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Literature DB >> 19452286

Hematopoetic stem cell transplantation in neutrophil disorders: severe congenital neutropenia, leukocyte adhesion deficiency and chronic granulomatous disease.

Abstract

Until further progress will occur in the field of gene therapy, the only curative treatment available in severe congenital neutropenia, leukocyte adhesion deficiency, and chronic granulomatous disease is allogeneic hematopoietic stem cell transplantation (HSCT). This review summarizes the current data regarding indications for transplantation in each disease, treatment results using related and unrelated donors, as well as toxicity of HSCT in the above diseases.

Entities: Disease

Mesh：

Year: 2010 PMID： 19452286 DOI： 10.1007/s12016-009-8129-y

Source DB: PubMed Journal: Clin Rev Allergy Immunol ISSN： 1080-0549 Impact factor: 8.667

54 in total

1. Prolonged production of NADPH oxidase-corrected granulocytes after gene therapy of chronic granulomatous disease.

Authors: H L Malech; P B Maples; N Whiting-Theobald; G F Linton; S Sekhsaria; S J Vowells; F Li; J A Miller; E DeCarlo; S M Holland; S F Leitman; C S Carter; R E Butz; E J Read; T A Fleisher; R D Schneiderman; D E Van Epps; S K Spratt; C A Maack; J A Rokovich; L K Cohen; J I Gallin
Journal: Proc Natl Acad Sci U S A Date: 1997-10-28 Impact factor: 11.205

2. Matched unrelated donor bone marrow transplantation in leukocyte adhesion deficiency.

Authors: C Mancias; A J Infante; N R Kamani
Journal: Bone Marrow Transplant Date: 1999-12 Impact factor: 5.483

3. Correction of X-linked chronic granulomatous disease by gene therapy, augmented by insertional activation of MDS1-EVI1, PRDM16 or SETBP1.

Authors: Marion G Ott; Manfred Schmidt; Kerstin Schwarzwaelder; Stefan Stein; Ulrich Siler; Ulrike Koehl; Hanno Glimm; Klaus Kühlcke; Andrea Schilz; Hana Kunkel; Sonja Naundorf; Andrea Brinkmann; Annette Deichmann; Marlene Fischer; Claudia Ball; Ingo Pilz; Cynthia Dunbar; Yang Du; Nancy A Jenkins; Neal G Copeland; Ursula Lüthi; Moustapha Hassan; Adrian J Thrasher; Dieter Hoelzer; Christof von Kalle; Reinhard Seger; Manuel Grez
Journal: Nat Med Date: 2006-04-02 Impact factor: 53.440

Review 4. Gene therapy for chronic granulomatous disease.

Authors: Stefan Stein; Ulrich Siler; Marion G Ott; Reinhard Seger; Maunel Grez
Journal: Curr Opin Mol Ther Date: 2006-10

5. Neutrophil elastase mutations and risk of leukaemia in severe congenital neutropenia.

Authors: Philip S Rosenberg; Blanche P Alter; Daniel C Link; Steven Stein; Elin Rodger; Audrey A Bolyard; Andrew A Aprikyan; Mary A Bonilla; Yigal Dror; George Kannourakis; Peter E Newburger; Laurence A Boxer; David C Dale
Journal: Br J Haematol Date: 2007-11-20 Impact factor: 6.998

6. The incidence of leukemia and mortality from sepsis in patients with severe congenital neutropenia receiving long-term G-CSF therapy.

Authors: Philip S Rosenberg; Blanche P Alter; Audrey A Bolyard; Mary Ann Bonilla; Laurence A Boxer; Bonnie Cham; Carol Fier; Melvin Freedman; George Kannourakis; Sally Kinsey; Beate Schwinzer; Connie Zeidler; Karl Welte; David C Dale
Journal: Blood Date: 2006-02-23 Impact factor: 22.113

7. A novel form of integrin dysfunction involving beta1, beta2, and beta3 integrins.

Authors: Alison McDowall; David Inwald; Birgit Leitinger; Alison Jones; Ri Liesner; Nigel Klein; Nancy Hogg
Journal: J Clin Invest Date: 2003-01 Impact factor: 14.808

8. Unrelated cord blood transplantation for severe congenital neutropenia: report of two cases with very different transplant courses.

Authors: Melissa K Markel; Paul R Haut; Jamie A Renbarger; Kent A Robertson; W Scott Goebel
Journal: Pediatr Transplant Date: 2008-04-22

9. Results of allogeneic bone marrow transplantation in patients with leukocyte adhesion deficiency.

Authors: C Thomas; F Le Deist; M Cavazzana-Calvo; M Benkerrou; E Haddad; S Blanche; W Hartmann; W Friedrich; A Fischer
Journal: Blood Date: 1995-08-15 Impact factor: 22.113

10. Allogeneic hematopoietic stem-cell transplantation for leukocyte adhesion deficiency.

Authors: Waseem Qasim; Marina Cavazzana-Calvo; E Graham Davies; Jeffery Davis; Michel Duval; Gretchen Eames; Nuno Farinha; Alexandra Filopovich; Alain Fischer; Wilhelm Friedrich; Andrew Gennery; Carsten Heilmann; Paul Landais; Mitchell Horwitz; Fulvio Porta; Petr Sedlacek; Reinhard Seger; Mary Slatter; Mary Slatten; Lochie Teague; Mary Eapen; Paul Veys
Journal: Pediatrics Date: 2009-03 Impact factor: 7.124

4 in total

4. Allogeneic Transplant in ELANE and MEFV Mutation Positive Severe Cyclic Neutropenia: Review of Prognostic Factors for Secondary Severe Events.

Authors: Onyemaechi N Okolo; Emmanuel Katsanis; Seongseok Yun; Candace Y Reveles; Faiz Anwer
Journal: Case Rep Hematol Date: 2017-01-18