Literature DB >> 21983849

Are patients with encephalocraniocutaneous lipomatosis at increased risk of developing low-grade gliomas?

Elvis Terci Valera1, María Sol Brassesco, Carlos Alberto Scrideli, Marcus Vinicius de Castro Barros, Antonio Carlos Santos, Ricardo Santos Oliveira, Hélio Rubens Machado, Luiz Gonzaga Tone.   

Abstract

INTRODUCTION: Cancer-prone genetic disorders are responsible for brain tumors in a considerable proportion of children. Additionally, rare genetic syndromes associated to cancer development may potentially disclose genetic mechanisms related to oncogenesis.
METHOD: We describe two pediatric patients with encephalocraniocutaneous lipomatosis (ECCL), a very rare genetic syndrome with around 60 reported cases, which developed low-grade astrocytoma at 3 and 12 years of age.
RESULTS: Patients with ECCL seem to be at risk of benign forms of osseous tumors such as ossifying fibromas, odontomas, and osteomas.
CONCLUSION: The association between brain tumor and ECCL was previously reported only once, in a pediatric case of a mixed neuronal-glial histology. Whether ECCL may be a genetic condition of predisposing brain tumor in children strongly needs to be addressed.

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Year:  2011        PMID: 21983849     DOI: 10.1007/s00381-011-1601-z

Source DB:  PubMed          Journal:  Childs Nerv Syst        ISSN: 0256-7040            Impact factor:   1.475


  18 in total

1.  Encephalocraniocutaneous lipomatosis. A new example of ectomesodermal dysgenesis.

Authors:  C Haberland; M Perou
Journal:  Arch Neurol       Date:  1970-02

2.  Mandibular osteoma in the encephalocraniocutaneous lipomatosis.

Authors:  Bogna Zielińska-Kaźmierska; Joanna Grodecka; Lidia Jabłońska-Polakowska; Piotr Arkuszewski
Journal:  J Craniomaxillofac Surg       Date:  2005-08       Impact factor: 2.078

3.  Encephalocraniocutaneous lipomatosis accompanied by maxillary compound odontoma and juvenile angiofibroma: report of a case.

Authors:  Dimitrios A Andreadis; Christos B Rizos; Maria Belazi; Milena Peneva; Demetrios Z Antoniades
Journal:  Birth Defects Res A Clin Mol Teratol       Date:  2004-11

4.  Cytogenetics in pediatric low-grade astrocytomas.

Authors:  Lesley C Orr; Julie Fleitz; Loris McGavran; Josephine Wyatt-Ashmead; Michael Handler; Nicholas K Foreman
Journal:  Med Pediatr Oncol       Date:  2002-03

Review 5.  Using neurofibromatosis-1 to better understand and treat pediatric low-grade glioma.

Authors:  David H Gutmann
Journal:  J Child Neurol       Date:  2008-10       Impact factor: 1.987

Review 6.  Nevoid basal cell carcinoma syndrome (Gorlin syndrome).

Authors:  Lorenzo Lo Muzio
Journal:  Orphanet J Rare Dis       Date:  2008-11-25       Impact factor: 4.123

Review 7.  Encephalocraniocutaneous lipomatosis.

Authors:  U Moog
Journal:  J Med Genet       Date:  2009-07-01       Impact factor: 6.318

8.  Brain anomalies in encephalocraniocutaneous lipomatosis.

Authors:  Ute Moog; Marilyn C Jones; David H Viskochil; Alain Verloes; Margot I Van Allen; William B Dobyns
Journal:  Am J Med Genet A       Date:  2007-12-15       Impact factor: 2.802

9.  Low-grade astrocytoma in a child with encephalocraniocutaneous lipomatosis.

Authors:  María Sol Brassesco; Elvis Terci Valera; Aline Paixão Becker; Angel Mauricio Castro-Gamero; André de Aboim Machado; Antônio Carlos Santos; Carlos Alberto Scrideli; Ricardo Santos Oliveira; Hélio Rubens Machado; Luiz Gonzaga Tone
Journal:  J Neurooncol       Date:  2009-08-04       Impact factor: 4.130

Review 10.  Recent advances in neurobiology of Tuberous Sclerosis Complex.

