Literature DB >> 20008620

Results of dasatinib therapy in patients with early chronic-phase chronic myeloid leukemia.

Jorge E Cortes1, Dan Jones, Susan O'Brien, Elias Jabbour, Farhad Ravandi, Charles Koller, Gautam Borthakur, Brenda Walker, Weiqiang Zhao, Jianqin Shan, Hagop Kantarjian.   

Abstract

PURPOSE: Dasatinib is effective therapy for chronic myeloid leukemia (CML) after imatinib failure. In this study, we investigate the efficacy of dasatinib as initial therapy for patients with CML in early chronic phase. PATIENTS AND METHODS: Patients with newly diagnosed CML in early chronic phase were randomly assigned to receive dasatinib 100 mg once daily or 50 mg twice daily as initial therapy.
RESULTS: Among 50 patients observed for at least 3 months, 49 patients (98%) achieved a complete cytogenetic response (CCyR), and 41 patients (82%) achieved a major molecular response (MMR). Responses occurred rapidly, with 94% of patients achieving CCyR by 6 months. There was no difference in response rate by treatment arm. The projected event-free survival rate at 24 months is 88%, and all patients are alive after a median follow-up time of 24 months. Grade >or= 3 neutropenia and thrombocytopenia occurred in 21% and 10% of patients, respectively. Nonhematologic toxicity was usually grade 1 to 2. There was no significant difference in toxicity between the two arms, and the actual median dose at 12 months was 100 mg (range, 20 to 100 mg).
CONCLUSION: Dasatinib is an effective agent for the initial management of CML in early chronic phase, producing high rates of CCyR and MMR.

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Year:  2009        PMID: 20008620      PMCID: PMC2815702          DOI: 10.1200/JCO.2009.25.4920

Source DB:  PubMed          Journal:  J Clin Oncol        ISSN: 0732-183X            Impact factor:   44.544


  22 in total

1.  Discovery of N-(2-chloro-6-methyl- phenyl)-2-(6-(4-(2-hydroxyethyl)- piperazin-1-yl)-2-methylpyrimidin-4- ylamino)thiazole-5-carboxamide (BMS-354825), a dual Src/Abl kinase inhibitor with potent antitumor activity in preclinical assays.

Authors:  Louis J Lombardo; Francis Y Lee; Ping Chen; Derek Norris; Joel C Barrish; Kamelia Behnia; Stephen Castaneda; Lyndon A M Cornelius; Jagabandhu Das; Arthur M Doweyko; Craig Fairchild; John T Hunt; Ivan Inigo; Kathy Johnston; Amrita Kamath; David Kan; Herbert Klei; Punit Marathe; Suhong Pang; Russell Peterson; Sidney Pitt; Gary L Schieven; Robert J Schmidt; John Tokarski; Mei-Li Wen; John Wityak; Robert M Borzilleri
Journal:  J Med Chem       Date:  2004-12-30       Impact factor: 7.446

2.  Survival advantage from imatinib compared with the combination interferon-alpha plus cytarabine in chronic-phase chronic myelogenous leukemia: historical comparison between two phase 3 trials.

Authors:  Lydia Roy; Joëlle Guilhot; Tillmann Krahnke; Agnès Guerci-Bresler; Brian J Druker; Richard A Larson; Steve O'Brien; Charlene So; Giorgio Massimini; François Guilhot
Journal:  Blood       Date:  2006-04-20       Impact factor: 22.113

3.  Molecular responses in patients with chronic myelogenous leukemia in chronic phase treated with imatinib mesylate.

Authors:  Jorge Cortes; Moshe Talpaz; Susan O'Brien; Dan Jones; Rajyalakshmi Luthra; Jenny Shan; Francis Giles; Stefan Faderl; Srdan Verstovsek; Guillermo Garcia-Manero; Mary B Rios; Hagop Kantarjian
Journal:  Clin Cancer Res       Date:  2005-05-01       Impact factor: 12.531

4.  Hematologic and cytogenetic responses to imatinib mesylate in chronic myelogenous leukemia.

Authors:  Hagop Kantarjian; Charles Sawyers; Andreas Hochhaus; Francois Guilhot; Charles Schiffer; Carlo Gambacorti-Passerini; Dietger Niederwieser; Debra Resta; Renaud Capdeville; Ulrike Zoellner; Moshe Talpaz; Brian Druker; John Goldman; Stephen G O'Brien; Nigel Russell; Thomas Fischer; Oliver Ottmann; Pascale Cony-Makhoul; Thierry Facon; Richard Stone; Carole Miller; Martin Tallman; Randy Brown; Michael Schuster; Thomas Loughran; Alois Gratwohl; Franco Mandelli; Giuseppe Saglio; Mario Lazzarino; Domenico Russo; Michele Baccarani; Enrica Morra
Journal:  N Engl J Med       Date:  2002-02-28       Impact factor: 91.245

5.  Phase III, randomized, open-label study of daily imatinib mesylate 400 mg versus 800 mg in patients with newly diagnosed, previously untreated chronic myeloid leukemia in chronic phase using molecular end points: tyrosine kinase inhibitor optimization and selectivity study.

