Literature DB >> 18945748

Donor/recipient mixed chimerism does not predict graft failure in children with beta-thalassemia given an allogeneic cord blood transplant from an HLA-identical sibling.

Daniela Lisini1, Marco Zecca, Giovanna Giorgiani, Daniela Montagna, Rosaria Cristantielli, Massimo Labirio, Pierangela Grignani, Carlo Previderè, Alessandra Di Cesare-Merlone, Giovanni Amendola, Elena Bergami, Angela Mastronuzzi, Rita Maccario, Franco Locatelli.   

Abstract

BACKGROUND: Donor/recipient mixed chimerism has been reported to be associated with an increased risk of graft failure in patients with beta-thalassemia given a bone marrow transplant. We investigated the relationship between the degree of mixed chimerism over time and clinical outcome of children undergoing cord blood transplantation for beta-thalassemia. DESIGN AND METHODS: Twenty-seven consecutive children given a cord blood transplant from a related donor were analyzed by short tandem repeat polymerase chain reaction and their chimerism results were compared with those of 79 consecutive patients who received a bone marrow transplant from either a relative (RD-BMT, n=42) or an unrelated donor (UD-BMT, n=37). Cord blood and bone marrow recipients received comparable preparative regimens.
RESULTS: All cord blood recipients engrafted and displayed mixed chimerism early after transplantation; 13/27 converted to full donor chimerism over time, while 14 maintained stable mixed chimerism; all patients are alive and transfusion-independent. Twenty-four of the 79 bone marrow-recipients (12 UD- and 12 RD-BMT) exhibited full donor chimerism at all time points examined, 4/79 (2 UD- and 2 RD-BMT) did not engraft and 51/79 (23 UD- and 28 RD-BMT) displayed mixed chimerism at the time of hematologic reconstitution. Forty of 51 bone marrow recipients with mixed chimerism converted to full donor chimerism (17 UD- and 23 RD-BMT), 3/51 maintained stable mixed chimerism (1 UD- and 2 RD-BMT), while 8/51 (5 UD- and 3 RD-BMT) progressively lost the graft, and became transfusion-dependent again.
CONCLUSIONS: Mixed chimerism is a frequent event and does not predict the occurrence of graft failure in children with beta-thalassemia given a cord blood transplant from a relative.

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Year:  2008        PMID: 18945748     DOI: 10.3324/haematol.13248

Source DB:  PubMed          Journal:  Haematologica        ISSN: 0390-6078            Impact factor:   9.941


  19 in total

1.  Umbilical cord blood transplantation for children with thalassemia and sickle cell disease.

Authors:  Annalisa Ruggeri; Mary Eapen; Andromachi Scaravadou; Mitchell S Cairo; Monica Bhatia; Joanne Kurtzberg; John R Wingard; Anders Fasth; Luca Lo Nigro; Mouhab Ayas; Duncan Purtill; Karim Boudjedir; Wagnara Chaves; Mark C Walters; John Wagner; Eliane Gluckman; Vanderson Rocha
Journal:  Biol Blood Marrow Transplant       Date:  2011-01-28       Impact factor: 5.742

2.  In mixed hematopoietic chimerism, the donor red cells win.

Authors:  Matthew M Hsieh; Catherine J Wu; John F Tisdale
Journal:  Haematologica       Date:  2011-01       Impact factor: 9.941

3.  Challenges and opportunities for international cooperative studies in pediatric hematopoeitic cell transplantation: priorities of the Westhafen Intercontinental Group.

Authors:  Rudolph Kirk R Schultz; Kevin Scott Baker; Jaap J Boelens; Catherine M Bollard; R Maarten Egeler; Mort Cowan; Ruth Ladenstein; Arjan Lankester; Franco Locatelli; Anita Lawitschka; John E Levine; Mignon Loh; Eneida Nemecek; Charlotte Niemeyer; Vinod K Prasad; Vanderson Rocha; Shalini Shenoy; Brigitte Strahm; Paul Veys; Donna Wall; Peter Bader; Stephan A Grupp; Michael A Pulsipher; Christina Peters
Journal:  Biol Blood Marrow Transplant       Date:  2013-07-21       Impact factor: 5.742

4.  The case for HLA-identical sibling hematopoietic stem cell transplantation in children with symptomatic sickle cell anemia.

Authors:  Courtney D Fitzhugh; Mark C Walters
Journal:  Blood Adv       Date:  2017-12-08

5.  Pharmacologic modulation of niche accessibility via tyrosine kinase inhibition enhances marrow and thymic engraftment after hematopoietic stem cell transplantation.

Authors:  Natasha M Fewkes; Aviva C Krauss; Martin Guimond; Joanna L Meadors; Stefania Dobre; Crystal L Mackall
Journal:  Blood       Date:  2010-03-15       Impact factor: 22.113

6.  Hematopoietic stem cell transplantation in thalassemia major and sickle cell disease: indications and management recommendations from an international expert panel.

Authors:  Emanuele Angelucci; Susanne Matthes-Martin; Donatella Baronciani; Françoise Bernaudin; Sonia Bonanomi; Maria Domenica Cappellini; Jean-Hugues Dalle; Paolo Di Bartolomeo; Cristina Díaz de Heredia; Roswitha Dickerhoff; Claudio Giardini; Eliane Gluckman; Ayad Achmed Hussein; Naynesh Kamani; Milen Minkov; Franco Locatelli; Vanderson Rocha; Petr Sedlacek; Frans Smiers; Isabelle Thuret; Isaac Yaniv; Marina Cavazzana; Christina Peters
Journal:  Haematologica       Date:  2014-05       Impact factor: 9.941

7.  Distribution of lentiviral vector integration sites in mice following therapeutic gene transfer to treat β-thalassemia.

Authors:  Keshet Ronen; Olivier Negre; Shannah Roth; Charlotte Colomb; Nirav Malani; Maria Denaro; Troy Brady; Floriane Fusil; Beatrix Gillet-Legrand; Kathleen Hehir; Yves Beuzard; Philippe Leboulch; Julian D Down; Emmanuel Payen; Frederic D Bushman
Journal:  Mol Ther       Date:  2011-03-08       Impact factor: 11.454

8.  Therapeutic effects of induced pluripotent stem cells in chimeric mice with β-thalassemia.

Authors:  Guanheng Yang; Wansheng Shi; Xingyin Hu; Jingzhi Zhang; Zhijuan Gong; Xinbing Guo; Zhaorui Ren; Fanyi Zeng
Journal:  Haematologica       Date:  2014-05-09       Impact factor: 9.941

Review 9.  Umbilical cord blood: an evolving stem cell source for sickle cell disease transplants.

Authors:  Shalini Shenoy
Journal:  Stem Cells Transl Med       Date:  2013-04-11       Impact factor: 6.940

10.  Type 1 regulatory T cells are associated with persistent split erythroid/lymphoid chimerism after allogeneic hematopoietic stem cell transplantation for thalassemia.

Authors:  Giorgia Serafini; Marco Andreani; Manuela Testi; MariaRosa Battarra; Andrea Bontadini; Eika Biral; Katharina Fleischhauer; Sarah Marktel; Guido Lucarelli; Maria Grazia Roncarolo; Rosa Bacchetta
Journal:  Haematologica       Date:  2009-07-16       Impact factor: 9.941

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