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Literature DB >> 17915570

Progress and problems when considering gene therapy for GSD-II.

A Kiang¹, A Amalfitano.

Abstract

Entities: Disease

Mesh：

Substances：

Year: 2007 PMID： 17915570 PMCID： PMC2949318

Source DB: PubMed Journal: Acta Myol ISSN： 1128-2460

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43 in total

Review 1. Update on adenovirus and its vectors.

Authors: W C Russell
Journal: J Gen Virol Date: 2000-11 Impact factor: 3.891

2. Acute cytokine response to systemic adenoviral vectors in mice is mediated by dendritic cells and macrophages.

Authors: Y Zhang; N Chirmule; G P Gao; R Qian; M Croyle; B Joshi; J Tazelaar; J M Wilson
Journal: Mol Ther Date: 2001-05 Impact factor: 11.454

3. Multiple innate inflammatory responses induced after systemic adenovirus vector delivery depend on a functional complement system.

Authors: Anne Kiang; Zachary C Hartman; Ruth S Everett; Delila Serra; Haixiang Jiang; Michael M Frank; Andrea Amalfitano
Journal: Mol Ther Date: 2006-06-02 Impact factor: 11.454

4. Recombinant adeno-associated virus serotype 9 leads to preferential cardiac transduction in vivo.

Authors: Christina A Pacak; Cathryn S Mah; Bijoy D Thattaliyath; Thomas J Conlon; Melissa A Lewis; Denise E Cloutier; Irene Zolotukhin; Alice F Tarantal; Barry J Byrne
Journal: Circ Res Date: 2006-07-27 Impact factor: 17.367

5. Intercellular transfer of the virally derived precursor form of acid alpha-glucosidase corrects the enzyme deficiency in inherited cardioskeletal myopathy Pompe disease.

Authors: D F Pauly; T J Fraites; C Toma; H S Bayes; M L Huie; R Hirschhorn; P H Plotz; N Raben; P D Kessler; B J Byrne
Journal: Hum Gene Ther Date: 2001-03-20 Impact factor: 5.695

6. Recombinant human alpha-glucosidase from rabbit milk in Pompe patients.

Authors: H Van den Hout; A J Reuser; A G Vulto; M C Loonen; A Cromme-Dijkhuis; A T Van der Ploeg
Journal: Lancet Date: 2000-07-29 Impact factor: 79.321

7. Fully deleted adenovirus persistently expressing GAA accomplishes long-term skeletal muscle glycogen correction in tolerant and nontolerant GSD-II mice.

Authors: Anne Kiang; Zachary C Hartman; Shaoxi Liao; Fang Xu; Delila Serra; Donna J Palmer; Philip Ng; Andrea Amalfitano
Journal: Mol Ther Date: 2005-10-05 Impact factor: 11.454

Review 8. Adenovirus: from foe to friend.

Authors: Manuel A F V Gonçalves; Antoine A F de Vries
Journal: Rev Med Virol Date: 2006 May-Jun Impact factor: 6.989

9. Biology of E1-deleted adenovirus vectors in nonhuman primate muscle.

Authors: P W Zoltick; N Chirmule; M A Schnell; G P Gao; J V Hughes; J M Wilson
Journal: J Virol Date: 2001-06 Impact factor: 5.103

10. Recombinant human acid alpha-glucosidase enzyme therapy for infantile glycogen storage disease type II: results of a phase I/II clinical trial.

Authors: A Amalfitano; A R Bengur; R P Morse; J M Majure; L E Case; D L Veerling; J Mackey; P Kishnani; W Smith; A McVie-Wylie; J A Sullivan; G E Hoganson; J A Phillips; G B Schaefer; J Charrow; R E Ware; E H Bossen; Y T Chen
Journal: Genet Med Date: 2001 Mar-Apr Impact factor: 8.822

3 in total