Literature DB >> 15505399

Management of movement disorders in glutaryl-CoA dehydrogenase deficiency: anticholinergic drugs and botulinum toxin as additional therapeutic options.

A P Burlina1, G Zara, G F Hoffmann, J Zschocke, A B Burlina.   

Abstract

Glutaric aciduria type I is an inborn error of metabolism due to the deficiency of glutaryl-CoA dehydrogenase, an enzyme responsible for the catabolism of lysine, hydroxylysine and tryptophan. The most important neurological symptoms include dyskinesia and dystonia, which can be focal, segmental or generalized. Treatment of the extrapyramidal syndrome is often unsatisfactory. We report our experience in the treatment of generalized and focal dystonia with anticholinergic drugs and botulinum toxin type A, respectively. Both therapies proved beneficial.

Entities:  

Mesh:

Substances:

Year:  2004        PMID: 15505399     DOI: 10.1023/B:BOLI.0000045776.50573.52

Source DB:  PubMed          Journal:  J Inherit Metab Dis        ISSN: 0141-8955            Impact factor:   4.982


  6 in total

1.  Botulinum neurotoxins: mechanism of action and therapeutic applications.

Authors:  C Montecucco; G Schiavo; V Tugnoli; D de Grandis
Journal:  Mol Med Today       Date:  1996-10

Review 2.  Glutaric aciduria type 1 (glutaryl-CoA-dehydrogenase deficiency): advances and unanswered questions. Report from an international meeting.

Authors:  A Superti-Furga; G F Hoffmann
Journal:  Eur J Pediatr       Date:  1997-11       Impact factor: 3.183

3.  Type I glutaric aciduria, part 1: natural history of 77 patients.

Authors:  Kevin A Strauss; Erik G Puffenberger; Donna L Robinson; D Holmes Morton
Journal:  Am J Med Genet C Semin Med Genet       Date:  2003-08-15       Impact factor: 3.908

4.  Clinical course, early diagnosis, treatment, and prevention of disease in glutaryl-CoA dehydrogenase deficiency.

Authors:  G F Hoffmann; S Athanassopoulos; A B Burlina; M Duran; J B de Klerk; W Lehnert; J V Leonard; A A Monavari; E Müller; A C Muntau; E R Naughten; B Plecko-Starting; A Superti-Furga; J Zschocke; E Christensen
Journal:  Neuropediatrics       Date:  1996-06       Impact factor: 1.947

5.  Bilateral pallidotomy for severe dystonia in an 18-month-old child with glutaric aciduria.

Authors:  Goran Rakocevic; Kelly E Lyons; Steven B Wilkinson; John W Overman; Rajesh Pahwa
Journal:  Stereotact Funct Neurosurg       Date:  2004-03-19       Impact factor: 1.875

6.  Dystonia and dyskinesia in glutaric aciduria type I: clinical heterogeneity and therapeutic considerations.

Authors:  M Kyllerman; O H Skjeldal; M Lundberg; I Holme; E Jellum; U von Döbeln; A Fossen; G Carlsson
Journal:  Mov Disord       Date:  1994-01       Impact factor: 10.338

  6 in total
  9 in total

1.  Guideline for the diagnosis and management of glutaryl-CoA dehydrogenase deficiency (glutaric aciduria type I).

Authors:  S Kölker; E Christensen; J V Leonard; C R Greenberg; A B Burlina; A P Burlina; M Dixon; M Duran; S I Goodman; D M Koeller; E Müller; E R Naughten; E Neumaier-Probst; J G Okun; M Kyllerman; R A Surtees; B Wilcken; G F Hoffmann; P Burgard
Journal:  J Inherit Metab Dis       Date:  2007-01-03       Impact factor: 4.982

Review 2.  Diagnosis of dystonic syndromes--a new eight-question approach.

Authors:  Kelly L Bertram; David R Williams
Journal:  Nat Rev Neurol       Date:  2012-03-20       Impact factor: 42.937

Review 3.  Proposed recommendations for diagnosing and managing individuals with glutaric aciduria type I: second revision.

Authors:  Nikolas Boy; Chris Mühlhausen; Esther M Maier; Jana Heringer; Birgit Assmann; Peter Burgard; Marjorie Dixon; Sandra Fleissner; Cheryl R Greenberg; Inga Harting; Georg F Hoffmann; Daniela Karall; David M Koeller; Michael B Krawinkel; Jürgen G Okun; Thomas Opladen; Roland Posset; Katja Sahm; Johannes Zschocke; Stefan Kölker
Journal:  J Inherit Metab Dis       Date:  2016-11-16       Impact factor: 4.982

Review 4.  Maintenance treatment of glutaryl-CoA dehydrogenase deficiency.

Authors:  C Mühlhausen; G F Hoffmann; K A Strauss; S Kölker; J G Okun; C R Greenberg; E R Naughten; K Ullrich
Journal:  J Inherit Metab Dis       Date:  2004       Impact factor: 4.982

5.  Orthopaedic manifestations of glutaric acidemia Type 1.

Authors:  Ahmet Imerci; Kevin A Strauss; Geovanny F Oleas-Santillan; Freeman Miller
Journal:  J Child Orthop       Date:  2020-10-01       Impact factor: 1.548

6.  Cognitive, behavioural and adaptive profiles of children with glutaric aciduria type I detected through newborn screening.

Authors:  M H Beauchamp; A Boneh; V Anderson
Journal:  J Inherit Metab Dis       Date:  2009-05-23       Impact factor: 4.982

Review 7.  Update on pediatric dystonias: etiology, epidemiology, and management.

Authors:  Emilio Fernández-Alvarez; Nardo Nardocci
Journal:  Degener Neurol Neuromuscul Dis       Date:  2012-04-11

Review 8.  Diagnosis and management of glutaric aciduria type I--revised recommendations.

Authors:  Stefan Kölker; Ernst Christensen; James V Leonard; Cheryl R Greenberg; Avihu Boneh; Alberto B Burlina; Alessandro P Burlina; Marjorie Dixon; Marinus Duran; Angels García Cazorla; Stephen I Goodman; David M Koeller; Mårten Kyllerman; Chris Mühlhausen; Edith Müller; Jürgen G Okun; Bridget Wilcken; Georg F Hoffmann; Peter Burgard
Journal:  J Inherit Metab Dis       Date:  2011-03-23       Impact factor: 4.982

9.  Early neonatal Glutaric aciduria type I hidden by perinatal asphyxia: a case report.

Authors:  Giacomo Biasucci; Nicola Morelli; Federica Natacci; Massimo Mastrangelo
Journal:  Ital J Pediatr       Date:  2018-01-15       Impact factor: 2.638

  9 in total

北京卡尤迪生物科技股份有限公司 © 2022-2023.