Literature DB >> 21789723

Inheritance pattern and clinical aspects of 93 Iranian patients with chronic granulomatous disease.

Fatemeh Fattahi1, Mohsen Badalzadeh, Leyla Sedighipour, Masoud Movahedi, Mohammad Reza Fazlollahi, Seyed Davood Mansouri, Ghamar Taj Khotaei, Mohammad Hassan Bemanian, Fatemeh Behmanesh, Amir Ali Hamidieh, Nasrin Bazargan, Setareh Mamishi, Fariborz Zandieh, Zahra Chavoshzadeh, Iraj Mohammadzadeh, Seyed Alireza Mahdaviani, Seyed Ahmad Tabatabaei, Najmeddin Kalantari, Shaghayegh Tajik, Marzieh Maddah, Zahra Pourpak, Mostafa Moin.   

Abstract

BACKGROUND: Chronic granulomatous disease (CGD) is a rare immunodeficiency due to a genetic defect in one of the NADPH-oxidase components. We studied CGD inheritance forms (autosomal recessive (AR) or X-linked (XL)) and AR-CGD subtypes in Iran.
METHODS: Clinical and functional investigations were conducted in 93 Iranian CGD patients from 75 families.
RESULTS: Most of the patients were AR-CGD (87.1%). This was related to consanguineous marriages (p = 0.001). The age of onset of symptoms and diagnosis were lower in XL-CGD compared with AR-CGD (p < 0.0001 for both). Among AR-CGD patients, p47phox defect was the predominant subtype (55.5%). The most common clinical features in patients were lymphadenopathy (65.6%) and pulmonary involvement (57%). XL-CGD patients were affected more frequently with severe infectious manifestations.
CONCLUSIONS: Although XL-CGD is the most common type of the disease worldwide, only 12 patients (12.9%) were XL-CGD in our study. The relatively high frequency of AR-CGD is probable due to widely common consanguineous marriages in Iran.

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Year:  2011        PMID: 21789723     DOI: 10.1007/s10875-011-9567-x

Source DB:  PubMed          Journal:  J Clin Immunol        ISSN: 0271-9142            Impact factor:   8.317


  36 in total

1.  Genetic and mutational heterogeneity of autosomal recessive chronic granulomatous disease in Tunisia.

Authors:  R El Kares; M R Barbouche; H Elloumi-Zghal; M Bejaoui; J Chemli; F Mellouli; N Tebib; M S Abdelmoula; S Boukthir; Z Fitouri; S M'Rad; K Bouslama; H Touiri; S Abdelhak; M K Dellagi
Journal:  J Hum Genet       Date:  2006-08-26       Impact factor: 3.172

2.  Genotype-dependent variability in flow cytometric evaluation of reduced nicotinamide adenine dinucleotide phosphate oxidase function in patients with chronic granulomatous disease.

Authors:  S J Vowells; T A Fleisher; S Sekhsaria; D W Alling; T E Maguire; H L Malech
Journal:  J Pediatr       Date:  1996-01       Impact factor: 4.406

3.  Long-term follow-up and outcome of 39 patients with chronic granulomatous disease.

Authors:  J Liese; S Kloos; V Jendrossek; T Petropoulou; U Wintergerst; G Notheis; M Gahr; B H Belohradsky
Journal:  J Pediatr       Date:  2000-11       Impact factor: 4.406

4.  Diagnostic criteria for primary immunodeficiencies. Representing PAGID (Pan-American Group for Immunodeficiency) and ESID (European Society for Immunodeficiencies).

Authors:  M E Conley; L D Notarangelo; A Etzioni
Journal:  Clin Immunol       Date:  1999-12       Impact factor: 3.969

5.  Diagnosis and carrier detection of chronic granulomatous disease in five families by flow cytometry.

Authors:  A D Crockard; J M Thompson; N A Boyd; D J Haughton; D R McCluskey; C P Turner
Journal:  Int Arch Allergy Immunol       Date:  1997-10       Impact factor: 2.749

6.  A new genetic subgroup of chronic granulomatous disease with autosomal recessive mutations in p40 phox and selective defects in neutrophil NADPH oxidase activity.

Authors:  Juan D Matute; Andres A Arias; Nicola A M Wright; Iwona Wrobel; Christopher C M Waterhouse; Xing Jun Li; Christophe C Marchal; Natalie D Stull; David B Lewis; MacGregor Steele; James D Kellner; Weiming Yu; Samy O Meroueh; William M Nauseef; Mary C Dinauer
Journal:  Blood       Date:  2009-08-19       Impact factor: 22.113

7.  Chronic granulomatous disease in Israel: clinical, functional and molecular studies of 38 patients.

Authors:  Baruch Wolach; Ronit Gavrieli; Martin de Boer; Giora Gottesman; Josef Ben-Ari; Menachem Rottem; Yechiel Schlesinger; Galia Grisaru-Soen; Amos Etzioni; Dirk Roos
Journal:  Clin Immunol       Date:  2008-08-16       Impact factor: 3.969

8.  Clinical features, long-term follow-up and outcome of a large cohort of patients with Chronic Granulomatous Disease: an Italian multicenter study.

