Literature DB >> 22006688

Subclinical autonomic dysfunction in spinobulbar muscular atrophy (Kennedy disease).

Camilla Rocchi1, Viviana Greco, Andrea Urbani, Alessandra Di Giorgio, Marina Priori, Roberto Massa, Giorgio Bernardi, Girolama A Marfia.   

Abstract

INTRODUCTION: Spinobulbar muscular atrophy (SBMA) is an inherited adult-onset motor neuron disease caused by the expansion of a polyglutamine tract within the androgen receptor. Autonomic nervous system involvement (ANS) is not considered part of SBMA. The aim of this study was to assess autonomic cardiovascular function in 5 SBMA patients.
METHODS: Five quantitative autonomic function tests (AFTs) were performed in 5 SBMA patients. Plasma noradrenaline (NA) concentration in patients and in 5 healthy subjects was also measured.
RESULTS: AFTs were abnormal in 4 of the 5 patients, and plasma NA concentration was significantly reduced in patients with respect to controls.
CONCLUSION: The impairment of cardiovascular responses to AFTs in addition to reduced plasma NA concentration observed in our patients suggests subclinical involvement of the ANS in Kennedy disease.
Copyright © 2011 Wiley Periodicals, Inc.

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Year:  2011        PMID: 22006688     DOI: 10.1002/mus.22159

Source DB:  PubMed          Journal:  Muscle Nerve        ISSN: 0148-639X            Impact factor:   3.217


  8 in total

Review 1.  Onset Manifestations of Spinal and Bulbar Muscular Atrophy (Kennedy's Disease).

Authors:  Josef Finsterer; Gianni Soraru
Journal:  J Mol Neurosci       Date:  2015-10-19       Impact factor: 3.444

2.  Early onset and novel features in a spinal and bulbar muscular atrophy patient with a 68 CAG repeat.

Authors:  Christopher Grunseich; Ilona R Kats; Laura C Bott; Carlo Rinaldi; Angela Kokkinis; Derrick Fox; Ke-Lian Chen; Alice B Schindler; Ami K Mankodi; Joseph A Shrader; Daniel P Schwartz; Tanya J Lehky; Chia-Ying Liu; Kenneth H Fischbeck
Journal:  Neuromuscul Disord       Date:  2014-07-03       Impact factor: 4.296

3.  Using genetic testing to diagnose Kennedy's disease: a case report and literature review.

Authors:  Jie Chen; Xie Long; Yan Han
Journal:  Am J Transl Res       Date:  2021-06-15       Impact factor: 4.060

Review 4.  Kennedy's disease (spinal and bulbar muscular atrophy): a clinically oriented review of a rare disease.

Authors:  Marianthi Breza; Georgios Koutsis
Journal:  J Neurol       Date:  2018-07-13       Impact factor: 4.849

Review 5.  Beyond motor neurons: expanding the clinical spectrum in Kennedy's disease.

Authors:  Raquel Manzano; Gianni Sorarú; Christopher Grunseich; Pietro Fratta; Emanuela Zuccaro; Maria Pennuto; Carlo Rinaldi
Journal:  J Neurol Neurosurg Psychiatry       Date:  2018-01-20       Impact factor: 10.154

6.  The French national protocol for Kennedy's disease (SBMA): consensus diagnostic and management recommendations.

Authors:  Pierre-François Pradat; Emilien Bernard; Philippe Corcia; Philippe Couratier; Christel Jublanc; Giorgia Querin; Capucine Morélot Panzini; François Salachas; Christophe Vial; Karim Wahbi; Peter Bede; Claude Desnuelle
Journal:  Orphanet J Rare Dis       Date:  2020-04-10       Impact factor: 4.123

7.  Clinical Phenotyping and Biomarkers in Spinal and Bulbar Muscular Atrophy.

Authors:  Elina Millere; Dmitrijs Rots; Ieva Glazere; Gita Taurina; Natalja Kurjane; Viktorija Priedite; Linda Gailite; Kaj Blennow; Henrik Zetterberg; Viktorija Kenina
Journal:  Front Neurol       Date:  2021-01-20       Impact factor: 4.003

8.  Non-neural phenotype of spinal and bulbar muscular atrophy: results from a large cohort of Italian patients.

Authors:  Giorgia Querin; Cinzia Bertolin; Elisa Da Re; Marco Volpe; Gabriella Zara; Elena Pegoraro; Nicola Caretta; Carlo Foresta; Maria Silvano; Domenico Corrado; Massimo Iafrate; Lorenzo Angelini; Leonardo Sartori; Maria Pennuto; Alessandra Gaiani; Luca Bello; Claudio Semplicini; Davide Pareyson; Vincenzo Silani; Mario Ermani; Alberto Ferlin; Gianni Sorarù
Journal:  J Neurol Neurosurg Psychiatry       Date:  2015-10-26       Impact factor: 10.154

  8 in total

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