Literature DB >> 20007873

Gene therapy. Beta-thalassemia treatment succeeds, with a caveat.

Jocelyn Kaiser.   

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Year:  2009        PMID： 20007873     DOI： 10.1126/science.326.5959.1468-b

Source DB:  PubMed          Journal:  Science        ISSN： 0036-8075            Impact factor:   47.728


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  18 in total

1.  Lentiviral vector gene therapy: effective and safe?

Authors:  Derek A Persons
Journal:  Mol Ther       Date:  2010-05       Impact factor: 11.454

2.  A Low Protein Binding Cationic Poly(2-oxazoline) as Non-Viral Vector.

Authors:  Zhijian He; Lei Miao; Rainer Jordan; Devika S-Manickam; Robert Luxenhofer; Alexander V Kabanov
Journal:  Macromol Biosci       Date:  2015-04-02       Impact factor: 4.979

3.  Site-specific gene insertion mediated by a Cre-loxP-carrying lentiviral vector.

Authors:  Gilles Michel; Yin Yu; Tammy Chang; Jiing-Kuan Yee
Journal:  Mol Ther       Date:  2010-07-13       Impact factor: 11.454

4.  Advances in Gene Delivery Systems.

Authors:  Kenya Kamimura; Takeshi Suda; Guisheng Zhang; Dexi Liu
Journal:  Pharmaceut Med       Date:  2011-10-01

5.  Gene therapy by allele selection in a mouse model of beta-thalassemia.

Authors:  Sigrid Eckardt; N Adrian Leu; Ashley Yanchik; Seigo Hatada; Michael Kyba; K John McLaughlin
Journal:  J Clin Invest       Date:  2011-02       Impact factor: 14.808

6.  Therapeutic levels of fetal hemoglobin in erythroid progeny of β-thalassemic CD34+ cells after lentiviral vector-mediated gene transfer.

Authors:  Andrew Wilber; Phillip W Hargrove; Yoon-Sang Kim; Janice M Riberdy; Vijay G Sankaran; Eleni Papanikolaou; Maria Georgomanoli; Nicholas P Anagnou; Stuart H Orkin; Arthur W Nienhuis; Derek A Persons
Journal:  Blood       Date:  2010-12-14       Impact factor: 22.113

Review 7.  Two decades of clinical gene therapy--success is finally mounting.

Authors:  Roland W Herzog; Ou Cao; Arun Srivastava
Journal:  Discov Med       Date:  2010-02       Impact factor: 2.970

8.  A preclinical approach for gene therapy of beta-thalassemia.

Authors:  Laura Breda; Dorothy A Kleinert; Carla Casu; Laura Casula; Luca Cartegni; Eitan Fibach; Irene Mancini; Patricia J Giardina; Roberto Gambari; Stefano Rivella
Journal:  Ann N Y Acad Sci       Date:  2010-08       Impact factor: 5.691

9.  Rescue of severe infantile hypophosphatasia mice by AAV-mediated sustained expression of soluble alkaline phosphatase.

Authors:  Tae Matsumoto; Koichi Miyake; Seiko Yamamoto; Hideo Orimo; Noriko Miyake; Yuko Odagaki; Kumi Adachi; Osamu Iijima; Sonoko Narisawa; José Luis Millán; Yoshitaka Fukunaga; Takashi Shimada
Journal:  Hum Gene Ther       Date:  2011-06-08       Impact factor: 5.695

10.  Correction of beta-thalassemia major by gene transfer in haematopoietic progenitors of pediatric patients.

Authors:  Emanuela Anna Roselli; Riccardo Mezzadra; Marta Claudia Frittoli; Giulietta Maruggi; Erika Biral; Fulvio Mavilio; Fabrizio Mastropietro; Antonio Amato; Giovanni Tonon; Chiara Refaldi; Maria Domenica Cappellini; Marco Andreani; Guido Lucarelli; Maria Grazia Roncarolo; Sarah Marktel; Giuliana Ferrari
Journal:  EMBO Mol Med       Date:  2010-08       Impact factor: 12.137
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