Literature DB >> 20651902

A First Step in Viral Gene Therapy for Muscular Dystrophy.

Michio Hirano1.   

Abstract

Entities:  

Year:  2010        PMID: 20651902      PMCID: PMC2861776          DOI: 10.1007/s11910-010-0090-x

Source DB:  PubMed          Journal:  Curr Neurol Neurosci Rep        ISSN: 1528-4042            Impact factor:   5.081


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  8 in total

1.  Gene therapy for muscular dystrophy reaches human clinical trial.

Authors:  Paula R Clemens; Saman Eghtesad; Daniel P Reay
Journal:  Ann Neurol       Date:  2009-09       Impact factor: 10.422

2.  Dystrophin: the protein product of the Duchenne muscular dystrophy locus.

Authors:  E P Hoffman; R H Brown; L M Kunkel
Journal:  Cell       Date:  1987-12-24       Impact factor: 41.582

3.  Gene therapy of human severe combined immunodeficiency (SCID)-X1 disease.

Authors:  M Cavazzana-Calvo; S Hacein-Bey; G de Saint Basile; F Gross; E Yvon; P Nusbaum; F Selz; C Hue; S Certain; J L Casanova; P Bousso; F L Deist; A Fischer
Journal:  Science       Date:  2000-04-28       Impact factor: 47.728

4.  A single intravenous injection of adeno-associated virus serotype-9 leads to whole body skeletal muscle transduction in dogs.

Authors:  Yongping Yue; Arkasubhra Ghosh; Chun Long; Brian Bostick; Bruce F Smith; Joe N Kornegay; Dongsheng Duan
Journal:  Mol Ther       Date:  2008-09-30       Impact factor: 11.454

Review 5.  The evolution of gene therapy in X-linked severe combined immunodeficiency.

Authors:  Tonya S Rans; Ronald England
Journal:  Ann Allergy Asthma Immunol       Date:  2009-05       Impact factor: 6.347

Review 6.  Therapy for neuromuscular disorders.

Authors:  Andrea L H Arnett; Joel R Chamberlain; Jeffrey S Chamberlain
Journal:  Curr Opin Genet Dev       Date:  2009-05-04       Impact factor: 5.578

Review 7.  Limb-girdle muscular dystrophies--from genetics to molecular pathology.

Authors:  S H Laval; K M D Bushby
Journal:  Neuropathol Appl Neurobiol       Date:  2004-04       Impact factor: 8.090

8.  Correction of ADA-SCID by stem cell gene therapy combined with nonmyeloablative conditioning.

Authors:  Alessandro Aiuti; Shimon Slavin; Memet Aker; Francesca Ficara; Sara Deola; Alessandra Mortellaro; Shoshana Morecki; Grazia Andolfi; Antonella Tabucchi; Filippo Carlucci; Enrico Marinello; Federica Cattaneo; Sergio Vai; Paolo Servida; Roberto Miniero; Maria Grazia Roncarolo; Claudio Bordignon
Journal:  Science       Date:  2002-06-28       Impact factor: 47.728

  8 in total
  1 in total

1.  Screening of mitochondrial mutations and insertion-deletion polymorphism in gestational diabetes mellitus in the Asian Indian population.

Authors:  Imran Ali Khan; Noor Ahmad Shaik; Nagarjuna Pasupuleti; Srinivas Chava; Parveen Jahan; Qurratulain Hasan; Pragna Rao
Journal:  Saudi J Biol Sci       Date:  2014-11-12       Impact factor: 4.219

  1 in total

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