Andy Extance. Show Affiliations »
Abstract
Entities: Disease
Mesh: See more » Gene Targeting/methodsHumansMuscular Dystrophy, Duchenne/geneticsMuscular Dystrophy, Duchenne/therapyMutationOligonucleotides, Antisense/therapeutic useProtein BiosynthesisRNA/metabolismTranscription, Genetic
Substances: See more » Oligonucleotides, AntisenseRNA
Year: 2009 PMID: 19949390 DOI: 10.1038/nrd3069
Source DB: PubMed Journal: Nat Rev Drug Discov ISSN: 1474-1776 Impact factor: 84.694