Literature DB >> 21289637

AAV6-mediated gene silencing fALS short.

Ronald J Mandel1, Pedro R Lowenstein, Barry J Byrne.   

Abstract

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Year:  2011        PMID： 21289637      PMCID： PMC3034865          DOI： 10.1038/mt.2010.306

Source DB:  PubMed          Journal:  Mol Ther        ISSN： 1525-0016            Impact factor:   11.454


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  14 in total

1.  Transduction patterns of pseudotyped lentiviral vectors in the nervous system.

Authors:  Liang-Fong Wong; Mimoun Azzouz; Lucy E Walmsley; Zoe Askham; Fraser J Wilkes; Kyriacos A Mitrophanous; Susan M Kingsman; Nicholas D Mazarakis
Journal:  Mol Ther       Date:  2004-01       Impact factor: 11.454

2.  Systemic delivery of genes to striated muscles using adeno-associated viral vectors.

Authors:  Paul Gregorevic; Michael J Blankinship; James M Allen; Robert W Crawford; Leonard Meuse; Daniel G Miller; David W Russell; Jeffrey S Chamberlain
Journal:  Nat Med       Date:  2004-07-25       Impact factor: 53.440

Review 3.  Altering the tropism of lentiviral vectors through pseudotyping.

Authors:  James Cronin; Xian-Yang Zhang; Jakob Reiser
Journal:  Curr Gene Ther       Date:  2005-08       Impact factor: 4.391

4.  Onset and progression in inherited ALS determined by motor neurons and microglia.

Authors:  Séverine Boillée; Koji Yamanaka; Christian S Lobsiger; Neal G Copeland; Nancy A Jenkins; George Kassiotis; George Kollias; Don W Cleveland
Journal:  Science       Date:  2006-06-02       Impact factor: 47.728

5.  Time course of transgene expression after intrastriatal pseudotyped rAAV2/1, rAAV2/2, rAAV2/5, and rAAV2/8 transduction in the rat.

Authors:  Sharon Reimsnider; Fredric P Manfredsson; Nicholas Muzyczka; Ronald J Mandel
Journal:  Mol Ther       Date:  2007-06-12       Impact factor: 11.454

6.  Increased motoneuron survival and improved neuromuscular function in transgenic ALS mice after intraspinal injection of an adeno-associated virus encoding Bcl-2.

Authors:  M Azzouz; A Hottinger; J C Paterna; A D Zurn; P Aebischer; H Büeler
Journal:  Hum Mol Genet       Date:  2000-03-22       Impact factor: 6.150

7.  Silencing mutant SOD1 using RNAi protects against neurodegeneration and extends survival in an ALS model.

Authors:  G Scott Ralph; Pippa A Radcliffe; Denise M Day; Janine M Carthy; Marie A Leroux; Debbie C P Lee; Liang-Fong Wong; Lynsey G Bilsland; Linda Greensmith; Susan M Kingsman; Kyriacos A Mitrophanous; Nicholas D Mazarakis; Mimoun Azzouz
Journal:  Nat Med       Date:  2005-03-13       Impact factor: 53.440

8.  Recombinant AAV viral vectors pseudotyped with viral capsids from serotypes 1, 2, and 5 display differential efficiency and cell tropism after delivery to different regions of the central nervous system.

Authors:  Corinna Burger; Oleg S Gorbatyuk; Margaret J Velardo; Carmen S Peden; Philip Williams; Sergei Zolotukhin; Paul J Reier; Ronald J Mandel; Nicholas Muzyczka
Journal:  Mol Ther       Date:  2004-08       Impact factor: 11.454

9.  Systemic AAV6 delivery mediating RNA interference against SOD1: neuromuscular transduction does not alter disease progression in fALS mice.

Authors:  Chris Towne; Cédric Raoul; Bernard L Schneider; Patrick Aebischer
Journal:  Mol Ther       Date:  2008-04-15       Impact factor: 11.454

Review 10.  Genetics of familial amyotrophic lateral sclerosis.

Authors:  Paul N Valdmanis; Guy A Rouleau
Journal:  Neurology       Date:  2008-01-08       Impact factor: 9.910
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  1 in total

1.  Therapeutic AAV9-mediated suppression of mutant SOD1 slows disease progression and extends survival in models of inherited ALS.

Authors:  Kevin D Foust; Desirée L Salazar; Shibi Likhite; Laura Ferraiuolo; Dara Ditsworth; Hristelina Ilieva; Kathrin Meyer; Leah Schmelzer; Lyndsey Braun; Don W Cleveland; Brian K Kaspar
Journal:  Mol Ther       Date:  2013-09-06       Impact factor: 11.454
  1 in total

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