Literature DB >> 21352278

Exon 87 skipping of the COL7A1 gene in dominant dystrophic epidermolysis bullosa.

Hiroshi Koga1, Takahiro Hamada, Norito Ishii, Shunpei Fukuda, Sachiko Sakaguchi, Hajime Nakano, Katuto Tamai, Daisuke Sawamura, Takashi Hashimoto.   

Abstract

Dystrophic epidermolysis bullosa (DEB) is a rare, inherited, blistering disorder resulting from mutations in the COL7A1 gene, which encodes the anchoring fibrils, type VII collagen. We herein describe a further Japanese girl diagnosed with dominant DEB (DDEB). She had blisters sporadically and erosions healed with mild scarring and milia on the knees and pretibial regions. Severe pruritus was present at this time. Direct nucleotide sequencing of genomic DNA disclosed a heterozygous same splice-site mutation c.6900G>A in the COL7A1, which causes in-frame exon 87 skipping. So far, five different COL7A1 mutations leading to exon 87 skipping have been identified in rare forms of DEB: four DDEB pruriginosa and one pretibial DDEB. Therefore, a recent study suggested that exon 87 skipping in COL7A1 was related to the phenotype of DDEB pruriginosa. When she was 18 years old, however, the blister formation and pruritus markedly decreased. Therefore, her clinical symptoms were consistent to very mild DDEB but not to DDEB pruriginosa. Taken together, in-frame exon 87 skipping through c.6900G>A mutation may account for the mild skin features, rather than DDEB pruriginosa, in the present case.
© 2010 Japanese Dermatological Association.

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Year:  2010        PMID: 21352278     DOI: 10.1111/j.1346-8138.2010.01008.x

Source DB:  PubMed          Journal:  J Dermatol        ISSN: 0385-2407            Impact factor:   4.005


  2 in total

1.  Analysis of the functional consequences of targeted exon deletion in COL7A1 reveals prospects for dystrophic epidermolysis bullosa therapy.

Authors:  Olivier Bornert; Tobias Kühl; Jeroen Bremer; Peter C van den Akker; Anna Mg Pasmooij; Alexander Nyström
Journal:  Mol Ther       Date:  2016-05-09       Impact factor: 11.454

2.  Nonsequential Splicing Events Alter Antisense-Mediated Exon Skipping Outcome in COL7A1.

Authors:  Kristin A Ham; May Thandar Aung-Htut; Sue Fletcher; Steve D Wilton
Journal:  Int J Mol Sci       Date:  2020-10-18       Impact factor: 5.923

  2 in total

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