Authors:  Jorge E Cortes; Michele Baccarani; François Guilhot; Brian J Druker; Susan Branford; Dong-Wook Kim; Fabrizio Pane; Ricardo Pasquini; Stuart L Goldberg; Matt Kalaycio; Beatriz Moiraghi; Jacob M Rowe; Elena Tothova; Carmino De Souza; Marc Rudoltz; Richard Yu; Tillmann Krahnke; Hagop M Kantarjian; Jerald P Radich; Timothy P Hughes
Journal:  J Clin Oncol       Date:  2009-12-14       Impact factor: 44.544

6.  Overriding imatinib resistance with a novel ABL kinase inhibitor.

Authors:  Neil P Shah; Chris Tran; Francis Y Lee; Ping Chen; Derek Norris; Charles L Sawyers
Journal:  Science       Date:  2004-07-16       Impact factor: 47.728

7.  High-dose imatinib mesylate therapy in newly diagnosed Philadelphia chromosome-positive chronic phase chronic myeloid leukemia.

Authors:  Hagop Kantarjian; Moshe Talpaz; Susan O'Brien; Guillermo Garcia-Manero; Srdan Verstovsek; Francis Giles; Mary Beth Rios; Jianqin Shan; Laurie Letvak; Deborah Thomas; Stefan Faderl; Alessandra Ferrajoli; Jorge Cortes
Journal:  Blood       Date:  2003-12-24       Impact factor: 22.113

8.  Imatinib and pegylated human recombinant interferon-alpha2b in early chronic-phase chronic myeloid leukemia.

Authors:  Michele Baccarani; Giovanni Martinelli; Gianantonio Rosti; Elena Trabacchi; Nicoletta Testoni; Simona Bassi; Marilina Amabile; Simona Soverini; Fausto Castagnetti; Daniela Cilloni; Barbara Izzo; Antonio de Vivo; Emanuela Messa; Francesca Bonifazi; Angela Poerio; Simona Luatti; Emilia Giugliano; Daniele Alberti; Gianluca Fincato; Domenico Russo; Fabrizio Pane; Giuseppe Saglio
Journal:  Blood       Date:  2004-08-19       Impact factor: 22.113

9.  Imatinib compared with interferon and low-dose cytarabine for newly diagnosed chronic-phase chronic myeloid leukemia.

Authors:  Stephen G O'Brien; François Guilhot; Richard A Larson; Insa Gathmann; Michele Baccarani; Francisco Cervantes; Jan J Cornelissen; Thomas Fischer; Andreas Hochhaus; Timothy Hughes; Klaus Lechner; Johan L Nielsen; Philippe Rousselot; Josy Reiffers; Giuseppe Saglio; John Shepherd; Bengt Simonsson; Alois Gratwohl; John M Goldman; Hagop Kantarjian; Kerry Taylor; Gregor Verhoef; Ann E Bolton; Renaud Capdeville; Brian J Druker
Journal:  N Engl J Med       Date:  2003-03-13       Impact factor: 91.245

10.  Frequency of major molecular responses to imatinib or interferon alfa plus cytarabine in newly diagnosed chronic myeloid leukemia.

Authors:  Tim P Hughes; Jaspal Kaeda; Susan Branford; Zbigniew Rudzki; Andreas Hochhaus; Martee L Hensley; Insa Gathmann; Ann E Bolton; Iris C van Hoomissen; John M Goldman; Jerald P Radich
Journal:  N Engl J Med       Date:  2003-10-09       Impact factor: 91.245

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  85 in total

1.  PF-114, a potent and selective inhibitor of native and mutated BCR/ABL is active against Philadelphia chromosome-positive (Ph+) leukemias harboring the T315I mutation.

