Literature DB >> 19293455

Gene therapy in large animal models of human genetic diseases. Introduction.

John H Wolfe1.   

Abstract

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Year:  2009        PMID： 19293455      PMCID： PMC2859173          DOI： 10.1093/ilar.50.2.107

Source DB:  PubMed          Journal:  ILAR J        ISSN： 1084-2020


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  32 in total

Review 1.  Stem cell gene transfer--efficacy and safety in large animal studies.

Authors:  Peter A Horn; Julia C Morris; Tobias Neff; Hans-Peter Kiem
Journal:  Mol Ther       Date:  2004-09       Impact factor: 11.454

Review 2.  Update on herpesvirus amplicon vectors.

Authors:  Angelika Oehmig; Cornel Fraefel; Xandra O Breakefield
Journal:  Mol Ther       Date:  2004-10       Impact factor: 11.454

Review 3.  Biology of adenovirus and its use as a vector for gene therapy.

Authors:  Michael J McConnell; Michael J Imperiale
Journal:  Hum Gene Ther       Date:  2004-11       Impact factor: 5.695

4.  Gene therapy restores vision in a canine model of childhood blindness.

Authors:  G M Acland; G D Aguirre; J Ray; Q Zhang; T S Aleman; A V Cideciyan; S E Pearce-Kelling; V Anand; Y Zeng; A M Maguire; S G Jacobson; W W Hauswirth; J Bennett
Journal:  Nat Genet       Date:  2001-05       Impact factor: 38.330

Review 5.  Research on genetic diseases: reciprocal benefits to animals and man.

Authors:  D F Patterson; M E Haskins; P F Jezyk; U Giger; V N Meyers-Wallen; G Aguirre; J C Fyfe; J H Wolfe
Journal:  J Am Vet Med Assoc       Date:  1988-11-01       Impact factor: 1.936

Review 6.  Large animal models and gene therapy.

Authors:  Margret Casal; Mark Haskins
Journal:  Eur J Hum Genet       Date:  2006-03       Impact factor: 4.246

7.  Effective gene therapy for an inherited CNS disease in a large animal model.

Authors:  Charles H Vite; Joseph C McGowan; Sumit N Niogi; Marco A Passini; Kenneth J Drobatz; Mark E Haskins; John H Wolfe
Journal:  Ann Neurol       Date:  2005-03       Impact factor: 10.422

Review 8.  AAV-mediated gene therapy for retinal disorders in large animal models.

Authors:  Knut Stieger; Elsa Lhériteau; Elsa Lhéariteau; Phillip Moullier; Fabienne Rolling
Journal:  ILAR J       Date:  2009

Review 9.  Preclinical animal models for hemophilia gene therapy: predictive value and limitations.

Authors:  Fiona E M Rawle; David Lillicrap
Journal:  Semin Thromb Hemost       Date:  2004-04       Impact factor: 4.180

Review 10.  Gene therapy for lysosomal storage diseases: the lessons and promise of animal models.

Authors:  N Matthew Ellinwood; Charles H Vite; Mark E Haskins
Journal:  J Gene Med       Date:  2004-05       Impact factor: 4.565
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  8 in total

Review 1.  Overcoming Gene-Delivery Hurdles: Physiological Considerations for Nonviral Vectors.

Authors:  Andrew B Hill; Mingfu Chen; Chih-Kuang Chen; Blaine A Pfeifer; Charles H Jones
Journal:  Trends Biotechnol       Date:  2015-12-23       Impact factor: 19.536

Review 2.  Drug discovery and development for rare genetic disorders.

Authors:  Wei Sun; Wei Zheng; Anton Simeonov
Journal:  Am J Med Genet A       Date:  2017-07-21       Impact factor: 2.802

Review 3.  Progress in gene therapy for neurological disorders.

Authors:  Michele Simonato; Jean Bennett; Nicholas M Boulis; Maria G Castro; David J Fink; William F Goins; Steven J Gray; Pedro R Lowenstein; Luk H Vandenberghe; Thomas J Wilson; John H Wolfe; Joseph C Glorioso
Journal:  Nat Rev Neurol       Date:  2013-04-23       Impact factor: 42.937

4.  Optimizing culture conditions of a porcine epithelial cell line IPEC-J2 through a histological and physiological characterization.

Authors:  Marisa M Geens; Theo A Niewold
Journal:  Cytotechnology       Date:  2011-05-29       Impact factor: 2.058

Review 5.  Precision editing of large animal genomes.

Authors:  Wenfang Spring Tan; Daniel F Carlson; Mark W Walton; Scott C Fahrenkrug; Perry B Hackett
Journal:  Adv Genet       Date:  2012       Impact factor: 1.944

Review 6.  Perspectives of pluripotent stem cells in livestock.

Authors:  Dharmendra Kumar; Thirumala R Talluri; Naresh L Selokar; Iqbal Hyder; Wilfried A Kues
Journal:  World J Stem Cells       Date:  2021-01-26       Impact factor: 5.326

Review 7.  Muscular dystrophy: Experimental animal models and therapeutic approaches (Review).

Authors:  Gisela Gaina; Alexandra Popa Gruianu
Journal:  Exp Ther Med       Date:  2021-04-14       Impact factor: 2.447

Review 8.  Preclinical Development of Autologous Hematopoietic Stem Cell-Based Gene Therapy for Immune Deficiencies: A Journey from Mouse Cage to Bed Side.

Authors:  Laura Garcia-Perez; Anita Ordas; Kirsten Canté-Barrett; Pauline Meij; Karin Pike-Overzet; Arjan Lankester; Frank J T Staal
Journal:  Pharmaceutics       Date:  2020-06-13       Impact factor: 6.321
  8 in total

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