Authors:  Baldassarre Martire; Roberto Rondelli; Annarosa Soresina; Claudio Pignata; Teresa Broccoletti; Andrea Finocchi; Paolo Rossi; Marco Gattorno; Marco Rabusin; Chiara Azzari; Rosa M Dellepiane; Maria C Pietrogrande; Antonino Trizzino; Paolo Di Bartolomeo; Silvana Martino; Luigi Carpino; Fausto Cossu; Franco Locatelli; Rita Maccario; Paolo Pierani; Maria C Putti; Achille Stabile; Luigi D Notarangelo; Alberto G Ugazio; Alessandro Plebani; Domenico De Mattia
Journal:  Clin Immunol       Date:  2007-11-26       Impact factor: 3.969

9.  Chronic granulomatous disease: a clinical survey of 41 patients from the Iranian primary immunodeficiency registry.

Authors:  Masoud Movahedi; Asghar Aghamohammadi; Nima Rezaei; Nikrad Shahnavaz; Ali Babaei Jandaghi; Abolhasan Farhoudi; Zahra Pourpak; Mostafa Moin; Mohammad Gharagozlou; Davoud Mansouri
Journal:  Int Arch Allergy Immunol       Date:  2004-06-01       Impact factor: 2.749

10.  Chronic granulomatous disease in adults.

Authors:  J G Liese; V Jendrossek; A Jansson; T Petropoulou; S Kloos; M Gahr; B H Belohradsky
Journal:  Lancet       Date:  1996-01-27       Impact factor: 79.321

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  35 in total

Review 1.  Bacillus Calmette-Guérin (BCG) complications associated with primary immunodeficiency diseases.

Authors:  Sayna Norouzi; Asghar Aghamohammadi; Setareh Mamishi; Sergio D Rosenzweig; Nima Rezaei
Journal:  J Infect       Date:  2012-03-16       Impact factor: 6.072

Review 2.  Infectious Complications in Patients With Chronic Granulomatous Disease.

Authors:  Nicholas Bennett; Paul J Maglione; Benjamin L Wright; Christa Zerbe
Journal:  J Pediatric Infect Dis Soc       Date:  2018-05-09       Impact factor: 3.164

3.  Infection Profile in Chronic Granulomatous Disease: a 23-Year Experience from a Tertiary Care Center in North India.

Authors:  Amit Rawat; Pandiarajan Vignesh; Avinash Sharma; Jitendra K Shandilya; Madhubala Sharma; Deepti Suri; Anju Gupta; Vikas Gautam; Pallab Ray; Shivaprakash M Rudramurthy; Arunaloke Chakrabarti; Kohsuke Imai; Shigeaki Nonoyama; Osamu Ohara; Yu L Lau; Surjit Singh
Journal:  J Clin Immunol       Date:  2017-03-22       Impact factor: 8.317

4.  Approach to Molecular Diagnosis of Chronic Granulomatous Disease (CGD): an Experience from a Large Cohort of 90 Indian Patients.

Authors:  Manasi Kulkarni; Gouri Hule; Martin de Boer; Karin van Leeuwen; Priyanka Kambli; Jahnavi Aluri; Maya Gupta; Aparna Dalvi; Snehal Mhatre; Prasad Taur; Mukesh Desai; Manisha Madkaikar
Journal:  J Clin Immunol       Date:  2018-11-23       Impact factor: 8.317

Review 5.  Mendelian susceptibility to mycobacterial disease: genetic, immunological, and clinical features of inborn errors of IFN-γ immunity.

Authors:  Jacinta Bustamante; Stéphanie Boisson-Dupuis; Laurent Abel; Jean-Laurent Casanova
Journal:  Semin Immunol       Date:  2014-10-26       Impact factor: 11.130

6.  NCF1 (p47phox)-deficient chronic granulomatous disease: comprehensive genetic and flow cytometric analysis.

Authors:  Douglas B Kuhns; Amy P Hsu; David Sun; Karen Lau; Danielle Fink; Paul Griffith; Da Wei Huang; Debra A Long Priel; Laura Mendez; Samantha Kreuzburg; Christa S Zerbe; Suk See De Ravin; Harry L Malech; Steven M Holland; Xiaolin Wu; John I Gallin
Journal:  Blood Adv       Date:  2019-01-22

