Literature DB >> 23467559

Seeing the light.

Adam P Wojno1, Eric A Pierce, Jean Bennett.   

Abstract

One-time gene therapy resulted in multiyear visual improvement, and new approaches were used to evaluate effects on retinal structure.

Mesh：

Year:  2013        PMID： 23467559     DOI： 10.1126/scitranslmed.3005798

Source DB:  PubMed          Journal:  Sci Transl Med        ISSN： 1946-6234            Impact factor:   17.956


  13 in total

Review 1.  What Is Next for Retinal Gene Therapy?

Authors:  Luk H Vandenberghe
Journal:  Cold Spring Harb Perspect Med       Date:  2015-04-15       Impact factor: 6.915

Review 2.  The Status of RPE65 Gene Therapy Trials: Safety and Efficacy.

Authors:  Eric A Pierce; Jean Bennett
Journal:  Cold Spring Harb Perspect Med       Date:  2015-01-29       Impact factor: 6.915

3.  My career path for developing gene therapy for blinding diseases: the importance of mentors, collaborators, and opportunities.

Authors:  Jean Bennett
Journal:  Hum Gene Ther       Date:  2014-08       Impact factor: 5.695

4.  Long-Term Structural Outcomes of Late-Stage RPE65 Gene Therapy.

Authors:  Kristin L Gardiner; Artur V Cideciyan; Malgorzata Swider; Valérie L Dufour; Alexander Sumaroka; András M Komáromy; William W Hauswirth; Simone Iwabe; Samuel G Jacobson; William A Beltran; Gustavo D Aguirre
Journal:  Mol Ther       Date:  2019-09-03       Impact factor: 11.454

5.  Synthetic Adeno-Associated Viral Vector Efficiently Targets Mouse and Nonhuman Primate Retina In Vivo.

Authors:  Livia S Carvalho; Ru Xiao; Sarah J Wassmer; Aliete Langsdorf; Eric Zinn; Simon Pacouret; Samiksha Shah; Jason I Comander; Leo A Kim; Laurence Lim; Luk H Vandenberghe
Journal:  Hum Gene Ther       Date:  2018-03-20       Impact factor: 5.695

Review 6.  Personalized therapeutic strategies for patients with retinitis pigmentosa.

Authors:  Andrew Zheng; Yao Li; Stephen H Tsang
Journal:  Expert Opin Biol Ther       Date:  2015-01-23       Impact factor: 4.388

Review 7.  Promising and delivering gene therapies for vision loss.

Authors:  Livia S Carvalho; Luk H Vandenberghe
Journal:  Vision Res       Date:  2014-08-02       Impact factor: 1.886

8.  "Is a cure in my sight?" Multi-stakeholder perspectives on phase I choroideremia gene transfer clinical trials.

Authors:  Shelly Benjaminy; Ian Macdonald; Tania Bubela
Journal:  Genet Med       Date:  2013-09-26       Impact factor: 8.822

9.  Concepts and Strategies in Retinal Gene Therapy.

Authors:  Gustavo D Aguirre
Journal:  Invest Ophthalmol Vis Sci       Date:  2017-10-01       Impact factor: 4.799

Review 10.  Genetically Engineering the Nervous System with CRISPR-Cas.

Authors:  Alfredo Sandoval; Hajira Elahi; Jonathan E Ploski
Journal:  eNeuro       Date:  2020-03-25
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