Literature DB >> 20485269

20 years of gene therapy for SCID.

Alain Fischer1, Salima Hacein-Bey-Abina, Marina Cavazzana-Calvo.   

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Year:  2010        PMID: 20485269     DOI: 10.1038/ni0610-457

Source DB:  PubMed          Journal:  Nat Immunol        ISSN: 1529-2908            Impact factor:   25.606


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  29 in total

1.  Diversity, functionality, and stability of the T cell repertoire derived in vivo from a single human T cell precursor.

Authors:  P Bousso; V Wahn; I Douagi; G Horneff; C Pannetier; F Le Deist; F Zepp; T Niehues; P Kourilsky; A Fischer; G de Saint Basile
Journal:  Proc Natl Acad Sci U S A       Date:  2000-01-04       Impact factor: 11.205

2.  Regulators split on gene therapy as patient shows signs of cancer.

Authors:  Erika Check
Journal:  Nature       Date:  2002-10-10       Impact factor: 49.962

3.  Second cancer case halts gene-therapy trials.

Authors:  Erika Check
Journal:  Nature       Date:  2003-01-23       Impact factor: 49.962

4.  Gene therapists hopeful as trials resume with childhood disease.

Authors:  Erika Check
Journal:  Nature       Date:  2004-06-10       Impact factor: 49.962

5.  NIH open-access plans draw fire from both sides.

Authors:  Erika Check
Journal:  Nature       Date:  2005-02-10       Impact factor: 49.962

6.  Gene therapy for immunodeficiency due to adenosine deaminase deficiency.

Authors:  Alessandro Aiuti; Federica Cattaneo; Stefania Galimberti; Ulrike Benninghoff; Barbara Cassani; Luciano Callegaro; Samantha Scaramuzza; Grazia Andolfi; Massimiliano Mirolo; Immacolata Brigida; Antonella Tabucchi; Filippo Carlucci; Martha Eibl; Memet Aker; Shimon Slavin; Hamoud Al-Mousa; Abdulaziz Al Ghonaium; Alina Ferster; Andrea Duppenthaler; Luigi Notarangelo; Uwe Wintergerst; Rebecca H Buckley; Marco Bregni; Sarah Marktel; Maria Grazia Valsecchi; Paolo Rossi; Fabio Ciceri; Roberto Miniero; Claudio Bordignon; Maria-Grazia Roncarolo
Journal:  N Engl J Med       Date:  2009-01-29       Impact factor: 91.245

Review 7.  How I treat ADA deficiency.

Authors:  H Bobby Gaspar; Alessandro Aiuti; Fulvio Porta; Fabio Candotti; Michael S Hershfield; Luigi D Notarangelo
Journal:  Blood       Date:  2009-07-28       Impact factor: 22.113

8.  T lymphocyte-directed gene therapy for ADA- SCID: initial trial results after 4 years.

Authors:  R M Blaese; K W Culver; A D Miller; C S Carter; T Fleisher; M Clerici; G Shearer; L Chang; Y Chiang; P Tolstoshev; J J Greenblatt; S A Rosenberg; H Klein; M Berger; C A Mullen; W J Ramsey; L Muul; R A Morgan; W F Anderson
Journal:  Science       Date:  1995-10-20       Impact factor: 47.728

9.  Gene therapy for human genetic disease?

Authors:  T Friedmann; R Roblin
Journal:  Science       Date:  1972-03-03       Impact factor: 47.728

10.  Correction of ADA-SCID by stem cell gene therapy combined with nonmyeloablative conditioning.

Authors:  Alessandro Aiuti; Shimon Slavin; Memet Aker; Francesca Ficara; Sara Deola; Alessandra Mortellaro; Shoshana Morecki; Grazia Andolfi; Antonella Tabucchi; Filippo Carlucci; Enrico Marinello; Federica Cattaneo; Sergio Vai; Paolo Servida; Roberto Miniero; Maria Grazia Roncarolo; Claudio Bordignon
Journal:  Science       Date:  2002-06-28       Impact factor: 47.728

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  46 in total

1.  Gene therapy for Fanconi anemia: one step closer to the clinic.

Authors:  Jakub Tolar; Pamela S Becker; D Wade Clapp; Helmut Hanenberg; Cristina Díaz de Heredia; Hans-Peter Kiem; Susana Navarro; Pankaj Qasba; Paula Rio; Manfred Schmidt; Julián Sevilla; Els Verhoeyen; Adrian J Thrasher; Juan Bueren
Journal:  Hum Gene Ther       Date:  2012-02       Impact factor: 5.695

2.  Sampling protein motion and solvent effect during ligand binding.

Authors:  Vittorio Limongelli; Luciana Marinelli; Sandro Cosconati; Concettina La Motta; Stefania Sartini; Laura Mugnaini; Federico Da Settimo; Ettore Novellino; Michele Parrinello
Journal:  Proc Natl Acad Sci U S A       Date:  2012-01-11       Impact factor: 11.205

3.  Genetics and bioethics: how our thinking has changed since 1969.

Authors:  LeRoy Walters
Journal:  Theor Med Bioeth       Date:  2012-02

Review 4.  Hematopoietic-stem-cell-based gene therapy for HIV disease.

Authors:  Hans-Peter Kiem; Keith R Jerome; Steven G Deeks; Joseph M McCune
Journal:  Cell Stem Cell       Date:  2012-02-03       Impact factor: 24.633

5.  Development of a diverse human T-cell repertoire despite stringent restriction of hematopoietic clonality in the thymus.

Authors:  Martijn H Brugman; Anna-Sophia Wiekmeijer; Marja van Eggermond; Ingrid Wolvers-Tettero; Anton W Langerak; Edwin F E de Haas; Leonid V Bystrykh; Jon J van Rood; Gerald de Haan; Willem E Fibbe; Frank J T Staal
Journal:  Proc Natl Acad Sci U S A       Date:  2015-10-19       Impact factor: 11.205

6.  Adeno-Associated Virus-Based Gene Therapy for Lifelong Correction of Genetic Disease.

Authors:  Christian M Brommel; Ashley L Cooney; Patrick L Sinn
Journal:  Hum Gene Ther       Date:  2020-08-21       Impact factor: 5.695

Review 7.  Flow Cytometry, a Versatile Tool for Diagnosis and Monitoring of Primary Immunodeficiencies.

Authors:  Roshini S Abraham; Geraldine Aubert
Journal:  Clin Vaccine Immunol       Date:  2016-04-04

Review 8.  Cardiovascular gene therapy for myocardial infarction.

Authors:  Maria C Scimia; Anna M Gumpert; Walter J Koch
Journal:  Expert Opin Biol Ther       Date:  2013-12-16       Impact factor: 4.388

Review 9.  Curing HIV: lessons from cancer therapy.

Authors:  Ronald Mitsuyasu
Journal:  Curr Opin HIV AIDS       Date:  2013-05       Impact factor: 4.283

10.  Cellular calibrators to quantitate T-cell receptor excision circles (TRECs) in clinical samples.

Authors:  Divya Punwani; Diana Gonzalez-Espinosa; Anne Marie Comeau; Amalia Dutra; Evgenia Pak; Jennifer Puck
Journal:  Mol Genet Metab       Date:  2012-09-21       Impact factor: 4.797

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