7.  Common severe infections in chronic granulomatous disease.

Authors:  Beatriz E Marciano; Christine Spalding; Alan Fitzgerald; Daphne Mann; Thomas Brown; Sharon Osgood; Lynne Yockey; Dirk N Darnell; Lisa Barnhart; Janine Daub; Lisa Boris; Amy P Rump; Victoria L Anderson; Carissa Haney; Douglas B Kuhns; Sergio D Rosenzweig; Corin Kelly; Adrian Zelazny; Tamika Mason; Suk See DeRavin; Elizabeth Kang; John I Gallin; Harry L Malech; Kenneth N Olivier; Gulbu Uzel; Alexandra F Freeman; Theo Heller; Christa S Zerbe; Steven M Holland
Journal:  Clin Infect Dis       Date:  2014-12-23       Impact factor: 9.079

8.  Primary immunodeficiency diseases: Genomic approaches delineate heterogeneous Mendelian disorders.

Authors:  Asbjørg Stray-Pedersen; Hanne Sørmo Sorte; Pubudu Samarakoon; Tomasz Gambin; Ivan K Chinn; Zeynep H Coban Akdemir; Hans Christian Erichsen; Lisa R Forbes; Shen Gu; Bo Yuan; Shalini N Jhangiani; Donna M Muzny; Olaug Kristin Rødningen; Ying Sheng; Sarah K Nicholas; Lenora M Noroski; Filiz O Seeborg; Carla M Davis; Debra L Canter; Emily M Mace; Timothy J Vece; Carl E Allen; Harshal A Abhyankar; Philip M Boone; Christine R Beck; Wojciech Wiszniewski; Børre Fevang; Pål Aukrust; Geir E Tjønnfjord; Tobias Gedde-Dahl; Henrik Hjorth-Hansen; Ingunn Dybedal; Ingvild Nordøy; Silje F Jørgensen; Tore G Abrahamsen; Torstein Øverland; Anne Grete Bechensteen; Vegard Skogen; Liv T N Osnes; Mari Ann Kulseth; Trine E Prescott; Cecilie F Rustad; Ketil R Heimdal; John W Belmont; Nicholas L Rider; Javier Chinen; Tram N Cao; Eric A Smith; Maria Soledad Caldirola; Liliana Bezrodnik; Saul Oswaldo Lugo Reyes; Francisco J Espinosa Rosales; Nina Denisse Guerrero-Cursaru; Luis Alberto Pedroza; Cecilia M Poli; Jose L Franco; Claudia M Trujillo Vargas; Juan Carlos Aldave Becerra; Nicola Wright; Thomas B Issekutz; Andrew C Issekutz; Jordan Abbott; Jason W Caldwell; Diana K Bayer; Alice Y Chan; Alessandro Aiuti; Caterina Cancrini; Eva Holmberg; Christina West; Magnus Burstedt; Ender Karaca; Gözde Yesil; Hasibe Artac; Yavuz Bayram; Mehmed Musa Atik; Mohammad K Eldomery; Mohammad S Ehlayel; Stephen Jolles; Berit Flatø; Alison A Bertuch; I Celine Hanson; Victor W Zhang; Lee-Jun Wong; Jianhong Hu; Magdalena Walkiewicz; Yaping Yang; Christine M Eng; Eric Boerwinkle; Richard A Gibbs; William T Shearer; Robert Lyle; Jordan S Orange; James R Lupski
Journal:  J Allergy Clin Immunol       Date:  2016-07-16       Impact factor: 10.793

9.  Chronic granulomatous disease in Morocco: genetic, immunological, and clinical features of 12 patients from 10 kindreds.

Authors:  Laila Ait Baba; Fatima Ailal; Naima El Hafidi; Marjorie Hubeau; Fabienne Jabot-Hanin; Noufissa Benajiba; Zahra Aadam; Francesca Conti; Caroline Deswarte; Leila Jeddane; Ayoub Aglaguel; Ouafaa El Maataoui; Ahmed Tissent; Chafiq Mahraoui; Jilali Najib; Ruben Martinez-Barricarte; Laurent Abel; Norddine Habti; Rachid Saile; Jean-Laurent Casanova; Jacinta Bustamante; Hanane Salih Alj; Ahmed Aziz Bousfiha
Journal:  J Clin Immunol       Date:  2014-03-05       Impact factor: 8.317

10.  Clinical and molecular features of 38 children with chronic granulomatous disease in mainland china.

Authors:  Huan Xu; Wen Tian; Shu-Juan Li; Lu-Ying Zhang; Wei Liu; Yao Zhao; Zhi-Yong Zhang; Xue-Mei Tang; Mo Wang; Dao-Qi Wu; Ji-Sheng Shi; Yuan Ding; Xiao-Dong Zhao; Xi-Qiang Yang; Li-Ping Jiang
Journal:  J Clin Immunol       Date:  2014-06-19       Impact factor: 8.317

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