| Literature DB >> 19574581 |
Faten Tinsa1, Catherine Caillaud, Marie Thérèse Vanier, Dorra Bousnina, Khadija Boussetta, Souad Bousnina.
Abstract
Metachromatic leukodystrophy is an autosomal recessive neurodegenerative lysosomal disease characterized by a deficiency of the lysosomal enzyme arylsulfatase A and the subsequent accumulation of sulfatide in neuronal and visceral tissues. Clinical diagnosis is usually confirmed by in vitro analysis of arylsulfatase A activity but may be complicated in cases of arylsulfatase A pseudodeficiency and sphingolipid activators protein deficiency. We report the case of a 3-year-old boy who presented a severe form of late infantile metachromatic leukodystrophy. This patient was found to be homozygous for the arylsulfatase A pseudodeficiency. This condition is rare and can lead to a severe disease. Prenatal diagnosis was performed in this family, and the fetus was healthy.Entities:
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Year: 2009 PMID: 19574581 DOI: 10.1177/0883073809334382
Source DB: PubMed Journal: J Child Neurol ISSN: 0883-0738 Impact factor: 1.987