Literature DB >> 15946210

Gene therapy for hemophilia: an imperative to succeed.

C Hough1, D Lillicrap.   

Abstract

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Year:  2005        PMID: 15946210     DOI: 10.1111/j.1538-7836.2005.01401.x

Source DB:  PubMed          Journal:  J Thromb Haemost        ISSN: 1538-7836            Impact factor:   5.824


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  10 in total

1.  Circumventing furin enhances factor VIII biological activity and ameliorates bleeding phenotypes in hemophilia models.

Authors:  Joshua I Siner; Benjamin J Samelson-Jones; Julie M Crudele; Robert A French; Benjamin J Lee; Shanzhen Zhou; Elizabeth Merricks; Robin Raymer; Timothy C Nichols; Rodney M Camire; Valder R Arruda
Journal:  JCI Insight       Date:  2016-10-06

Review 2.  Gene therapy for haemophilia: prospects and challenges to prevent or reverse inhibitor formation.

Authors:  David W Scott; Jay N Lozier
Journal:  Br J Haematol       Date:  2011-11-07       Impact factor: 6.998

Review 3.  Delivery of nucleic acid therapeutics by genetically engineered hematopoietic stem cells.

Authors:  Christopher B Doering; David Archer; H Trent Spencer
Journal:  Adv Drug Deliv Rev       Date:  2010-09-30       Impact factor: 15.470

4.  Gene Therapy for Inherited Bleeding Disorders.

Authors:  Valder R Arruda; Jesse Weber; Benjamin J Samelson-Jones
Journal:  Semin Thromb Hemost       Date:  2021-02-26       Impact factor: 4.180

5.  Co-Infection of the Hepatitis C Virus With Other Blood-Borne and Hepatotropic Viruses Among Hemophilia Patients in Poland.

Authors:  Marta Kucharska; Malgorzata Inglot; Aleksandra Szymczak; Weronika Rymer; Malgorzata Zalewska; Krzysztof Malyszczak; Urszula Zaleska-Dorobisz; Malgorzata Kuliszkiewicz-Janus
Journal:  Hepat Mon       Date:  2016-07-23       Impact factor: 0.660

6.  Evaluation of the activity levels of rat FVIII and human FVIII delivered by adeno-associated viral vectors both in vitro and in vivo.

Authors:  Wei Zhang; Jianhua Mao; Yan Shen; Guowei Zhang; Yanyan Shao; Zheng Ruan; Yun Wang; Wenman Wu; Xuefeng Wang; Jiang Zhu; Saijuan Chen; Weidong Xiao; Xiaodong Xi
Journal:  Blood Cells Mol Dis       Date:  2018-09-20       Impact factor: 3.039

7.  Obstacles and future of gene therapy for hemophilia.

Authors:  Valder R Arruda; Ben J Samelson-Jones
Journal:  Expert Opin Orphan Drugs       Date:  2015-07-18       Impact factor: 0.694

8.  Seroprevalence of hepatitis C, hepatitis B and HIV viruses in hemophiliacs born 1985-2010 in west Azarbaijan of Iran.

Authors:  Nasim Valizadeh; Shahin Nateghi; Mehran Noroozi; Sasan Hejazi; Fateme Aghanezhad; Afsaneh Akbarpoor Morad Ali
Journal:  Asian J Transfus Sci       Date:  2013-01

Review 9.  Protein-Engineered Coagulation Factors for Hemophilia Gene Therapy.

Authors:  Benjamin J Samelson-Jones; Valder R Arruda
Journal:  Mol Ther Methods Clin Dev       Date:  2018-12-31       Impact factor: 6.698

Review 10.  Gene Therapy for Hemophilia: Facts and Quandaries in the 21st Century.

Authors:  Valder R Arruda; Bhavya S Doshi
Journal:  Mediterr J Hematol Infect Dis       Date:  2020-09-01       Impact factor: 3.122

  10 in total

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