Literature DB >> 22183334

Gene delivery of wild-type rhodopsin rescues retinal function in an autosomal dominant retinitis pigmentosa mouse model.

Haoyu Mao1, Marina S Gorbatyuk, William W Hauswirth, Alfred S Lewin.   

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Year:  2012        PMID： 22183334      PMCID： PMC3392039          DOI： 10.1007/978-1-4614-0631-0_27

Source DB:  PubMed          Journal:  Adv Exp Med Biol        ISSN： 0065-2598            Impact factor:   2.622


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  28 in total

Review 1.  Perspective on genes and mutations causing retinitis pigmentosa.

Authors:  Stephen P Daiger; Sara J Bowne; Lori S Sullivan
Journal:  Arch Ophthalmol       Date:  2007-02

2.  Gene therapy for mouse models of ADRP.

Authors:  Marina S Gorbatyuk; William W Hauswirth; Alfred S Lewin
Journal:  Adv Exp Med Biol       Date:  2008       Impact factor: 2.622

3.  Characterization of rhodopsin P23H-induced retinal degeneration in a Xenopus laevis model of retinitis pigmentosa.

Authors:  Beatrice M Tam; Orson L Moritz
Journal:  Invest Ophthalmol Vis Sci       Date:  2006-08       Impact factor: 4.799

4.  Knockdown of wild-type mouse rhodopsin using an AAV vectored ribozyme as part of an RNA replacement approach.

Authors:  M S Gorbatyuk; J J Pang; J Thomas; William W Hauswirth; Alfred S Lewin
Journal:  Mol Vis       Date:  2005-08-29       Impact factor: 2.367

5.  Suppression of mouse rhodopsin expression in vivo by AAV mediated siRNA delivery.

Authors:  M Gorbatyuk; V Justilien; J Liu; W W Hauswirth; A S Lewin
Journal:  Vision Res       Date:  2007-02-12       Impact factor: 1.886

6.  Preservation of photoreceptor morphology and function in P23H rats using an allele independent ribozyme.

Authors:  M Gorbatyuk; V Justilien; J Liu; W W Hauswirth; A S Lewin
Journal:  Exp Eye Res       Date:  2006-11-01       Impact factor: 3.467

7.  AAV-mediated knockdown of peripherin-2 in vivo using miRNA-based hairpins.

Authors:  A Georgiadis; M Tschernutter; J W B Bainbridge; S J Robbie; J McIntosh; A C Nathwani; A J Smith; R R Ali
Journal:  Gene Ther       Date:  2009-12-10       Impact factor: 5.250

8.  Effect of gene therapy on visual function in Leber's congenital amaurosis.

Authors:  James W B Bainbridge; Alexander J Smith; Susie S Barker; Scott Robbie; Robert Henderson; Kamaljit Balaggan; Ananth Viswanathan; Graham E Holder; Andrew Stockman; Nick Tyler; Simon Petersen-Jones; Shomi S Bhattacharya; Adrian J Thrasher; Fred W Fitzke; Barrie J Carter; Gary S Rubin; Anthony T Moore; Robin R Ali
Journal:  N Engl J Med       Date:  2008-04-27       Impact factor: 91.245

9.  Human RPE65 gene therapy for Leber congenital amaurosis: persistence of early visual improvements and safety at 1 year.

Authors:  Artur V Cideciyan; William W Hauswirth; Tomas S Aleman; Shalesh Kaushal; Sharon B Schwartz; Sanford L Boye; Elizabeth A M Windsor; Thomas J Conlon; Alexander Sumaroka; Ji-Jing Pang; Alejandro J Roman; Barry J Byrne; Samuel G Jacobson
Journal:  Hum Gene Ther       Date:  2009-09       Impact factor: 5.695

10.  Gene therapy for Leber's congenital amaurosis is safe and effective through 1.5 years after vector administration.

Authors:  Francesca Simonelli; Albert M Maguire; Francesco Testa; Eric A Pierce; Federico Mingozzi; Jeannette L Bennicelli; Settimio Rossi; Kathleen Marshall; Sandro Banfi; Enrico M Surace; Junwei Sun; T Michael Redmond; Xiaosong Zhu; Kenneth S Shindler; Gui-Shuang Ying; Carmela Ziviello; Carmela Acerra; J Fraser Wright; Jennifer Wellman McDonnell; Katherine A High; Jean Bennett; Alberto Auricchio
Journal:  Mol Ther       Date:  2009-12-01       Impact factor: 11.454
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  1 in total

Review 1.  Use of human pluripotent stem cells to study and treat retinopathies.

Authors:  Karim Ben M'Barek; Florian Regent; Christelle Monville
Journal:  World J Stem Cells       Date:  2015-04-26       Impact factor: 5.326
  1 in total

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