Authors:  Valerio Napolioni; Romina Moavero; Paolo Curatolo
Journal:  Brain Dev       Date:  2008-11-22       Impact factor: 1.961

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  9 in total

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2.  Mosaic Activating Mutations in FGFR1 Cause Encephalocraniocutaneous Lipomatosis.

Authors:  James T Bennett; Tiong Yang Tan; Diana Alcantara; Martine Tétrault; Andrew E Timms; Dana Jensen; Sarah Collins; Malgorzata J M Nowaczyk; Marjorie J Lindhurst; Katherine M Christensen; Stephen R Braddock; Heather Brandling-Bennett; Raoul C M Hennekam; Brian Chung; Anna Lehman; John Su; SuYuen Ng; David J Amor; Jacek Majewski; Les G Biesecker; Kym M Boycott; William B Dobyns; Mark O'Driscoll; Ute Moog; Laura M McDonell
Journal:  Am J Hum Genet       Date:  2016-03-03       Impact factor: 11.025

3.  Encephalocraniocutaneous lipomatosis, a rare neurocutaneous disorder: report of additional three cases.

Authors:  O Kocak; C Yarar; K B Carman
Journal:  Childs Nerv Syst       Date:  2015-08-01       Impact factor: 1.475

4.  The association between BMP4 gene polymorphism and its serum level with the incidence of LVH in hypertensive patients.

Authors:  G L Gu; Q Y Yang; R L Zeng; X L Xu
Journal:  J Transl Med       Date:  2015-01-16       Impact factor: 5.531

5.  Role of osteoprotegerin and its gene polymorphisms in the occurrence of left ventricular hypertrophy in essential hypertensive patients.

Authors:  Anna Shen; Xuwei Hou; Deguang Yang; Tingrong Liu; Dezhong Zheng; Liehua Deng; Tao Zhou
Journal:  Medicine (Baltimore)       Date:  2014-12       Impact factor: 1.889

6.  A rare case of dysembryoplastic neuroepithelial tumor combined with encephalocraniocutaneous lipomatosis and intractable seizures.

Authors:  Jee-Yeon Han; Mi-Sun Yum; Eun-Hee Kim; Seokho Hong; Tae-Sung Ko
Journal:  Korean J Pediatr       Date:  2016-11-30

7.  Expansion of the phenotypic spectrum and description of molecular findings in a cohort of patients with oculocutaneous mosaic RASopathies.

Authors:  Oscar F Chacon-Camacho; Daniel Lopez-Moreno; Martha A Morales-Sanchez; Enriqueta Hofmann; Michelle Pacheco-Quito; Ilse Wieland; Vianney Cortes-Gonzalez; Cristina Villanueva-Mendoza; Martin Zenker; Juan Carlos Zenteno
Journal:  Mol Genet Genomic Med       Date:  2019-03-19       Impact factor: 2.183

Review 8.  Encephalocraniocutaneous lipomatosis: a case report and review of the literature.

Authors:  Shivcharan L Chandravanshi
Journal:  Indian J Ophthalmol       Date:  2014-05       Impact factor: 1.848

9.  Methylome analysis and whole-exome sequencing reveal that brain tumors associated with encephalocraniocutaneous lipomatosis are midline pilocytic astrocytomas.

Authors:  Elvis Terci Valera; Melissa K McConechy; Tenzin Gayden; Barbara Rivera; David T W Jones; Andrea Wittmann; HyeRim Han; Eric Bareke; Hamid Nikbakht; Leonie Mikael; Rosane Gomes Queiroz; Veridiana Kiill Suazo; Ji Hoon Phi; Seung-Ki Kim; Sung-Hye Park; Raita Fukaya; Mi-Sun Yum; Tae-Sung Ko; Ricardo Santos de Oliveira; Helio Rubens Machado; María Sol Brassesco; Antonio Carlos do Santos; Gustavo Novelino Simão; Leandra Náira Zambelli Ramalho; Luciano Neder; Carlos Alberto Scrideli; Luiz Gonzaga Tone; Jacek Majewski; Nada Jabado
Journal:  Acta Neuropathol       Date:  2018-08-24       Impact factor: 17.088

  9 in total

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