI/BlnI fragment is associated with a bilateral, progressive, sloping, high-frequency hearing loss with onset in childhood. Patients with FSHD and small EcoRI/BlnI fragment sizes should have hearing screened, even if the child passed newborn hearing screening.

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Year:  2013        PMID: 24042093      PMCID: PMC3806909          DOI: 10.1212/WNL.0b013e3182a84140

Source DB:  PubMed          Journal:  Neurology        ISSN: 0028-3878            Impact factor:   9.910


  5 in total

1.  Unusual clinical presentations in patients harboring the facioscapulohumeral dystrophy 4q35 deletion.

Authors:  K J Felice; S A Moore
Journal:  Muscle Nerve       Date:  2001-03       Impact factor: 3.217

2.  171st ENMC international workshop: Standards of care and management of facioscapulohumeral muscular dystrophy.

Authors:  Rabi Tawil; Silvere van der Maarel; George W Padberg; Baziel G M van Engelen
Journal:  Neuromuscul Disord       Date:  2010-07       Impact factor: 4.296

3.  Hearing loss in facioscapulohumeral dystrophy.

Authors:  T Voit; A Lamprecht; H G Lenard; H H Goebel
Journal:  Eur J Pediatr       Date:  1986-09       Impact factor: 3.183

4.  Coats-like retinopathy in an infant with preclinical facioscapulohumeral dystrophy.

Authors:  Anuradha Ganesh; Swathi Kaliki; Carol L Shields
Journal:  J AAPOS       Date:  2012-04       Impact factor: 1.220

5.  Coats syndrome in facioscapulohumeral dystrophy type 1: frequency and D4Z4 contraction size.

Authors:  Jeffrey M Statland; Sabrina Sacconi; Constantine Farmakidis; Colleen M Donlin-Smith; Mina Chung; Rabi Tawil
Journal:  Neurology       Date:  2013-02-27       Impact factor: 9.910

  5 in total
  21 in total

Review 1.  Facioscapulohumeral Muscular Dystrophy.

Authors:  Jeffrey M Statland; Rabi Tawil
Journal:  Continuum (Minneap Minn)       Date:  2016-12

2.  Dynamic transcriptomic analysis reveals suppression of PGC1α/ERRα drives perturbed myogenesis in facioscapulohumeral muscular dystrophy.

Authors:  Christopher R S Banerji; Maryna Panamarova; Johanna Pruller; Nicolas Figeac; Husam Hebaishi; Efthymios Fidanis; Alka Saxena; Julian Contet; Sabrina Sacconi; Simone Severini; Peter S Zammit
Journal:  Hum Mol Genet       Date:  2019-04-15       Impact factor: 6.150

Review 3.  Facioscapulohumeral Dystrophy.

Authors:  Leo H Wang; Rabi Tawil
Journal:  Curr Neurol Neurosci Rep       Date:  2016-07       Impact factor: 5.081

4.  Dominant lethal pathologies in male mice engineered to contain an X-linked DUX4 transgene.

Authors:  Abhijit Dandapat; Darko Bosnakovski; Lynn M Hartweck; Robert W Arpke; Kristen A Baltgalvis; Derek Vang; June Baik; Radbod Darabi; Rita C R Perlingeiro; F Kent Hamra; Kalpna Gupta; Dawn A Lowe; Michael Kyba
Journal:  Cell Rep       Date:  2014-08-28       Impact factor: 9.423

Review 5.  Facioscapulohumeral muscular dystrophy.

Authors:  Jeffrey Statland; Rabi Tawil
Journal:  Neurol Clin       Date:  2014-05-15       Impact factor: 3.806

6.  Milder phenotype in facioscapulohumeral dystrophy with 7-10 residual D4Z4 repeats.

Authors:  Jeffrey M Statland; Colleen M Donlin-Smith; Stephen J Tapscott; Richard J L F Lemmers; Silvère M van der Maarel; Rabi Tawil
Journal:  Neurology       Date:  2015-11-11       Impact factor: 9.910

Review 7.  Facioscapulohumeral dystrophy: activating an early embryonic transcriptional program in human skeletal muscle.

Authors:  Amy E Campbell; Andrea E Belleville; Rebecca Resnick; Sean C Shadle; Stephen J Tapscott
Journal:  Hum Mol Genet       Date:  2018-08-01       Impact factor: 6.150

8.  Facioscapulohumeral dystrophy in children: design of a prospective, observational study on natural history, predictors and clinical impact (iFocus FSHD).

Authors:  Rianne J M Goselink; Tim H A Schreuder; Karlien Mul; Nicol C Voermans; Maaike Pelsma; Imelda J M de Groot; Nens van Alfen; Bas Franck; Thomas Theelen; Richard J Lemmers; Jean K Mah; Silvère M van der Maarel; Baziel G van Engelen; Corrie E Erasmus
Journal:  BMC Neurol       Date:  2016-08-17       Impact factor: 2.474

Review 9.  Facioscapulohumeral dystrophy: the path to consensus on pathophysiology.

Authors:  Rabi Tawil; Silvère M van der Maarel; Stephen J Tapscott
Journal:  Skelet Muscle       Date:  2014-06-10       Impact factor: 4.912

10.  High Frequency Hearing Loss and Hyperactivity in DUX4 Transgenic Mice.

Authors:  Abhijit Dandapat; Benjamin J Perrin; Christine Cabelka; Maria Razzoli; James M Ervasti; Alessandro Bartolomucci; Dawn A Lowe; Michael Kyba
Journal:  PLoS One       Date:  2016-03-15       Impact factor: 3.240

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