Literature DB >> 15886987

[Comparison of several viral vectors for gene therapy of corneal endothelial cells].

S C Beutelspacher1, N Serbecic, P Tan, M O McClure.   

Abstract

AIM: In this paper we compare the transduction efficiency, toxicity, and safety of retroviral vectors [equine infectious anemia virus (EIAV), human immunodeficiency virus-1 (HIV-1), human foamy virus (PFV] and adenovirus (Ad) for potential use in gene therapy of corneal endothelial cells.
METHOD: Murine corneal endothelial cells were transduced with EIAV, HIV-1, PFV, and Ad, resulting in the overexpression of a green fluorescent protein (eGFP) transgene marker. The transduction efficiency was assessed by flow cytometry, while cytotoxicity and apoptosis rate were detected by annexin V/propidium iodide (PI) stain.
RESULTS: Ad had the highest transduction efficiency with 99% of the cells expressing the transgene, followed by EIAV (95%), HIV-1 (75%), and PFV (43%). However, the high transduction efficiency of Ad also resulted in the highest apoptosis rate (25%) in the corneal endothelial cells. There was no detectable difference in the toxicity between PFV and HIV-1 (10%). EIAV transduction had the lowest cytotoxicity, with only 3% of the cells being annexin V/PI positive.
CONCLUSION: Compared to other vectors EIAV exhibited high transduction efficiency combined with low toxicity to corneal endothelial cells. Therefore, it is a powerful tool for gene therapy applications in selected corneal endothelial diseases.

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Year:  2005        PMID: 15886987     DOI: 10.1007/s00347-005-1230-6

Source DB:  PubMed          Journal:  Ophthalmologe        ISSN: 0941-293X            Impact factor:   1.059


  42 in total

Review 1.  In vivo gene delivery by lentiviral vectors.

Authors:  L Naldini
Journal:  Thromb Haemost       Date:  1999-08       Impact factor: 5.249

2.  Lipoadenofection-mediated gene delivery to the corneal endothelium: prospects for modulating graft rejection.

Authors:  C V Arancibia-Cárcamo; H B Oral; D O Haskard; D F Larkin; A J George
Journal:  Transplantation       Date:  1998-01-15       Impact factor: 4.939

3.  Modulation of human dendritic-cell function following transduction with viral vectors: implications for gene therapy.

Authors:  Peng H Tan; Sven C Beutelspacher; Shao-An Xue; Yao-He Wang; Peter Mitchell; James C McAlister; D Frank P Larkin; Myra O McClure; Hans J Stauss; Mary A Ritter; Giovanna Lombardi; Andrew J T George
Journal:  Blood       Date:  2005-01-25       Impact factor: 22.113

4.  Foamy virus particle formation.

Authors:  N Fischer; M Heinkelein; D Lindemann; J Enssle; C Baum; E Werder; H Zentgraf; J G Müller; A Rethwilm
Journal:  J Virol       Date:  1998-02       Impact factor: 5.103

5.  Development of a self-inactivating, minimal lentivirus vector based on simian immunodeficiency virus.

Authors:  T Schnell; P Foley; M Wirth; J Münch; K Uberla
Journal:  Hum Gene Ther       Date:  2000-02-10       Impact factor: 5.695

6.  Long-term replacement of a mutated nonfunctional CNS gene: reversal of hypothalamic diabetes insipidus using an EIAV-based lentiviral vector expressing arginine vasopressin.

Authors:  Alison S Bienemann; Enca Martin-Rendon; Anna S Cosgrave; Colin P J Glover; Liang-Fong Wong; Susan M Kingsman; Kyriacos A Mitrophanous; Nicholas D Mazarakis; James B Uney
Journal:  Mol Ther       Date:  2003-05       Impact factor: 11.454

7.  Analysis of gene transfer and expression in skeletal muscle using enhanced EIAV lentivirus vectors.

Authors:  J P O'Rourke; H Hiraragi; K Urban; M Patel; J C Olsen; B A Bunnell
Journal:  Mol Ther       Date:  2003-05       Impact factor: 11.454

8.  Retroviral vector-mediated gene transfer into keratocytes: in vitro effects of polybrene and protamine sulfate.

Authors:  B Seitz; E Baktanian; E M Gordon; W F Anderson; L LaBree; P J McDonnell
Journal:  Graefes Arch Clin Exp Ophthalmol       Date:  1998-08       Impact factor: 3.117

9.  Mitotic inhibition of corneal endothelium in neonatal rats.

Authors:  N C Joyce; D L Harris; J D Zieske
Journal:  Invest Ophthalmol Vis Sci       Date:  1998-12       Impact factor: 4.799

10.  Replicating foamy virus-based vectors directing high level expression of foreign genes.

Authors:  M Schmidt; A Rethwilm
Journal:  Virology       Date:  1995-06-20       Impact factor: 3.616

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  1 in total

Review 1.  [Gene therapy as a treatment concept for inherited retinal diseases].

Authors:  J-S Bellingrath; M D Fischer
Journal:  Ophthalmologe       Date:  2015-09       Impact factor: 1.059

  1 in total

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