Literature DB >> 18578029

Genetic modification of somatic stem cells. The progress, problems and prospects of a new therapeutic technology.

Fulvio Mavilio1, Giuliana Ferrari.   

Abstract

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Year:  2008        PMID： 18578029      PMCID： PMC3327547          DOI： 10.1038/embor.2008.81

Source DB:  PubMed          Journal:  EMBO Rep        ISSN： 1469-221X            Impact factor:   8.807


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  23 in total

Review 1.  Primary immunodeficiency diseases: an experimental model for molecular medicine.

Authors:  A Fischer
Journal:  Lancet       Date:  2001-06-09       Impact factor: 79.321

Review 2.  Stem cell transplantation for hemoglobinopathies.

Authors:  Javid Gaziev; Guido Lucarelli
Journal:  Curr Opin Pediatr       Date:  2003-02       Impact factor: 2.856

Review 3.  The cure of thalassemia by bone marrow transplantation.

Authors:  G Lucarelli; M Andreani; E Angelucci
Journal:  Blood Rev       Date:  2002-06       Impact factor: 8.250

4.  Gene therapy of human severe combined immunodeficiency (SCID)-X1 disease.

Authors:  M Cavazzana-Calvo; S Hacein-Bey; G de Saint Basile; F Gross; E Yvon; P Nusbaum; F Selz; C Hue; S Certain; J L Casanova; P Bousso; F L Deist; A Fischer
Journal:  Science       Date:  2000-04-28       Impact factor: 47.728

5.  Functional requirements for phenotypic correction of murine beta-thalassemia: implications for human gene therapy.

Authors:  D A Persons; E R Allay; D E Sabatino; P Kelly; D M Bodine; A W Nienhuis
Journal:  Blood       Date:  2001-05-15       Impact factor: 22.113

6.  Long-term survival and transplantation of haemopoietic stem cells for immunodeficiencies: report of the European experience 1968-99.

Authors:  Corinne Antoine; Susanna Müller; Andrew Cant; Marina Cavazzana-Calvo; Paul Veys; Jaak Vossen; Anders Fasth; Carsten Heilmann; Nicolas Wulffraat; Reinhard Seger; Stéphane Blanche; Wilhelm Friedrich; Mario Abinun; Graham Davies; Robert Bredius; Ansgar Schulz; Paul Landais; Alain Fischer
Journal:  Lancet       Date:  2003-02-15       Impact factor: 79.321

7.  Fatal systemic inflammatory response syndrome in a ornithine transcarbamylase deficient patient following adenoviral gene transfer.

Authors:  Steven E Raper; Narendra Chirmule; Frank S Lee; Nelson A Wivel; Adam Bagg; Guang-ping Gao; James M Wilson; Mark L Batshaw
Journal:  Mol Genet Metab       Date:  2003 Sep-Oct       Impact factor: 4.797

8.  LMO2-associated clonal T cell proliferation in two patients after gene therapy for SCID-X1.

Authors:  S Hacein-Bey-Abina; C Von Kalle; M Schmidt; M P McCormack; N Wulffraat; P Leboulch; A Lim; C S Osborne; R Pawliuk; E Morillon; R Sorensen; A Forster; P Fraser; J I Cohen; G de Saint Basile; I Alexander; U Wintergerst; T Frebourg; A Aurias; D Stoppa-Lyonnet; S Romana; I Radford-Weiss; F Gross; F Valensi; E Delabesse; E Macintyre; F Sigaux; J Soulier; L E Leiva; M Wissler; C Prinz; T H Rabbitts; F Le Deist; A Fischer; M Cavazzana-Calvo
Journal:  Science       Date:  2003-10-17       Impact factor: 47.728

9.  In vivo selection of genetically modified erythroblastic progenitors leads to long-term correction of beta-thalassemia.

Authors:  Annarita Miccio; Rossano Cesari; Francesco Lotti; Claudia Rossi; Francesca Sanvito; Maurilio Ponzoni; Samantha J E Routledge; Cheok-Man Chow; Michael N Antoniou; Giuliana Ferrari
Journal:  Proc Natl Acad Sci U S A       Date:  2008-07-23       Impact factor: 11.205

10.  Correction of ADA-SCID by stem cell gene therapy combined with nonmyeloablative conditioning.

Authors:  Alessandro Aiuti; Shimon Slavin; Memet Aker; Francesca Ficara; Sara Deola; Alessandra Mortellaro; Shoshana Morecki; Grazia Andolfi; Antonella Tabucchi; Filippo Carlucci; Enrico Marinello; Federica Cattaneo; Sergio Vai; Paolo Servida; Roberto Miniero; Maria Grazia Roncarolo; Claudio Bordignon
Journal:  Science       Date:  2002-06-28       Impact factor: 47.728
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  4 in total

1.  Ex-vivo gene therapy restores LEKTI activity and corrects the architecture of Netherton syndrome-derived skin grafts.

Authors:  Wei-Li Di; Fernado Larcher; Ekaterina Semenova; Gill E Talbot; John I Harper; Marcela Del Rio; Adrian J Thrasher; Waseem Qasim
Journal:  Mol Ther       Date:  2010-09-28       Impact factor: 11.454

Review 2.  Towards a therapy for phosphomannomutase 2 deficiency, the defect in CDG-Ia patients.

Authors:  Hudson H Freeze
Journal:  Biochim Biophys Acta       Date:  2009-09

3.  Genome-wide Profiling Reveals Remarkable Parallels Between Insertion Site Selection Properties of the MLV Retrovirus and the piggyBac Transposon in Primary Human CD4(+) T Cells.

Authors:  Andreas Gogol-Döring; Ismahen Ammar; Saumyashree Gupta; Mario Bunse; Csaba Miskey; Wei Chen; Wolfgang Uckert; Thomas F Schulz; Zsuzsanna Izsvák; Zoltán Ivics
Journal:  Mol Ther       Date:  2016-01-12       Impact factor: 11.454

Review 4.  Battling Neurodegenerative Diseases with Adeno-Associated Virus-Based Approaches.

Authors:  Olja Mijanović; Ana Branković; Anton Borovjagin; Denis V Butnaru; Evgeny A Bezrukov; Roman B Sukhanov; Anastasia Shpichka; Peter Timashev; Ilya Ulasov
Journal:  Viruses       Date:  2020-04-18       Impact factor: 5.048
  4 in total

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