Literature DB >> 22344719

Cyclodextrin-based iminosugar click clusters: the first examples of multivalent pharmacological chaperones for the treatment of lysosomal storage disorders.

Camille Decroocq1, David Rodríguez-Lucena, Kyoko Ikeda, Naoki Asano, Philippe Compain.   

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Year:  2012        PMID: 22344719     DOI: 10.1002/cbic.201200005

Source DB:  PubMed          Journal:  Chembiochem        ISSN: 1439-4227            Impact factor:   3.164


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  7 in total

1.  Design, synthesis and photochemical properties of the first examples of iminosugar clusters based on fluorescent cores.

Authors:  Mathieu L Lepage; Antoine Mirloup; Manon Ripoll; Fabien Stauffert; Anne Bodlenner; Raymond Ziessel; Philippe Compain
Journal:  Beilstein J Org Chem       Date:  2015-05-06       Impact factor: 2.883

Review 2.  Pharmacological Chaperone Therapy for Pompe Disease.

Authors:  Marc Borie-Guichot; My Lan Tran; Yves Génisson; Stéphanie Ballereau; Cécile Dehoux
Journal:  Molecules       Date:  2021-11-29       Impact factor: 4.411

Review 3.  GCase Enhancers: A Potential Therapeutic Option for Gaucher Disease and Other Neurological Disorders.

Authors:  Macarena Martínez-Bailén; Francesca Clemente; Camilla Matassini; Francesca Cardona
Journal:  Pharmaceuticals (Basel)       Date:  2022-07-02

4.  Synthesis of the first examples of iminosugar clusters based on cyclopeptoid cores.

Authors:  Mathieu L Lepage; Alessandra Meli; Anne Bodlenner; Céline Tarnus; Francesco De Riccardis; Irene Izzo; Philippe Compain
Journal:  Beilstein J Org Chem       Date:  2014-06-23       Impact factor: 2.883

5.  Exploring architectures displaying multimeric presentations of a trihydroxypiperidine iminosugar.

Authors:  Camilla Matassini; Stefania Mirabella; Andrea Goti; Inmaculada Robina; Antonio J Moreno-Vargas; Francesca Cardona
Journal:  Beilstein J Org Chem       Date:  2015-12-16       Impact factor: 2.883

Review 6.  Synthesis and Therapeutic Applications of Iminosugars in Cystic Fibrosis.

Authors:  Anna Esposito; Daniele D'Alonzo; Maria De Fenza; Eliana De Gregorio; Anna Tamanini; Giuseppe Lippi; Maria Cristina Dechecchi; Annalisa Guaragna
Journal:  Int J Mol Sci       Date:  2020-05-09       Impact factor: 5.923

7.  3,4,5-Trihydroxypiperidine Based Multivalent Glucocerebrosidase (GCase) Enhancers.

Authors:  Costanza Vanni; Francesca Clemente; Paolo Paoli; Amelia Morrone; Camilla Matassini; Andrea Goti; Francesca Cardona
Journal:  Chembiochem       Date:  2022-04-07       Impact factor: 3.461

  7 in total

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