Literature DB >> 21660611

[Neuromuscular diseases].

B Schoser1, S Zierz.   

Abstract

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Year:  2011        PMID: 21660611     DOI: 10.1007/s00115-010-3038-0

Source DB:  PubMed          Journal:  Nervenarzt        ISSN: 0028-2804            Impact factor:   1.214


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  3 in total

Review 1.  New insights in gene-derived therapy: the example of Duchenne muscular dystrophy.

Authors:  Annemieke Aartsma-Rus; Johan T den Dunnen; Gert-Jan B van Ommen
Journal:  Ann N Y Acad Sci       Date:  2010-12-01       Impact factor: 5.691

2.  Systemic administration of PRO051 in Duchenne's muscular dystrophy.

Authors:  Nathalie M Goemans; Mar Tulinius; Johanna T van den Akker; Brigitte E Burm; Peter F Ekhart; Niki Heuvelmans; Tjadine Holling; Anneke A Janson; Gerard J Platenburg; Jessica A Sipkens; J M Ad Sitsen; Annemieke Aartsma-Rus; Gert-Jan B van Ommen; Gunnar Buyse; Niklas Darin; Jan J Verschuuren; Giles V Campion; Sjef J de Kimpe; Judith C van Deutekom
Journal:  N Engl J Med       Date:  2011-03-23       Impact factor: 91.245

3.  A randomized study of alglucosidase alfa in late-onset Pompe's disease.

Authors:  Ans T van der Ploeg; Paula R Clemens; Deyanira Corzo; Diana M Escolar; Julaine Florence; Geert Jan Groeneveld; Serge Herson; Priya S Kishnani; Pascal Laforet; Stephen L Lake; Dale J Lange; Robert T Leshner; Jill E Mayhew; Claire Morgan; Kenkichi Nozaki; Dorothy J Park; Alan Pestronk; Barry Rosenbloom; Alison Skrinar; Carine I van Capelle; Nadine A van der Beek; Melissa Wasserstein; Sasa A Zivkovic
Journal:  N Engl J Med       Date:  2010-04-15       Impact factor: 91.245

  3 in total

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