Monica Hoyos Flight. Show Affiliations »
Abstract
Mesh: See more » Clinical Trials, Phase I as TopicClinical Trials, Phase II as TopicGenetic Therapy/methodsGenetic VectorsHematopoietic Stem Cell Transplantation/methodsHumansLentivirus/geneticsLeukodystrophy, Metachromatic/geneticsLeukodystrophy, Metachromatic/therapyWiskott-Aldrich Syndrome/geneticsWiskott-Aldrich Syndrome/therapy
Year: 2013 PMID: 23989781 DOI: 10.1038/nrd4111
Source DB: PubMed Journal: Nat Rev Drug Discov ISSN: 1474-1776 Impact factor: 84.694