Literature DB >> 23569001

Tafamidis for transthyretin familial amyloid polyneuropathy: a randomized, controlled trial.

Ingemar S J Merkies.   

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Year:  2013        PMID: 23569001     DOI: 10.1212/01.wnl.0000429338.33391.87

Source DB:  PubMed          Journal:  Neurology        ISSN: 0028-3878            Impact factor:   9.910


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  5 in total

Review 1.  Systemic amyloidosis: moving into the spotlight.

Authors:  Oliver C Cohen; Ashutosh D Wechalekar
Journal:  Leukemia       Date:  2020-04-09       Impact factor: 11.528

2.  Muscle quantitative MRI as a novel biomarker in hereditary transthyretin amyloidosis with polyneuropathy: a cross-sectional study.

Authors:  Elisa Vegezzi; Andrea Cortese; Laura Obici; Anna Pichiecchio; Niels Bergsland; Roberta Mussinelli; Matteo Paoletti; Francesca Solazzo; Riccardo Currò; Lucia Ascagni; Ilaria Callegari; Ilaria Quartesan; Alessandro Lozza; Xeni Deligianni; Francesco Santini; Enrico Marchioni; Giuseppe Cosentino; Enrico Alfonsi; Cristina Tassorelli; Stefano Bastianello; Giampaolo Merlini; Giovanni Palladini
Journal:  J Neurol       Date:  2022-09-06       Impact factor: 6.682

3.  Repositioning tolcapone as a potent inhibitor of transthyretin amyloidogenesis and associated cellular toxicity.

Authors:  Ricardo Sant'Anna; Pablo Gallego; Lei Z Robinson; Alda Pereira-Henriques; Nelson Ferreira; Francisca Pinheiro; Sebastian Esperante; Irantzu Pallares; Oscar Huertas; Maria Rosário Almeida; Natàlia Reixach; Raul Insa; Adrian Velazquez-Campoy; David Reverter; Núria Reig; Salvador Ventura
Journal:  Nat Commun       Date:  2016-02-23       Impact factor: 14.919

4.  Green tea extract as a treatment for patients with wild-type transthyretin amyloidosis: an observational study.

Authors:  Fabian aus dem Siepen; Ralf Bauer; Matthias Aurich; Sebastian J Buss; Henning Steen; Klaus Altland; Hugo A Katus; Arnt V Kristen
Journal:  Drug Des Devel Ther       Date:  2015-12-04       Impact factor: 4.162

5.  Biophysical characterization and modulation of Transthyretin Ala97Ser.

Authors:  Yo-Tsen Liu; Yueh-Jung Yen; Frans Ricardo; Yu Chang; Pei-Hao Wu; Shing-Jong Huang; Kon-Ping Lin; Tsyr-Yan Yu
Journal:  Ann Clin Transl Neurol       Date:  2019-09-10       Impact factor: 4.511

  5 in total

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