Paul J Orchard1, John E Wagner. Show Affiliations » 1. Department of Pediatrics and the Bone and Marrow Transplant Program, University of Minnesota Medical School, Minneapolis, USA.
Abstract
Entities: Disease
Mesh: See more » Galactosylceramidase/geneticsGalactosylceramidase/metabolismGene Expression RegulationGenetic TherapyHematopoietic Stem Cells/metabolismHumansLeukodystrophy, Globoid Cell/geneticsLeukodystrophy, Globoid Cell/therapyMicroRNAs
Substances: See more » MicroRNAsGalactosylceramidase
Year: 2011 PMID: 21306246 DOI: 10.1056/NEJMcibr1013082
Source DB: PubMed Journal: N Engl J Med ISSN: 0028-4793 Impact factor: 91.245