Authors:  A A Mian; A Rafiei; I Haberbosch; A Zeifman; I Titov; V Stroylov; A Metodieva; O Stroganov; F Novikov; B Brill; G Chilov; D Hoelzer; O G Ottmann; M Ruthardt
Journal:  Leukemia       Date:  2014-11-14       Impact factor: 11.528

2.  Dasatinib or imatinib in newly diagnosed chronic-phase chronic myeloid leukemia: 2-year follow-up from a randomized phase 3 trial (DASISION).

Authors:  Hagop M Kantarjian; Neil P Shah; Jorge E Cortes; Michele Baccarani; Mohan B Agarwal; María Soledad Undurraga; Jianxiang Wang; Juan Julio Kassack Ipiña; Dong-Wook Kim; Michinori Ogura; Carolina Pavlovsky; Christian Junghanss; Jorge H Milone; Franck E Nicolini; Tadeusz Robak; Jan Van Droogenbroeck; Edo Vellenga; M Brigid Bradley-Garelik; Chao Zhu; Andreas Hochhaus
Journal:  Blood       Date:  2011-12-09       Impact factor: 22.113

3.  EUTOS score is not predictive for survival and outcome in patients with early chronic phase chronic myeloid leukemia treated with tyrosine kinase inhibitors: a single institution experience.

Authors:  Elias Jabbour; Jorge Cortes; Aziz Nazha; Susan O'Brien; Alfonso Quintas-Cardama; Sherry Pierce; Guillermo Garcia-Manero; Hagop Kantarjian
Journal:  Blood       Date:  2012-03-19       Impact factor: 22.113

Review 4.  Molecular monitoring of BCR-ABL transcripts in patients with chronic myelogenous leukemia: is high sensitivity of clinical value?

Authors:  Maxim Norkin; Charles A Schiffer
Journal:  Curr Hematol Malig Rep       Date:  2010-04       Impact factor: 3.952

5.  The response to imatinib and interferon-alpha is more rapid than the response to imatinib alone: a retrospective analysis of 495 Philadelphia-positive chronic myeloid leukemia patients in early chronic phase.

Authors:  Francesca Palandri; Fausto Castagnetti; Ilaria Iacobucci; Giovanni Martinelli; Marilina Amabile; Gabriele Gugliotta; Angela Poerio; Nicoletta Testoni; Massimo Breccia; Monica Bocchia; Monica Crugnola; Giovanna Rege-Cambrin; Bruno Martino; Ivana Pierri; Franca Radaelli; Giorgina Specchia; Fabrizio Pane; Giuseppe Saglio; Gianantonio Rosti; Michele Baccarani
Journal:  Haematologica       Date:  2010-03-19       Impact factor: 9.941

6.  The clinical significance of achieving different levels of cytogenetic response in patients with chronic phase chronic myeloid leukemia after failure to front-line therapy: is complete cytogenetic response the only desirable endpoint?

Authors:  Jorge Cortes; Alfonso Quintas-Cardama; Elias Jabbour; Susan O'Brien; Srdan Verstovsek; Gautam Borthakur; Farhad Ravandi; Guillermo Garcia-Manero; Elizabeth Burton; Jenny Shan; Hagop Kantarjian
Journal:  Clin Lymphoma Myeloma Leuk       Date:  2011-08-10

Review 7.  Chronic myeloid leukemia in the tyrosine kinase inhibitor era: what is the "best" therapy?

Authors:  Meetu Agrawal; Ravin J Garg; Hagop Kantarjian; Jorge Cortes
Journal:  Curr Oncol Rep       Date:  2010-09       Impact factor: 5.075

Review 8.  Molecular resistance: an early indicator for treatment change?

Authors:  Carmen Fava; Hagop Kantarjian; Jorge Cortes
Journal:  Clin Lymphoma Myeloma Leuk       Date:  2012-01-28

Review 9.  Management of the new patient with CML in chronic phase.

Authors:  David Marin
Journal:  Curr Hematol Malig Rep       Date:  2013-03       Impact factor: 3.952

10.  Early results of lower dose dasatinib (50 mg daily) as frontline therapy for newly diagnosed chronic-phase chronic myeloid leukemia.

Authors:  Kiran Naqvi; Elias Jabbour; Jeffrey Skinner; Musa Yilmaz; Alessandra Ferrajoli; Prithviraj Bose; Philip Thompson; Yesid Alvarado; Nitin Jain; Koichi Takahashi; Jan Burger; Zeev Estrov; Gautam Borthakur; Naveen Pemmaraju; Shilpa Paul; Jorge Cortes; Hagop M Kantarjian
Journal:  Cancer       Date:  2018-05-03       Impact factor: 6.860

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