Literature DB >> 19469831

Enzyme replacement therapy in late-onset type II glycogenosis.

S Ravaglia, A Moglia, A Costa, A Repetto, C Danesino.   

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Year:  2009        PMID: 19469831     DOI: 10.1111/j.1468-1331.2009.02667.x

Source DB:  PubMed          Journal:  Eur J Neurol        ISSN: 1351-5101            Impact factor:   6.089


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  3 in total

1.  Long-term observational, non-randomized study of enzyme replacement therapy in late-onset glycogenosis type II.

Authors:  Bruno Bembi; Federica Edith Pisa; Marco Confalonieri; Giovanni Ciana; Agata Fiumara; Rossella Parini; Miriam Rigoldi; Arrigo Moglia; Alfredo Costa; Annalisa Carlucci; Cesare Danesino; Maria Gabriela Pittis; Andrea Dardis; Sabrina Ravaglia
Journal:  J Inherit Metab Dis       Date:  2010-09-14       Impact factor: 4.982

2.  Changes in skeletal muscle qualities during enzyme replacement therapy in late-onset type II glycogenosis: temporal and spatial pattern of mass vs. strength response.

Authors:  Sabrina Ravaglia; Anna Pichiecchio; Michela Ponzio; Cesare Danesino; Kolsoum Saeidi Garaghani; Guy Umberto Poloni; Antonio Toscano; Arrigo Moglia; Annalisa Carlucci; Paola Bini; Mauro Ceroni; Stefano Bastianello
Journal:  J Inherit Metab Dis       Date:  2010-09-16       Impact factor: 4.982

Review 3.  Consensus treatment recommendations for late-onset Pompe disease.

Authors:  Edward J Cupler; Kenneth I Berger; Robert T Leshner; Gil I Wolfe; Jay J Han; Richard J Barohn; John T Kissel
Journal:  Muscle Nerve       Date:  2011-12-15       Impact factor: 3.217

  3 in total

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