Literature DB >> 16720667

Diagnosis of parathyroid tumors in familial isolated hyperparathyroidism with HRPT2 mutation: implications for cancer surveillance.

Vito Guarnieri1, Alfredo Scillitani, Lucia Anna Muscarella, Claudia Battista, Nazzareno Bonfitto, Michele Bisceglia, Salvatore Minisola, Maria Lucia Mascia, Leonardo D'Agruma, David E C Cole.   

Abstract

CONTEXT: Mutations of the HRPT2 gene have recently been implicated in the development of parathyroid carcinoma.
OBJECTIVE: The objective of this study was early diagnosis of parathyroid tumor in a family with germline HRPT2 mutation. PATIENTS, METHODS, AND
RESULTS: In a 40-yr-old male previously treated for parathyroid atypical adenoma, we screened the 17 translated HRPT2 exons and their exon-intron boundaries and found a germline frameshift mutation in exon 7 (685delAGAG) predicting a premature stop codon at nucleotides 767-769. Nine family members (age, 33.9 +/- 19.8 yr, mean +/- SD) also carry the mutation, but eight have had normal serum calcium. Biochemical and ultrasonographic evaluation uncovered a 27-yr-old hypercalcemic carrier niece with an atypical parathyroid adenoma, and a 43-yr-old normocalcemic carrier sister was found by ultrasonography to have an extrathyroidal nodule, which proved to be parathyroid carcinoma. The index case, 12 yr after surgery, was normocalcemic, but ultrasonography revealed an extrathyroidal nodule in the contralateral hemithyroid tissue that proved to be atypical adenoma.
CONCLUSIONS: Our report confirms that germline mutations of HRPT2 gene may be associated with multiple parathyroid neoplasms. Our experience suggests that longitudinal surveillance by serum biochemistry alone may not be 100% sensitive, and addition of routine neck ultrasonography is a readily accepted adjunct that may facilitate earlier disease detection in some families.

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Year:  2006        PMID: 16720667     DOI: 10.1210/jc.2005-1239

Source DB:  PubMed          Journal:  J Clin Endocrinol Metab        ISSN: 0021-972X            Impact factor:   5.958


  32 in total

Review 1.  Evolution of Our Understanding of the Hyperparathyroid Syndromes: A Historical Perspective.

Authors:  Stephen J Marx; David Goltzman
Journal:  J Bone Miner Res       Date:  2018-12-10       Impact factor: 6.741

2.  Allelic imbalance in sporadic parathyroid carcinoma and evidence for its de novo origins.

Authors:  Jessica Costa-Guda; Yasuo Imanishi; Nallasivam Palanisamy; Norihiko Kawamata; H Phillip Koeffler; R S K Chaganti; Andrew Arnold
Journal:  Endocrine       Date:  2013-02-24       Impact factor: 3.633

3.  Novel nonsense CDC73 mutations in Chinese patients with parathyroid tumors.

Authors:  Wai Kwan Siu; Chun Yiu Law; Ching Wan Lam; Chloe Miu Mak; Gary Wing Kin Wong; Andrew Yiu Yan Ho; Kwok Yip Ho; Ka Tai Loo; Sin Chuen Chiu; Louis Tsun Cheung Chow; Sui Fan Tong; Albert Yan Wo Chan
Journal:  Fam Cancer       Date:  2011-12       Impact factor: 2.375

Review 4.  Genetic basis of familial isolated hyperparathyroidism: a case series and a narrative review of the literature.

Authors:  Nikolaos Pontikides; Spyridon Karras; Athina Kaprara; Panagiotis Anagnostis; Gesthimani Mintziori; Dimitrios G Goulis; Eleni Memi; Gerasimos Krassas
Journal:  J Bone Miner Metab       Date:  2014-01-19       Impact factor: 2.626

5.  Non-functioning parathyroid cystic tumour: malignant or not? Report of a case.

Authors:  G Cocorullo; G Scerrino; G Melfa; C Raspanti; G Rotolo; V Mannino; P Richiusa; D Cabibi; A G Giannone; C Porrello; G Gulotta
Journal:  G Chir       Date:  2017 Sep-Oct

6.  Expression, function, and regulation of the embryonic transcription factor TBX1 in parathyroid tumors.

Authors:  Chiara Verdelli; Laura Avagliano; Vito Guarnieri; Filomena Cetani; Stefano Ferrero; Leonardo Vicentini; Edoardo Beretta; Alfredo Scillitani; Pasquale Creo; Gaetano Pietro Bulfamante; Valentina Vaira; Sabrina Corbetta
Journal:  Lab Invest       Date:  2017-09-18       Impact factor: 5.662

7.  The parafibromin tumor suppressor protein inhibits cell proliferation by repression of the c-myc proto-oncogene.

Authors:  Ling Lin; Jian-Hua Zhang; Leelamma M Panicker; William F Simonds
Journal:  Proc Natl Acad Sci U S A       Date:  2008-11-05       Impact factor: 11.205

8.  Hyperparathyroidism 2 gene (HRPT2, CDC73) and parafibromin studies in two patients with primary hyperparathyroidism and uncertain pathological assessment.

Authors:  F Cetani; E Pardi; E Ambrogini; C Banti; P Viacava; S Borsari; J P Bilezikian; A Pinchera; C Marcocci
Journal:  J Endocrinol Invest       Date:  2008-10       Impact factor: 4.256

Review 9.  Endocrine neoplasms in familial syndromes of hyperparathyroidism.

Authors:  Yulong Li; William F Simonds
Journal:  Endocr Relat Cancer       Date:  2016-05-20       Impact factor: 5.678

10.  A Novel Mutation in a Patient with Hyperparathyroidism-Jaw Tumour Syndrome.

Authors:  Virginia Bellido; Ihintza Larrañaga; Maite Guimón; Rafael Martinez-Conde; Asier Eguia; Gustavo Perez de Nanclares; Luis Castaño; Sonia Gaztambide
Journal:  Endocr Pathol       Date:  2016-06       Impact factor: 3.943

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