Literature DB >> 17984995

Progress and prospects: gene therapy clinical trials (part 2).

Eric Alton1, Stefano Ferrari, Uta Griesenbach, A Aiuti, A C Bachoud-Lévi, A Blesch, M K Brenner, F Cattaneo, E A Chiocca, G Gao, K A High, A M Leen, N R Lemoine, I A McNeish, G Meneguzzi, M Peschanski, M G Roncarolo, D S Strayer, M H Tuszynski, D J Waxman, J M Wilson.   

Abstract

This is the second part of a review summarizing progress and prospects in gene therapy clinical research. Twenty key diseases/strategies are succinctly described and commented on by leaders in the field. This part includes clinical trials for skin diseases, neurological disorders, HIV/AIDS, ornithine transcarbamylase deficiency, alpha(1)-antitrypsin deficiency, haemophilia and cancer.

Entities:  

Mesh:

Year:  2007        PMID: 17984995     DOI: 10.1038/sj.gt.3303033

Source DB:  PubMed          Journal:  Gene Ther        ISSN: 0969-7128            Impact factor:   5.250


  24 in total

Review 1.  Chlorotoxin-conjugated nanoparticles as potential glioma-targeted drugs.

Authors:  Yuejun Fu; Na An; Ke Li; Yali Zheng; Aihua Liang
Journal:  J Neurooncol       Date:  2011-11-23       Impact factor: 4.130

Review 2.  Exosomes and their Application in Biomedical Field: Difficulties and Advantages.

Authors:  Jafar Rezaie; Saeed Ajezi; Çığır Biray Avci; Mohammad Karimipour; Mohammad Hossein Geranmayeh; Alireza Nourazarian; Emel Sokullu; Aysa Rezabakhsh; Reza Rahbarghazi
Journal:  Mol Neurobiol       Date:  2017-05-11       Impact factor: 5.590

Review 3.  Current status of non-viral gene therapy for CNS disorders.

Authors:  Rahul Dev Jayant; Daniela Sosa; Ajeet Kaushik; Venkata Atluri; Arti Vashist; Asahi Tomitaka; Madhavan Nair
Journal:  Expert Opin Drug Deliv       Date:  2016-06-01       Impact factor: 6.648

4.  Gene and cell therapy based treatment strategies for inflammatory bowel diseases.

Authors:  Sander van der Marel; Anna Majowicz; Sander van Deventer; Harald Petry; Daniel W Hommes; Valerie Ferreira
Journal:  World J Gastrointest Pathophysiol       Date:  2011-12-15

5.  An adeno-associated virus vector efficiently and specifically transduces mouse skeletal muscle.

Authors:  Isao Murakami; Takamasa Takeuchi; Mayuyo Mori-Uchino; Seiichiro Mori; Takuma Fujii; Daisuke Aoki; Keiichi Nakagawa; Tadahito Kanda
Journal:  Mol Biotechnol       Date:  2011-09       Impact factor: 2.695

6.  Selective gene transfection of individual cells in vitro with plasmonic nanobubbles.

Authors:  Ekaterina Y Lukianova-Hleb; Adam P Samaniego; Jianguo Wen; Leonid S Metelitsa; Chung-Che Chang; Dmitri O Lapotko
Journal:  J Control Release       Date:  2011-02-17       Impact factor: 9.776

7.  A ligand-mediated nanovector for targeted gene delivery and transfection in cancer cells.

Authors:  Omid Veiseh; Forrest M Kievit; Jonathan W Gunn; Buddy D Ratner; Miqin Zhang
Journal:  Biomaterials       Date:  2008-11-05       Impact factor: 12.479

8.  Cytotoxic T lymphocyte responses to transgene product, not adeno-associated viral capsid protein, limit transgene expression in mice.

Authors:  William M Siders; Jacqueline Shields; Johanne Kaplan; Michael Lukason; Lisa Woodworth; Sam Wadsworth; Abraham Scaria
Journal:  Hum Gene Ther       Date:  2009-01       Impact factor: 5.695

9.  Analysis of adenovirus trans-complementation-mediated gene expression controlled by melanoma-specific TETP promoter in vitro.

Authors:  Alessandra Curioni Fontecedro; Verena Lutschg; Ossia Eichhoff; Reinhard Dummer; Urs F Greber; Silvio Hemmi
Journal:  Virol J       Date:  2010-07-29       Impact factor: 4.099

10.  Design of hybrid lipid/retroviral-like particle gene delivery vectors.

Authors:  Rahul K Keswani; Ian M Pozdol; Daniel W Pack
Journal:  Mol Pharm       Date:  2013-03-26       Impact factor: 4.939

View more

北京卡尤迪生物科技股份有限公司 © 2022-2023.