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Literature DB >> 22183336

Suppression of rds expression by siRNA and gene replacement strategies for gene therapy using rAAV vector.

Hilda Petrs-Silva¹, Douglas Yasumura, Michael T Matthes, Matthew M LaVail, Alfred S Lewin, William W Hauswirth.

Abstract

Entities: CellLine Chemical Disease Gene Species

Mesh：

Substances：

Year: 2012 PMID： 22183336 PMCID： PMC3556273 DOI： 10.1007/978-1-4614-0631-0_29

Source DB: PubMed Journal: Adv Exp Med Biol ISSN： 0065-2598 Impact factor: 2.622

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Review 3. Retinitis pigmentosa.

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5. Peripherin/rds influences membrane vesicle morphology. Implications for retinopathies.

Authors: J D Wrigley; T Ahmed; C L Nevett; J B Findlay
Journal: J Biol Chem Date: 2000-05-05 Impact factor: 5.157

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Authors: G M Sarra; C Stephens; M de Alwis; J W Bainbridge; A J Smith; A J Thrasher; R R Ali
Journal: Hum Mol Genet Date: 2001-10-01 Impact factor: 6.150

7. Restoration of photoreceptor ultrastructure and function in retinal degeneration slow mice by gene therapy.

Authors: R R Ali; G M Sarra; C Stephens; M D Alwis; J W Bainbridge; P M Munro; S Fauser; M B Reichel; C Kinnon; D M Hunt; S S Bhattacharya; A J Thrasher
Journal: Nat Genet Date: 2000-07 Impact factor: 38.330

8. Retinal degeneration slow (rds) in mouse results from simple insertion of a t haplotype-specific element into protein-coding exon II.

Authors: J Ma; J C Norton; A C Allen; J B Burns; K W Hasel; J L Burns; J G Sutcliffe; G H Travis
Journal: Genomics Date: 1995-07-20 Impact factor: 5.736

9. Association of a novel mutation in the retinol dehydrogenase 12 (RDH12) gene with autosomal dominant retinitis pigmentosa.

Authors: John H Fingert; Kean Oh; Mina Chung; Todd E Scheetz; Jeaneen L Andorf; Rebecca M Johnson; Val C Sheffield; Edwin M Stone
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10. Long-term evaluation of retinal function in Prph2Rd2/Rd2 mice following AAV-mediated gene replacement therapy.

Authors: Frank C Schlichtenbrede; Lyndon da Cruz; Clare Stephens; Alexander J Smith; Anastasios Georgiadis; Adrian J Thrasher; James W B Bainbridge; Mathias W Seeliger; Robin R Ali
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Review 2. Small-interfering RNAs (siRNAs) as a promising tool for ocular therapy.

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Review 4. Non-viral therapeutic approaches to ocular diseases: An overview and future directions.

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