Warning: Undefined array key "mm" in /www/wwwroot/www.ai-bt.com/si.php on line 10 Deprecated: trim(): Passing null to parameter #1 ($string) of type string is deprecated in /www/wwwroot/www.ai-bt.com/si.php on line 10 Intramuscular administration of AAV1-lipoprotein lipase S447X lowers triglycerides in lipoprotein lipase-deficient patients.

Literature DB >> 18802015

Intramuscular administration of AAV1-lipoprotein lipase S447X lowers triglycerides in lipoprotein lipase-deficient patients.

Erik S Stroes¹, Melchior C Nierman, Janneke J Meulenberg, Remco Franssen, Jaap Twisk, C Pieter Henny, Mario M Maas, Aeilko H Zwinderman, Colin Ross, Eleonora Aronica, Katherine A High, Marcel M Levi, Michael R Hayden, John J Kastelein, Jan Albert Kuivenhoven.

Abstract

Entities: Chemical Disease Gene Mutation Species

Mesh：

Substances：

Year: 2008 PMID： 18802015 DOI： 10.1161/ATVBAHA.108.175620

Source DB: PubMed Journal: Arterioscler Thromb Vasc Biol ISSN： 1079-5642 Impact factor: 8.311

Keyword Cloud
Cited

× No keyword cloud information.

81 in total

1. Adeno-Associated Virus: The Naturally Occurring Virus Versus the Recombinant Vector.

Authors: Arun Srivastava
Journal: Hum Gene Ther Date: 2016-01 Impact factor: 5.695

Review 2. Adeno-associated Virus as a Mammalian DNA Vector.

Authors: Max Salganik; Matthew L Hirsch; Richard Jude Samulski
Journal: Microbiol Spectr Date: 2015-08

Review 3. The AAV vector toolkit: poised at the clinical crossroads.

Authors: Aravind Asokan; David V Schaffer; R Jude Samulski
Journal: Mol Ther Date: 2012-01-24 Impact factor: 11.454

4. Peripheral transvenular delivery of adeno-associated viral vectors to skeletal muscle as a novel therapy for hemophilia B.

Authors: Valder R Arruda; Hansell H Stedman; Virginia Haurigot; George Buchlis; Stefano Baila; Patricia Favaro; Yifeng Chen; Helen G Franck; Shangzhen Zhou; J Fraser Wright; Linda B Couto; Haiyan Jiang; Glenn F Pierce; Dwight A Bellinger; Federico Mingozzi; Timothy C Nichols; Katherine A High
Journal: Blood Date: 2010-03-24 Impact factor: 22.113

Review 5. Therapeutic in vivo gene transfer for genetic disease using AAV: progress and challenges.

Authors: Federico Mingozzi; Katherine A High
Journal: Nat Rev Genet Date: 2011-05 Impact factor: 53.242

6. AAV-1-mediated gene transfer to skeletal muscle in humans results in dose-dependent activation of capsid-specific T cells.

Authors: Federico Mingozzi; Janneke J Meulenberg; Daniel J Hui; Etiena Basner-Tschakarjan; Nicole C Hasbrouck; Shyrie A Edmonson; Natalie A Hutnick; Michael R Betts; John J Kastelein; Erik S Stroes; Katherine A High
Journal: Blood Date: 2009-06-08 Impact factor: 22.113

Intramuscular administration of AAV1-lipoprotein lipase S447X lowers triglycerides in lipoprotein lipase-deficient patients.

1. Adeno-Associated Virus: The Naturally Occurring Virus Versus the Recombinant Vector.

Review 2. Adeno-associated Virus as a Mammalian DNA Vector.

Review 3. The AAV vector toolkit: poised at the clinical crossroads.

4. Peripheral transvenular delivery of adeno-associated viral vectors to skeletal muscle as a novel therapy for hemophilia B.

Review 5. Therapeutic in vivo gene transfer for genetic disease using AAV: progress and challenges.

6. AAV-1-mediated gene transfer to skeletal muscle in humans results in dose-dependent activation of capsid-specific T cells.

Review 7. Plasma lipoproteins: genetic influences and clinical implications.

Review 8. Lessons learned from the clinical development and market authorization of Glybera.

9. Gene delivery to rat and human Schwann cells and nerve segments: a comparison of AAV 1-9 and lentiviral vectors.

Review 10. Genetic determinants of plasma triglycerides.