Literature DB >> 21221100

Out of harm's way.

David A Williams, Adrian J Thrasher.   

Abstract

Mesh:

Year:  2011        PMID: 21221100     DOI: 10.1038/nbt.1750

Source DB:  PubMed          Journal:  Nat Biotechnol        ISSN: 1087-0156            Impact factor:   54.908


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  10 in total

1.  Functional genomics, proteomics, and regulatory DNA analysis in isogenic settings using zinc finger nuclease-driven transgenesis into a safe harbor locus in the human genome.

Authors:  Russell C DeKelver; Vivian M Choi; Erica A Moehle; David E Paschon; Dirk Hockemeyer; Sebastiaan H Meijsing; Yasemin Sancak; Xiaoxia Cui; Eveline J Steine; Jeffrey C Miller; Phillip Tam; Victor V Bartsevich; Xiangdong Meng; Igor Rupniewski; Sunita M Gopalan; Helena C Sun; Kathleen J Pitz; Jeremy M Rock; Lei Zhang; Gregory D Davis; Edward J Rebar; Iain M Cheeseman; Keith R Yamamoto; David M Sabatini; Rudolf Jaenisch; Philip D Gregory; Fyodor D Urnov
Journal:  Genome Res       Date:  2010-05-27       Impact factor: 9.043

2.  High-definition mapping of retroviral integration sites identifies active regulatory elements in human multipotent hematopoietic progenitors.

Authors:  Claudia Cattoglio; Danilo Pellin; Ermanno Rizzi; Giulietta Maruggi; Giorgio Corti; Francesca Miselli; Daniela Sartori; Alessandro Guffanti; Clelia Di Serio; Alessandro Ambrosi; Gianluca De Bellis; Fulvio Mavilio
Journal:  Blood       Date:  2010-09-23       Impact factor: 22.113

3.  Transfusion independence and HMGA2 activation after gene therapy of human β-thalassaemia.

Authors:  Marina Cavazzana-Calvo; Emmanuel Payen; Olivier Negre; Gary Wang; Kathleen Hehir; Floriane Fusil; Julian Down; Maria Denaro; Troy Brady; Karen Westerman; Resy Cavallesco; Beatrix Gillet-Legrand; Laure Caccavelli; Riccardo Sgarra; Leila Maouche-Chrétien; Françoise Bernaudin; Robert Girot; Ronald Dorazio; Geert-Jan Mulder; Axel Polack; Arthur Bank; Jean Soulier; Jérôme Larghero; Nabil Kabbara; Bruno Dalle; Bernard Gourmel; Gérard Socie; Stany Chrétien; Nathalie Cartier; Patrick Aubourg; Alain Fischer; Kenneth Cornetta; Frédéric Galacteros; Yves Beuzard; Eliane Gluckman; Frederick Bushman; Salima Hacein-Bey-Abina; Philippe Leboulch
Journal:  Nature       Date:  2010-09-16       Impact factor: 49.962

4.  Genomic safe harbors permit high β-globin transgene expression in thalassemia induced pluripotent stem cells.

Authors:  Eirini P Papapetrou; Gabsang Lee; Nirav Malani; Manu Setty; Isabelle Riviere; Laxmi M S Tirunagari; Kyuichi Kadota; Shoshannah L Roth; Patricia Giardina; Agnes Viale; Christina Leslie; Frederic D Bushman; Lorenz Studer; Michel Sadelain
Journal:  Nat Biotechnol       Date:  2010-12-12       Impact factor: 54.908

5.  Induction of pluripotent stem cells from mouse embryonic and adult fibroblast cultures by defined factors.

Authors:  Kazutoshi Takahashi; Shinya Yamanaka
Journal:  Cell       Date:  2006-08-10       Impact factor: 41.582

6.  Establishment of HIV-1 resistance in CD4+ T cells by genome editing using zinc-finger nucleases.

Authors:  Elena E Perez; Jianbin Wang; Jeffrey C Miller; Yann Jouvenot; Kenneth A Kim; Olga Liu; Nathaniel Wang; Gary Lee; Victor V Bartsevich; Ya-Li Lee; Dmitry Y Guschin; Igor Rupniewski; Adam J Waite; Carmine Carpenito; Richard G Carroll; Jordan S Orange; Fyodor D Urnov; Edward J Rebar; Dale Ando; Philip D Gregory; James L Riley; Michael C Holmes; Carl H June
Journal:  Nat Biotechnol       Date:  2008-06-29       Impact factor: 54.908

7.  Treatment of sickle cell anemia mouse model with iPS cells generated from autologous skin.

Authors:  Jacob Hanna; Marius Wernig; Styliani Markoulaki; Chiao-Wang Sun; Alexander Meissner; John P Cassady; Caroline Beard; Tobias Brambrink; Li-Chen Wu; Tim M Townes; Rudolf Jaenisch
Journal:  Science       Date:  2007-12-06       Impact factor: 47.728

8.  Site-specific integration of adeno-associated virus involves partial duplication of the target locus.

Authors:  Els Henckaerts; Nathalie Dutheil; Nadja Zeltner; Steven Kattman; Erik Kohlbrenner; Peter Ward; Nathalie Clément; Patricia Rebollo; Marion Kennedy; Gordon M Keller; R Michael Linden
Journal:  Proc Natl Acad Sci U S A       Date:  2009-04-16       Impact factor: 11.205

9.  Efficient targeting of expressed and silent genes in human ESCs and iPSCs using zinc-finger nucleases.

Authors:  Dirk Hockemeyer; Frank Soldner; Caroline Beard; Qing Gao; Maisam Mitalipova; Russell C DeKelver; George E Katibah; Ranier Amora; Elizabeth A Boydston; Bryan Zeitler; Xiangdong Meng; Jeffrey C Miller; Lei Zhang; Edward J Rebar; Philip D Gregory; Fyodor D Urnov; Rudolf Jaenisch
Journal:  Nat Biotechnol       Date:  2009-08-13       Impact factor: 54.908

10.  Transcription factor binding sites are genetic determinants of retroviral integration in the human genome.

Authors:  Barbara Felice; Claudia Cattoglio; Davide Cittaro; Anna Testa; Annarita Miccio; Giuliana Ferrari; Lucilla Luzi; Alessandra Recchia; Fulvio Mavilio
Journal:  PLoS One       Date:  2009-02-24       Impact factor: 3.240

  10 in total
  1 in total

1.  Derivation of genetically modified human pluripotent stem cells with integrated transgenes at unique mapped genomic sites.

Authors:  Eirini P Papapetrou; Michel Sadelain
Journal:  Nat Protoc       Date:  2011-08-04       Impact factor: 13.491

  1 in total

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