Literature DB >> 22051598

AAV vector biology in primates: finding the missing link?

Roland W Herzog, Andrew M Davidoff, David M Markusic, Amit C Nathwani.   

Abstract

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Year:  2011        PMID： 22051598      PMCID： PMC3222536          DOI： 10.1038/mt.2011.218

Source DB:  PubMed          Journal:  Mol Ther        ISSN： 1525-0016            Impact factor:   11.454


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  13 in total

1.  AAV8-mediated hepatic gene transfer in infant rhesus monkeys (Macaca mulatta).

Authors:  Lili Wang; Peter Bell; Jianping Lin; Roberto Calcedo; Alice F Tarantal; James M Wilson
Journal:  Mol Ther       Date:  2011-08-02       Impact factor: 11.454

2.  The pleiotropic effects of natural AAV infections on liver-directed gene transfer in macaques.

Authors:  Lili Wang; Roberto Calcedo; Huan Wang; Peter Bell; Rebecca Grant; Luk H Vandenberghe; Julio Sanmiguel; Hiroki Morizono; Mark L Batshaw; James M Wilson
Journal:  Mol Ther       Date:  2009-11-03       Impact factor: 11.454

3.  Hemophilia gene therapy: a Holy Grail found.

Authors:  Katherine P Ponder
Journal:  Mol Ther       Date:  2011-03       Impact factor: 11.454

4.  Preexisting immunity and low expression in primates highlight translational challenges for liver-directed AAV8-mediated gene therapy.

Authors:  Gregory D Hurlbut; Robin J Ziegler; Jennifer B Nietupski; Joseph W Foley; Lisa A Woodworth; Elizabeth Meyers; Scott D Bercury; Nilesh N Pande; David W Souza; Mark P Bree; Michael J Lukason; John Marshall; Seng H Cheng; Ronald K Scheule
Journal:  Mol Ther       Date:  2010-08-24       Impact factor: 11.454

5.  Systemic administration of AAV8-α-galactosidase A induces humoral tolerance in nonhuman primates despite low hepatic expression.

Authors:  Jennifer B Nietupski; Gregory D Hurlbut; Robin J Ziegler; Qiuming Chu; Bradley L Hodges; Karen M Ashe; Mark Bree; Seng H Cheng; Richard J Gregory; John Marshall; Ronald K Scheule
Journal:  Mol Ther       Date:  2011-06-28       Impact factor: 11.454

6.  Capsid-specific T-cell responses to natural infections with adeno-associated viruses in humans differ from those of nonhuman primates.

Authors:  Hua Li; Marcio O Lasaro; Bei Jia; Shih Wen Lin; Larissa H Haut; Katherine A High; Hildegund C J Ertl
Journal:  Mol Ther       Date:  2011-05-17       Impact factor: 11.454

Review 7.  Gene therapy for haemophilia: a long and winding road.

Authors:  K A High
Journal:  J Thromb Haemost       Date:  2011-07       Impact factor: 5.824

8.  Long-term safety and efficacy following systemic administration of a self-complementary AAV vector encoding human FIX pseudotyped with serotype 5 and 8 capsid proteins.

Authors:  Amit C Nathwani; Cecilia Rosales; Jenny McIntosh; Ghasem Rastegarlari; Devhrut Nathwani; Deepak Raj; Sushmita Nawathe; Simon N Waddington; Roderick Bronson; Scott Jackson; Robert E Donahue; Katherine A High; Federico Mingozzi; Catherine Y C Ng; Junfang Zhou; Yunyu Spence; M Beth McCarville; Marc Valentine; James Allay; John Coleman; Susan Sleep; John T Gray; Arthur W Nienhuis; Andrew M Davidoff
Journal:  Mol Ther       Date:  2011-01-18       Impact factor: 11.454

9.  Stable human FIX expression after 0.9G intrauterine gene transfer of self-complementary adeno-associated viral vector 5 and 8 in macaques.

Authors:  Citra N Z Mattar; Amit C Nathwani; Simon N Waddington; Niraja Dighe; Christine Kaeppel; Ali Nowrouzi; Jenny Mcintosh; Nuryanti B Johana; Bryan Ogden; Nicholas M Fisk; Andrew M Davidoff; Anna David; Donald Peebles; Marcus B Valentine; Jens-Uwe Appelt; Christof von Kalle; Manfred Schmidt; Arijit Biswas; Mahesh Choolani; Jerry K Y Chan
Journal:  Mol Ther       Date:  2011-05-31       Impact factor: 11.454

10.  Safe and efficient transduction of the liver after peripheral vein infusion of self-complementary AAV vector results in stable therapeutic expression of human FIX in nonhuman primates.

Authors:  Amit C Nathwani; John T Gray; Jenny McIntosh; Catherine Y C Ng; Junfang Zhou; Yunyu Spence; Melanie Cochrane; Elaine Gray; Edward G D Tuddenham; Andrew M Davidoff
Journal:  Blood       Date:  2006-11-07       Impact factor: 22.113
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  4 in total

1.  Covert warfare against the immune system: decoy capsids, stealth genomes, and suppressors.

Authors:  Brad E Hoffman; Roland W Herzog
Journal:  Mol Ther       Date:  2013-09       Impact factor: 11.454

Review 2.  Delivery technologies for genome editing.

Authors:  Hao Yin; Kevin J Kauffman; Daniel G Anderson
Journal:  Nat Rev Drug Discov       Date:  2017-03-24       Impact factor: 84.694

3.  Long-term efficacy following readministration of an adeno-associated virus vector in dogs with glycogen storage disease type Ia.

Authors:  Amanda Demaster; Xiaoyan Luo; Sarah Curtis; Kyha D Williams; Dustin J Landau; Elizabeth J Drake; Daniel M Kozink; Andrew Bird; Bayley Crane; Francis Sun; Carlos R Pinto; Talmage T Brown; Alex R Kemper; Dwight D Koeberl
Journal:  Hum Gene Ther       Date:  2012-03-08       Impact factor: 5.695

4.  Therapeutic levels of FVIII following a single peripheral vein administration of rAAV vector encoding a novel human factor VIII variant.

Authors:  Jenny McIntosh; Peter J Lenting; Cecilia Rosales; Doyoung Lee; Samira Rabbanian; Deepak Raj; Nishil Patel; Edward G D Tuddenham; Olivier D Christophe; John H McVey; Simon Waddington; Arthur W Nienhuis; John T Gray; Paolo Fagone; Federico Mingozzi; Shang-Zhen Zhou; Katherine A High; Maria Cancio; Catherine Y C Ng; Junfang Zhou; Christopher L Morton; Andrew M Davidoff; Amit C Nathwani
Journal:  Blood       Date:  2013-02-20       Impact factor: 22.113
  4 in total

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