Literature DB >> 22028225

Prevalence of congenital myopathies in a representative pediatric united states population.

Kimberly Amburgey1, Nancy McNamara, Lindsey R Bennett, M Eileen McCormick, Gyula Acsadi, James J Dowling.   

Abstract

The prevalence of congenital myopathies in the United States has not been examined. To address this, we determined the point prevalence of congenital myopathies in a well-defined pediatric population from Southeastern Michigan. The overall point prevalence was 1:26,000. Mutations in RYR1 were the most common cause of congenital myopathies at 1:90,000. Our data broadly agrees with estimates from previous European studies and provides the first estimate of the prevalence of congenital myopathies in the United States. Ann Neurol 2011;70:662-665.
Copyright © 2011 American Neurological Association.

Entities:  

Mesh:

Substances:

Year:  2011        PMID: 22028225     DOI: 10.1002/ana.22510

Source DB:  PubMed          Journal:  Ann Neurol        ISSN: 0364-5134            Impact factor:   10.422


  53 in total

1.  Understanding Symptoms in RYR1-Related Myopathies: A Mixed-Methods Analysis Based on Participants' Experience.

Authors:  Carlos Capella-Peris; Mary M Cosgrove; Irene C Chrismer; M Sonia Razaqyar; Jeffrey S Elliott; Anna Kuo; Magalie Emile-Backer; Katherine G Meilleur
Journal:  Patient       Date:  2020-08       Impact factor: 3.883

2.  Clinical utility gene card for: Centronuclear and myotubular myopathies.

Authors:  Valérie Biancalana; Alan H Beggs; Soma Das; Heinz Jungbluth; Wolfram Kress; Ichizo Nishino; Kathryn North; Norma B Romero; Jocelyn Laporte
Journal:  Eur J Hum Genet       Date:  2012-05-23       Impact factor: 4.246

3.  Dominant mutation of CCDC78 in a unique congenital myopathy with prominent internal nuclei and atypical cores.

Authors:  Karen Majczenko; Ann E Davidson; Sandra Camelo-Piragua; Pankaj B Agrawal; Richard A Manfready; Xingli Li; Sucheta Joshi; Jishu Xu; Weiping Peng; Alan H Beggs; Jun Z Li; Margit Burmeister; James J Dowling
Journal:  Am J Hum Genet       Date:  2012-07-19       Impact factor: 11.025

4.  Mouse model of severe recessive RYR1-related myopathy.

Authors:  Stephanie Brennan; Maricela Garcia-Castañeda; Antonio Michelucci; Nesrin Sabha; Sundeep Malik; Linda Groom; Lan Wei LaPierre; James J Dowling; Robert T Dirksen
Journal:  Hum Mol Genet       Date:  2019-09-15       Impact factor: 6.150

5.  Variants in the Oxidoreductase PYROXD1 Cause Early-Onset Myopathy with Internalized Nuclei and Myofibrillar Disorganization.

Authors:  Gina L O'Grady; Heather A Best; Tamar E Sztal; Vanessa Schartner; Myriam Sanjuan-Vazquez; Sandra Donkervoort; Osorio Abath Neto; Roger Bryan Sutton; Biljana Ilkovski; Norma Beatriz Romero; Tanya Stojkovic; Jahannaz Dastgir; Leigh B Waddell; Anne Boland; Ying Hu; Caitlin Williams; Avnika A Ruparelia; Thierry Maisonobe; Anthony J Peduto; Stephen W Reddel; Monkol Lek; Taru Tukiainen; Beryl B Cummings; Himanshu Joshi; Juliette Nectoux; Susan Brammah; Jean-François Deleuze; Viola Oorschot Ing; Georg Ramm; Didem Ardicli; Kristen J Nowak; Beril Talim; Haluk Topaloglu; Nigel G Laing; Kathryn N North; Daniel G MacArthur; Sylvie Friant; Nigel F Clarke; Robert J Bryson-Richardson; Carsten G Bönnemann; Jocelyn Laporte; Sandra T Cooper
Journal:  Am J Hum Genet       Date:  2016-10-13       Impact factor: 11.025

Review 6.  Congenital myopathies: an update.

Authors:  Jessica R Nance; James J Dowling; Elizabeth M Gibbs; Carsten G Bönnemann
Journal:  Curr Neurol Neurosci Rep       Date:  2012-04       Impact factor: 5.081

7.  Novel deletion of lysine 7 expands the clinical, histopathological and genetic spectrum of TPM2-related myopathies.

Authors:  Ann E Davidson; Fazeel M Siddiqui; Michael A Lopez; Peter Lunt; Heather A Carlson; Brian E Moore; Seth Love; Donald E Born; Helen Roper; Anirban Majumdar; Suman Jayadev; Hunter R Underhill; Corrine O Smith; Maja von der Hagen; Angela Hubner; Philip Jardine; Andria Merrison; Elizabeth Curtis; Thomas Cullup; Heinz Jungbluth; Mary O Cox; Thomas L Winder; Hossam Abdel Salam; Jun Z Li; Steven A Moore; James J Dowling
Journal:  Brain       Date:  2013-02       Impact factor: 13.501

8.  Respiratory motor function in individuals with centronuclear myopathies.

Authors:  Barbara K Smith; Markus S Renno; Meghan M Green; Terry M Sexton; Lee Ann Lawson; Anatole D Martin; Manuela Corti; Barry J Byrne
Journal:  Muscle Nerve       Date:  2015-12-29       Impact factor: 3.217

Review 9.  Pathophysiological concepts in the congenital myopathies: blurring the boundaries, sharpening the focus.

Authors:  Gianina Ravenscroft; Nigel G Laing; Carsten G Bönnemann
Journal:  Brain       Date:  2014-12-31       Impact factor: 13.501

10.  Pathogenic Variants in the Myosin Chaperone UNC-45B Cause Progressive Myopathy with Eccentric Cores.

Authors:  Sandra Donkervoort; Carl E Kutzner; Ying Hu; Xavière Lornage; John Rendu; Tanya Stojkovic; Jonathan Baets; Sarah B Neuhaus; Jantima Tanboon; Reza Maroofian; Véronique Bolduc; Magdalena Mroczek; Stefan Conijn; Nancy L Kuntz; Ana Töpf; Soledad Monges; Fabiana Lubieniecki; Riley M McCarty; Katherine R Chao; Serena Governali; Johann Böhm; Kanokwan Boonyapisit; Edoardo Malfatti; Tumtip Sangruchi; Iren Horkayne-Szakaly; Carola Hedberg-Oldfors; Stephanie Efthymiou; Satoru Noguchi; Sarah Djeddi; Aritoshi Iida; Gabriella di Rosa; Chiara Fiorillo; Vincenzo Salpietro; Niklas Darin; Julien Fauré; Henry Houlden; Anders Oldfors; Ichizo Nishino; Willem de Ridder; Volker Straub; Wojciech Pokrzywa; Jocelyn Laporte; A Reghan Foley; Norma B Romero; Coen Ottenheijm; Thorsten Hoppe; Carsten G Bönnemann
Journal:  Am J Hum Genet       Date:  2020-11-19       Impact factor: 11.025

View more

北京卡尤迪生物科技股份有限公司 © 2022-2023.