Literature DB >> 21203978

Revival of gene therapy.

Xiaoxue Zhang, George F Gao.   

Abstract

Mesh:

Year:  2010        PMID: 21203978      PMCID: PMC4875167          DOI: 10.1007/s13238-010-0026-x

Source DB:  PubMed          Journal:  Protein Cell        ISSN: 1674-800X            Impact factor:   14.870


× No keyword cloud information.
  6 in total

1.  Gene therapy. Second child in French trial is found to have leukemia.

Authors:  Eliot Marshall
Journal:  Science       Date:  2003-01-17       Impact factor: 47.728

2.  Gene therapy. Seeking the cause of induced leukemias in X-SCID trial.

Authors:  Jocelyn Kaiser
Journal:  Science       Date:  2003-01-24       Impact factor: 47.728

3.  Gene therapy for red-green colour blindness in adult primates.

Authors:  Katherine Mancuso; William W Hauswirth; Qiuhong Li; Thomas B Connor; James A Kuchenbecker; Matthew C Mauck; Jay Neitz; Maureen Neitz
Journal:  Nature       Date:  2009-09-16       Impact factor: 49.962

4.  Safety and efficacy of gene transfer for Leber's congenital amaurosis.

Authors:  Albert M Maguire; Francesca Simonelli; Eric A Pierce; Edward N Pugh; Federico Mingozzi; Jeannette Bennicelli; Sandro Banfi; Kathleen A Marshall; Francesco Testa; Enrico M Surace; Settimio Rossi; Arkady Lyubarsky; Valder R Arruda; Barbara Konkle; Edwin Stone; Junwei Sun; Jonathan Jacobs; Lou Dell'Osso; Richard Hertle; Jian-xing Ma; T Michael Redmond; Xiaosong Zhu; Bernd Hauck; Olga Zelenaia; Kenneth S Shindler; Maureen G Maguire; J Fraser Wright; Nicholas J Volpe; Jennifer Wellman McDonnell; Alberto Auricchio; Katherine A High; Jean Bennett
Journal:  N Engl J Med       Date:  2008-04-27       Impact factor: 91.245

5.  Hematopoietic stem cell gene therapy with a lentiviral vector in X-linked adrenoleukodystrophy.

Authors:  Nathalie Cartier; Salima Hacein-Bey-Abina; Cynthia C Bartholomae; Gabor Veres; Manfred Schmidt; Ina Kutschera; Michel Vidaud; Ulrich Abel; Liliane Dal-Cortivo; Laure Caccavelli; Nizar Mahlaoui; Véronique Kiermer; Denice Mittelstaedt; Céline Bellesme; Najiba Lahlou; François Lefrère; Stéphane Blanche; Muriel Audit; Emmanuel Payen; Philippe Leboulch; Bruno l'Homme; Pierre Bougnères; Christof Von Kalle; Alain Fischer; Marina Cavazzana-Calvo; Patrick Aubourg
Journal:  Science       Date:  2009-11-06       Impact factor: 47.728

6.  Age-dependent effects of RPE65 gene therapy for Leber's congenital amaurosis: a phase 1 dose-escalation trial.

Authors:  Albert M Maguire; Katherine A High; Alberto Auricchio; J Fraser Wright; Eric A Pierce; Francesco Testa; Federico Mingozzi; Jeannette L Bennicelli; Gui-shuang Ying; Settimio Rossi; Ann Fulton; Kathleen A Marshall; Sandro Banfi; Daniel C Chung; Jessica I W Morgan; Bernd Hauck; Olga Zelenaia; Xiaosong Zhu; Leslie Raffini; Frauke Coppieters; Elfride De Baere; Kenneth S Shindler; Nicholas J Volpe; Enrico M Surace; Carmela Acerra; Arkady Lyubarsky; T Michael Redmond; Edwin Stone; Junwei Sun; Jennifer Wellman McDonnell; Bart P Leroy; Francesca Simonelli; Jean Bennett
Journal:  Lancet       Date:  2009-10-23       Impact factor: 79.321

  6 in total
  2 in total

1.  A novel xeno-free and feeder-cell-free system for human pluripotent stem cell culture.

Authors:  Qihui Wang; Xiaoning Mou; Henghua Cao; Qingzhang Meng; Yanni Ma; Pengcheng Han; Junjie Jiang; Hao Zhang; Yue Ma
Journal:  Protein Cell       Date:  2012-01-19       Impact factor: 14.870

2.  Recombinant adenovirus-mediated intestinal trefoil factor gene therapy for burn-induced intestinal mucosal injury.

Authors:  Yong Sun; Yun Zhu; Liangxi Wang; Xuefei Mao; Xi Peng; Yizhi Peng
Journal:  PLoS One       Date:  2013-04-24       Impact factor: 3.240

  2 in total

北京卡尤迪生物科技股份有限公司 © 2022-2023.