Literature DB >> 23789807

[Treatment with cyclodextrin for Niemann Pick s disease].

Sonia Cruz-Pardos, Patricia García-Poza, Francisco-Javier Sánchez-García.   

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Year:  2013        PMID: 23789807     DOI: 10.7399/FH.2013.37.1.66

Source DB:  PubMed          Journal:  Farm Hosp        ISSN: 1130-6343


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  3 in total

Review 1.  Early experience with compassionate use of 2 hydroxypropyl-beta-cyclodextrin for Niemann-Pick type C disease: review of initial published cases.

Authors:  Juan Eduardo Megías-Vericat; Ana García-Robles; María José Company-Albir; María José Fernández-Megía; Francisco Carlos Pérez-Miralles; Eduardo López-Briz; Bonaventura Casanova; José Luis Poveda
Journal:  Neurol Sci       Date:  2017-02-02       Impact factor: 3.307

Review 2.  The Extending Spectrum of NPC1-Related Human Disorders: From Niemann-Pick C1 Disease to Obesity.

Authors:  Amel Lamri; Marie Pigeyre; William S Garver; David Meyre
Journal:  Endocr Rev       Date:  2018-04-01       Impact factor: 19.871

3.  Intrathecal cyclodextrin in the treatment of Niemann-Pick disease type C.

Authors:  Maria Roch Santed; Maria Josep Cabañas Poy; Mireia Del Toro Riera; Carme Cañete Ramírez; Aurora Fernández Polo; Susana Clemente Bautista
Journal:  Eur J Hosp Pharm       Date:  2016-11-04
  3 in total

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